ISOLATION AND QUANTIFICATION OF THE CORTICAL GRANULE LECTIN LIGAND OLIGOSACCHARIDES AND ELUCIDATION OF THEIR ROLE IN THE BLOCK TO POLYSPERMIC FERTILIZATION IN XENOPUS LAEVIS Noah Peter Kiedrowski B.S., California State University, Sacramento, 2007 THESIS Submitted in partial satisfaction of the requirements for the degree of MASTER OF SCIENCE in BIOLOGICAL SCIENCES (Molecular and Cellular Biology) at CALIFORNIA STATE UNIVERSITY, SACRAMENTO SPRING 2010 © 2010 Noah Peter Kiedrowski ALL RIGHTS RESERVED ii ISOLATION AND QUANTIFICATION OF THE CORTICAL GRANULE LECTIN LIGAND OLIGOSACCHARIDES AND ELUCIDATION OF THEIR ROLE IN THE BLOCK TO POLYSPERMIC FERTILIZATION IN XENOPUS LAEVIS A Thesis by Noah Peter Kiedrowski Approved by: __________________________________, Committee Chair Dr. Tom Peavy __________________________________, Second Reader Dr. Roy Dixon __________________________________, Third Reader Dr. Tom Landerholm iii Student: Noah Peter Kiedrowski I certify that this student has met the requirements for format contained in the University format manual, and that this thesis is suitable for shelving in the Library and credit is to be awarded for the thesis. __________________________, Graduate Coordinator Dr. James W. Baxter Department of Biological Sciences iv _________________ Date Abstract of ISOLATION AND QUANTIFICATION OF THE CORTICAL GRANULE LECTIN LIGAND OLIGOSACCHARIDES AND ELUCIDATION OF THEIR ROLE IN THE BLOCK TO POLYSPERMIC FERTILIZATION IN XENOPUS LAEVIS by Noah Peter Kiedrowski The block to polyspermic fertilization in Xenopus laevis is mediated by a calcium-dependent, galactose specific binding reaction between a lectin derived from the cortical granules and its ligand partners located in the immediate surroundings within the egg extracellular matrix. The cortical granule lectin (CGL) ligands have been shown to possess O-linked oligosaccharides as the functional moieties when binding to the CGL. However, it is unknown as to which particular ligand oligosaccharides are the functional moieties in the binding interaction. Elucidation of the functional oligosaccharides will be valuable to our understanding of fertilization and cell-cell binding interactions involving this lectin family of CGL-like proteins. In the current work, an HPLC based method was developed to profile the oligosaccharides found on the ligands and to isolate and quantify them for subsequent functional binding assays. A novel method was developed without derivatization agents or exact standards utilizing the HPLC-CAD (Charged Aerosol Detection) system v interfaced with an amino Prevail Carbohydrate ES HPLC column. The hypothesis for this study was that the HPLC-CAD methodology will allow the isolation and quantification of O-linked oligosaccharides released from the CGL ligand which can then be utilized in functional binding assays to assess which oligosaccharides function in the lectin-ligand binding interaction during the X. laevis block to polyspermy. In testing the methodology, it was demonstrated to be sensitive in the picomolar range or mass detection limits 0.3 to 0.9 ng with regard to oligosaccharides separated under optimized conditions. Commercially available standard oligosaccharides were accurately quantified to within less than a 19% average error with excellent reproducibility. The X. laevis CGL ligand oligosaccharides were chemically released and profiled using the HPLC-CAD demonstrating the presence of four predominate oligosaccharide peaks. Oligosaccharides were subsequently separated, isolated and quantified utilizing the developed quantification methodology employing the Prevail Carbohydrate ES HPLC column. A plate binding assay was developed (enzyme-linked lectin assay) to test whether particular compounds could competitively inhibit the binding interaction of purified CGL and ligands thereby implicating a functional role in binding. The data indicated that binding could be inhibited by galactose, fucose and the galactose containing disaccharides lactose and melibiose. In addition, it was found that whole vi CGL ligand oligosaccharide fractions possessed strong inhibition properties. The neutral CGL ligand oligosaccharide fraction demonstrated strong lectin-ligand inhibition characteristics eliciting a 95% reduction in binding, whereas the acidic CGL ligand fraction elicited only a 35% reduction. However, when the isolated and quantified CGL ligand oligosaccharide fractions were tested at concentrations of 10 and 45 µM, they were unable to elicit an inhibitory response of the lectin-ligand binding interaction. Based on these observations, the evidence suggests that there are oligosaccharides that do inhibit lectin-ligand binding that are derived from the ligands, but that the particular purified oligosaccharides tested were not effective at inhibiting binding at the concentrations used. Future studies will need to test these compounds at higher concentrations and to test other oligosaccharide fractions to elucidate which oligosaccharides are the functional binding moieties on the ligand. ___________________________, Committee Chair Dr. Tom Peavy ___________________________ Date vii ACKNOWLEDGEMENTS Dr. Tom Peavy I would like to give a special thanks to Dr. Tom Peavy for recruiting me into the graduate program and accepting to serve as my thesis advisor and mentor. I would like to thank him for introducing me into the research laboratory along with other graduate students from the onset of the graduate program and for proposing this specific research project for my thesis research. Additionally, I would like to thank Dr. Peavy for writing the grant proposal in collaboration with Dr. Roy Dixon that provided funding and support for my thesis research. I would like to thank him for graciously providing the purified cortical granule lectin (CGL) and Xenopus laevis egg jelly for the biological aspects of my thesis research. Furthermore, I would like to thank him for his supervisory role and support in my research efforts and lending his expertise in biological techniques and data interpretation. Lastly, I would to thank him for his time and assistance in proof reading, meeting and preparing for my advancement to candidacy, thesis and thesis defense seminar. Dr. Roy Dixon I would like to thank Dr. Roy Dixon for his supervisory role and support throughout my thesis research. Dr. Dixon was undoubtedly instrumental in bringing my thesis project to fruition, specifically with regard to the initial stages of the research viii project. His expertise in analytical chemistry and HPLC based chromatographic separations was indispensable to the project as a whole. Additionally, his assistance in trouble-shooting instrumentation, data interpretation and data analysis was essential in developing the HPLC-CAD oligosaccharide isolation and quantification methodology. I would like to thank him for his support in attending both CSU Biotechnology Symposiums in which our HPLC-CAD preliminary data was presented. Lastly, I would like to thank him for his assistance and time in preparing for both my advancement to candidacy and thesis defense seminar. Dr. Tom Landerholm I would like to thank Dr. Landerholm for accepting to serve as the final member of my graduate committee and facilitating my advancement to candidacy. Additionally, I would like to thank him for his advice throughout graduate school and proof reading my thesis. I would also like to thank Dr. Landerholm for the invitation and pleasure to be a guest speaker in his undergraduate biology seminar course. Simon Helminski I would like to thank my graduate colleague and friend Simon for providing laboratory support and advice throughout the graduate program and collaboration on experiments. I would like to thank him for assisting me with SDS-PAGE gel techniques, initial binding assay parameters and additional biological techniques and ix aspects of my thesis research. Additionally, I would like to thank him for lending his assistance and time on occasion as needed for some of my experimental questions and interpretation of results. Monique Bastidas I would like to thank Monique for assisting me in some of my quantitative HPLC-CAD work and for collaborating on both CSU Biotechnology Symposium presentations. Tom Boyce I would like to thank Tom Boyce for his contributions with regard to the initial HPLC-CAD work that was completed. My Family I would like to give a special thanks to my family for their unconditional support, patience and appreciation throughout graduate school and my thesis research. They have been extremely supportive and helpful during times when I have encountered difficult academic, research and/or personal obstacles during graduate school and throughout my thesis research. They have been a large part of my overall success in both the laboratory and in the academic setting throughout the graduate program. I appreciate their tolerance and patience during periods of frustration and setbacks. x Lastly, I would like to thank them for assisting me through times of doubt about graduate school on a whole and for helping me maintain my perseverance and optimism. xi TABLE OF CONTENTS Page Acknowledgements.........................................................................................................viii List of Tables...................................................................................................................xiii List of Figures................................................................................................................. xiv INTRODUCTION .............................................................................................................1 MATERIALS AND METHODS .....................................................................................19 Purification of X. laevis CGL Ligands .................................................................19 Release and Purification of X. laevis CGL Ligand Oligosaccharides .................19 HPLC-CAD Methodology Development ............................................................21 Separation, Fractionation and Isolation of CGL Ligand Oligosaccharides .........29 Quantification and Secondary Purification ..........................................................30 Procurement and Preparation of X. laevis Egg Jelly and CGL ............................31 SDS-PAGE Gel Characterization of X. laevis Egg Jelly and CGL .....................32 Competitive Enzyme-Linked Lectin Assays .......................................................34 RESULTS ........................................................................................................................37 DISCUSSION ................................................................................................................104 Literature Cited ..............................................................................................................121 xii LIST OF TABLES Page Table 1. Initial characterization and profiling of CGL ligand oligosaccharides .............58 Table 2. HPLC-CAD profile of X. laevis CGL ligand oligosaccharides. .......................62 Table 3. CGL ligand oligosaccharide fractions with concentrations. .............................72 xiii LIST OF FIGURES Page Figure 1A. Distribution of X. laevis egg jelly layers ........................................................6 Figure 1B. Diagrammatic representation of the frog egg .................................................6 Figure 2. Diagrammatic representation of the HPLC-CAD system ...............................23 Figure 3. Diagrammatic representation of the electrical aerosol size-analyzer. .............26 Figure 4. A Gradient method chromatogram (oligosaccharide standards) .....................38 Figure 5. Gradient calibration plot (oligosaccharide standards). ....................................41 Figure 6. ‘A’ Term calibration plot.................................................................................43 Figure 7. ‘b’ Term calibration plot. ................................................................................44 Figure 8. Quantification of surrogate oligosaccharide standards....................................47 Figure 9. Short chain oligosaccharide structures. ...........................................................49 Figure 10. Quantification of short chain oligosaccharides .............................................52 Figure 11. Biological test oligosaccharide structures. ....................................................54 Figure 12. Quantification of biological test oligosaccharides ........................................56 Figure 13. Prevail chromatogram of X. laevis ligand oligosaccharides. .........................60 Figure 14. Hypercarb chromatogram of X. laevis ligand oligosaccharides ....................61 Figure 15. Prevail chromatogram overlay with oligosaccharide standards. ...................66 Figure 16. Prevail purity and quantification fraction analysis (CAD signal) .................68 Figure 17. Prevail purity and quantification fraction analysis (UV signal). ..................70 Figure 18. X. laevis egg jelly SDS-PAGE gel ................................................................75 xiv Figure 19. X. laevis native CGL and biotinylated CGL SDS-PAGE gel. .......................78 Figure 20. Reactivity of the enzyme-linked lectin assay ................................................81 Figure 21. Monosaccharide inhibition of the enzyme-linked lectin assay......................84 Figure 22. Monosaccharide inhibition of the enzyme-linked lectin assay......................86 Figure 23. Monosaccharide inhibition of the enzyme-linked lectin assay......................87 Figure 24. Disaccharide inhibition of the enzyme-linked lectin assay ...........................89 Figure 25. Disaccharide inhibition of the enzyme-linked lectin assay. ..........................91 Figure 26. Monosaccharide structures and binding specificity of the CGL ...................94 Figure 27. Disaccharide structures and binding specificity of the CGL. ........................95 Figure 28. Enzyme-linked lectin assay (whole ligand oligosaccharide fractions)..........97 Figure 29. Enzyme-linked lectin assay (isolated ligand oligosaccharide fractions). ....101 Figure 30. Enzyme-linked lectin assay (isolated ligand oligosaccharide fractions). ....103 xv 1 INTRODUCTION Fertilization is a highly choreographed event that is essential for the reproductive success of a species so as to produce viable offspring. Fertilization typically involves the union between a nucleus of a male haploid (N) gamete and a nucleus of a female haploid (N) gamete to reconstitute the normal diploid (2N) chromosome number. Species have evolved a highly stringent regulatory process with regard to sperm selection and entry into the egg to ensure successful fertilization. Regulation of sperm entry into the egg is essential in disallowing more than one sperm from penetrating the egg in the majority of species. The penetration of multiple sperm into the egg results in polyspermic fertilization and subsequent deleterious effects such as spontaneous abortion, premature death or developmental abnormalities [1]. Polyploid conditions (i.e. greater than 2N) in human embryos are usually fatal. If more than one sperm is successful in fertilizing an egg, the abundance of genetic material results in faulty segregation of chromosomes and the resulting polyploid embryo is aborted. If survival beyond parturition occurs, then many detrimental polyploid conditions manifest themselves in which mental retardation along with a host of physical defects are observed. To prevent polyploid associated conditions, most species have evolved molecular and structural mechanisms to ensure the fusion of only one sperm with the female pronucleus. In nearly all vertebrates, the extracellular matrices surrounding the 2 egg are utilized as an essential defense mechanism in disallowing more than one sperm from penetrating the egg. These extracellular matrices are composed of glycoproteinrich layers overlying the egg plasma membrane. The innermost layer, termed the zona pellucida in mammals and the vitelline envelope in most non-mammals (in general, this innermost layer will be referred to as the egg envelope), participates in a number of essential functions during fertilization. These functions include sperm-egg binding, induction of the acrosome reaction and formation of the block to polyspermy [2,3]. In particular, sperm-egg binding occurs between molecules located on the outer surface of the sperm plasma membrane and outer surface of the egg envelope. Subsequent to a single sperm entry into the egg, these egg envelope sperm-binding glycoproteins become structurally modified by a series of events triggered by the release of secretory vesicles that reside just beneath the egg plasma membrane. These secretory vesicles, termed cortical granules, release their contents by exocytosis (fusion with the overlying plasma membrane) and the subsequent interaction of their contents with the egg envelope constitutes the egg cortical reaction. These cortical granules are triggered to fuse with the egg plasma membrane. Cortical granule fusion is initiated near the site of sperm contact, facilitating a wave of calcium release which sweeps around the egg, followed by a wave of cortical granule fusion [2,3]. Contents of the egg cortical granules vary with species however they typically include enzymes and structural proteins. The enzymatic contents consist of glycosidases 3 and proteases which remove carbohydrate and cleave proteins respectively and are targeted to destroy sperm binding receptors and thus the ability of sperm to bind and penetrate through the egg envelope. Additionally, non-enzymatic components are released which include a glycoprotein, termed the cortical granule lectin (CGL). Lectins are broadly classified as sugar-binding proteins, which are highly specific for their sugar moieties and typically play a role in binding mechanisms involving cells and proteins. In fertilization, a binding reaction occurs between the cortical granule derived lectin, CGL, and glycoproteins found on the outer surface of the egg envelope, termed CGL ligands. When CGL binds to these ligands, they form a large complex which induces a conformational change in the extracellular matrix, thereby providing a physical barrier to additional sperm penetration. Collectively, these released cortical granule contents (enzymes and CGL) result in a “hardening” by means of chemically modifying the structure of the egg envelope, thereby establishing a permanent block to polyspermy [2,3,4]. Nearly all of what is currently known about the block to polyspermy in vertebrate organisms originally were derived from experiments utilizing the model frog Xenopus laevis and then subsequently were discovered to be conserved in mammals as well [13]. The South African frog X. laevis has served as an excellent model for fertilization studies due to its large egg size (1 mm in diameter), ease of obtaining large quantities of gametes (inducing ovulation via hormone injection and yielding ~3000 eggs) and visibility of the process since fertilization is external (typically in pond 4 water). Much of what has been found in X. laevis is translatable to mammals. With respect to the mammalian zona pellucida and the X. laevis, vitelline envelope, they both consist of homologous proteins which perform identical functions during fertilization [5,6,7]. Additionally, in both mammals and X. laevis these egg envelope protein homologues originate from the egg itself during oogenesis and follicle maturation [7,8]. Subsequent to ovulation in X. laevis, the egg transits through the oviduct where mucous-like glycoproteins secreted from the oviduccal tissue are sequentially deposited around the egg, forming a thick outer jelly coat [7,8]. Mammals are dissimilar in this respect as they do not possess a thick outer jelly coat layer per se, however the mammalian egg does consist of oviduct-derived glycoproteins that associate with the egg and mucous-like secretions derived from follicle cells termed cumulus cells [2,3]. Many functional parallels have been established between X. laevis and mammals with regard to fertilization, thus much of what we learn about the molecular interactions involved during fertilization using X. laevis may be informative with regard to mammalian fertilization. In X. laevis, three morphologically distinct jelly coat layers, J1, J2 and J3 from innermost to outermost, are deposited around the egg sequentially as the egg transverses through the oviduct (Figure 1). These egg jelly coat layers have been demonstrated to play an essential role in fertilization, whereby removal of the jelly layers resulted in the inability of sperm to fertilize the egg. Interestingly, this observation was reversible in 5 the presence of solubilized egg jelly [6,7]. This finding has been attributed to chemotactic molecules, calcium-binding reservoirs and other structurally and/or functionally important glycoproteins residing in the egg jelly [5,6,14]. 6 Figure 1 – A. Distribution of X. laevis egg jelly layers containing glycoproteins involved in fertilization [18]. B. Diagrammatic representation of the frog egg and the cortical granules lying beneath the plasma membrane. 7 It has been well documented that the contents of the egg cortical granules, alter the properties of the jelly coat layers when released by sperm-induced exocytosis, thereby establishing the functional block to polyspermy [5,6,7,9]. In particular, the CGL binds to jelly coat ligands at the innermost jelly coat layer, J1, and thereby forms an electron dense fertilization layer which results in a physical compositional and conformational change of the extracellular matrix that becomes impenetrable by sperm [7,10,11]. The CGL ligands are large highly glycosylated extracellular matrix proteins that are derived from the superior portion of the oviduct and possess an affinity for the CGL. This fertilization layer leads to “hardening” of the egg as measured by an increased resistance to physical deformation, proteolysis, thermal dissolution and solubility of the VE [5,6,7,9]. CGL is the major constituent of the cortical granule exudate, accounting for 77% of the total glycoproteins released [9]. In addition to the CGL, the cortical granule exudate consists of several other proteins such as proteases and glycosidases which collectively act to simultaneously produce a permanent block to polyspermy, as mentioned previously. CGL is a carbohydrate binding glycoprotein that serves in binding recognition involving cells and proteins. The binding interaction with its jelly coat ligands has been shown to be specific for terminal galactose residues and also dependent on the presence of calcium [9,10,11]. 8 Further analysis of this specific lectin-ligand glycoprotein binding interaction has valuable implications since the existence of the X. laevis CGL gene was found to be present in a variety of vertebrate genomes, including humans. The presence of the CGL homologue was found to be expressed in the eggs of mice, pigs and rhesus macaque [13,14]. The human and mouse homologue, termed intelectin, displayed high amino acid identity (> 60%) relative to the X. laevis CGL polypeptide [15]. Interestingly, invitro fertilization experiments with mice demonstrated further functional homology when exogenous X. laevis CGL was incubated with mouse eggs prior to the addition of sperm and it was observed that the CGL prevented sperm entry into the mouse eggs [13,14]. Additionally, the CGL effect on the unfertilized mouse eggs was found to be concentration dependent and could be inhibited when galactose and/or galactosecontaining compounds were competitively introduced [13,14]. Furthermore, human and mouse intelectin was found to be expressed not only in the egg, but in many different tissues. Human intelectin gene expression has been shown to occur in at least 24 different tissues including; heart, liver, kidney, lung, brain, prostate, bone marrow, small intestines and notably the ovary [16]. Expression of the CGL homologue in many human adult tissues suggests that CGL participates in a wide variety of functions in the fully developed organism in addition to the block to polyspermy. Expression of the CGL gene in X. laevis has been shown to be present at other developmental stages in non-ovarian tissues, suggesting a possible role of the CGL in somatic tissues as well [15]. 9 Several other CGL-like proteins have since been identified in organisms as diverse as ascidians [15]. Since CGL and CGL-like proteins are not significantly related to any of the other known lectin families, they have been classified as a new family of lectins termed the eglectins [15]. All of the eglectins found to date appear to function in cell-cell recognition mechanisms and can be found as both soluble lectins or as cell-surface receptors. The eglectins possess four significant characteristics; 1) binding is calcium-dependent; 2) binding is specific for terminal galactose residues; 3) exist as large oligomers; and 4) are glycosylated proteins [15]. Collectively, this evidence suggests that the structural and functional properties of eglectins and in particular CGL are likely to be conserved including their binding specificity. Although CGL has been purified, cloned and well characterized, little is know about the molecular identity of its ligand partners [6,9,15,17]. Yet, previous work has demonstrated that the X. laevis CGL ligands, isolated from the fertilization layer, are high molecular weight glycoproteins of 450 and 630 kDa [6,11,12]. The amino acid sequence of these proteins is unknown and thus it is unclear as to how these two ligands are related. The CGL ligands have been shown to possess O-linked oligosaccharides which are characterized by the addition of sugars to the hydroxyl (-OH) groups of selected serine or threonine side chains of the polypeptide backbone. The CGL ligands have been demonstrated to possess O-linked oligosaccharides with terminal galactose residues as the functional moieties in binding activity [9,11,12]. Previous research has demonstrated that under hydrolysis conditions in which β-elimination was employed to 10 cleave O-linked oligosaccharides, ligand function was rendered non-functional [11]. Furthermore, exposure to α-galactosidase (cleavage of terminal α-galactosyl moieties from glycoproteins) conditions, ligand binding capabilities and its affinity for its lectin partner were rendered ineffective, resulting in a 75% decrease in binding association [11]. In addition, monosaccharide competitive inhibition analysis of the lectin-ligand binding reaction utilizing an enzyme-linked lectin assay (ELLA) demonstrated that galactose was able to inhibit the binding interaction, while no significant inhibition was observed with mannose [11,12]. Competitive inhibition studies utilizing galactosecontaining disaccharides such as lactose and melibiose exhibited complete inhibition of the lectin-ligand binding reaction as well [9,13]. These data provide strong evidence that terminal galactose residues may be the essential terminal carbohydrate component that is recognized by the CGL and that the binding interaction is dependent on ligand Olinked oligosaccharide moieties. O-linked oligosaccharides are distributed throughout the X. laevis egg extracellular matrix as well as the three distinct jelly coat layers; J1, J2 and J3 from innermost to outermost, respectively (Figure 1) [18,19]. Each jelly coat layer is composed of 50-60% O-linked oligosaccharides by weight, therefore these oligosaccharide rich layers in combination with the egg envelope are likely to play a critical role in many events leading to fertilization such as sperm binding, sperm 11 selection, the acrosome reaction and the block to polyspermy [5,6,7,8,19,20]. Structural elucidation of the vastly distributed O-linked oligosaccharides throughout the egg jelly coats have been performed by utilizing nuclear magnetic resonance (NMR) and mass spectrometry (MS) [19,21,22]. The primary structural motifs of neutral oligosaccharides released by β-elimination from the egg jelly coats were determined by NMR analysis, and it was found that a subset of these oligosaccharide structures contained terminal galactose and fucose residues [19,21]. In addition, structural determination of both neutral and anionic O-linked oligosaccharides derived from the whole egg jelly coat extract was elucidated by MS [22]. The MS analysis demonstrated the presence of O-linked oligosaccharide components with conjugated anionic sulfate groups throughout the egg jelly coat [22]. In addition to the sulfated O-linked oligosaccharides, the structure of many neutral oligosaccharides were elucidated and demonstrated that terminal galactose and fucose residues are prevalent throughout these neutral species. It was also found that neutral oligosaccharides from whole jelly glycoproteins ranged in size from trisaccharides to octasaccharides [18,22]. A complementary study on X. laevis employed MS to characterize the distribution and structure of O-linked oligosaccharides with respect to the three distinct egg coat jelly layers [18]. The sulfated O-linked oligosaccharides were found to be present in both the combined J1 and J2 layers of the egg jelly; however, these sulfated oligosaccharides were entirely absent in the J3 layer [18]. The J3 layer was composed primarily of neutral oligosaccharides and the combined J1 and J2 layers 12 contained approximately half the number of neutral species but contained all the sulfated species. Substantial progress has been obtained in elucidating the role of the ligand Olinked oligosaccharides as the functional moieties in binding to its CGL partner. Interestingly, the 450 and 630 kDa CGL ligands have been shown to stain with alcian blue, a dye that stains sulfated (acidic) glycoconjugates [14,18,23,24,25]. In addition, MS studies have shown that these ligands contain sulfated groups attached to their oligosaccharide structures. Collectively, O-linked oligosaccharide components present within the egg jelly coat layers contain terminal galactose and fucose residues along with associated sulfate groups, all of which may be biologically relevant structures recognized by the CGL during the block to polyspermy [11,12,18,19,21,22]. Lectins in general are known to have more residues involved in their binding interactions than merely a single terminal monosaccharide (oligosaccharide specificity). This is demonstrated by the mannose-binding lectin, a free blood plasma protein instrumental in the pathogen-recognition system of innate immunity. The mannosebinding lectin recognizes bacterial surfaces that display a specific spatial arrangement of both mannose and fucose residues [26]. Regarding the CGL specifically, it has been demonstrated to possess specificity for galactose-containing saccharides and the relative affinities are modulated by secondary structural features such as terminal sugar, anomeric configuration and the linkage pattern of branching sugars [9,11,13,27]. As 13 mentioned previously, CGL exists naturally in an oligomeric conformation (~10-12 subunits) and thus possesses multivalency for ligand oligosaccharides. It has been postulated that the biological role of multivalency is utilized to compensate for weaker binding affinities for the monovalent binding interactions of single subunits and thus increases the overall binding strength of the interaction. The dissociation constants measured for lectins generally are in the range of Kd = 10-6 whereas antigen-antibody and other receptor-ligand interactions are in Kd = 10-9 or one thousand-fold stronger. A useful analogy for the accumulated strength attained by multivalent binding interactions is velcro. A single velcro hook and loop interaction is not very strong and can be easily pried apart, whereas the overall bond strength is increased by possessing more individual hook and loop fasteners involved in the interaction thereby increasing the amount of surface area available for contact. Thus, the spatial orientation and surface area of the lectin binding sites provided by the natural ligand may also be important with respect to producing the block to polyspermy [26,27]. Although quite a bit has been learned about the CGL-ligand interaction, it is unknown which of the ligand O-linked oligosaccharides are functionally relevant. Therefore, further analyses such as isolation and quantification of the oligosaccharide functional moieties and determining which structures bind with the highest relative affinity to the CGL will contribute to a more definitive molecular mechanism and role in the block to polyspermy. Elucidation of the CGL-ligand molecular specificity of oligosaccharide binding will likely advance our understanding of fertilization and cell- 14 cell binding interactions involving eglectins, since the binding properties of the CGL and its biological role appear to be conserved. Challenges arise when studying the biological properties of oligosaccharides since isolation and quantification methods often involve multiple analytical instruments and derivatization procedures, respectively [28]. Quantification of oligosaccharides typically requires large quantities for assays and/or derivatization procedures that chemically modify their structures. Previous methods employed to separate oligosaccharides liberated from their polypeptide backbone by either chemical or enzymatic means have included different HPLC techniques and capillary electrophoresis along with subsequent analysis from MS and NMR to elucidate structural characteristics [18,28,29]. Since oligosaccharides lack strong chromophores, or lack chromophores all together, sensitive quantification analysis methodologies have utilized derivatization by incorporating a UV-absorbing or fluorescing group into the oligosaccharide for subsequent detection [28]. Derivatization procedures require the removal of such chemical modifications to reestablish the native compound for subsequent biological assays. Thus, derivatization possesses limitations and can be a laborious process. Methods have been employed that do not require derivatization, such as highperformance/high-pH anion exchange chromatography (HPAEC) coupled to pulsed amperometric detection (PAD) and HPLC equipped with UV detection, however these 15 methodologies have limitations. The HPLC-PAD requires a high salt content for this methodology to be effective which can interfere with subsequent analysis, while the HPLC-UV is limited to oligosaccharides that contain an N-acetyl group in the hexosamine residues of chromophores in order to absorb at a specified wavelength and the sensitivity is poor [18,28,30]. Previously, quantification of underivatized O-linked oligosaccharides derived from the X. laevis egg jelly coat layers was attempted using measured UV absorbance of chromophores at 206nm [18]. However, researchers were unable to profile all possible oligosaccharides since the absence of N-acetylhexosamine residues would result in no detectable signal. Interestingly, no linear relationship was found to exist between UV absorbance and the number of N-acetylhexosamine residues present, which would limit the ability to accurately quantify the oligosaccharide chains [18]. It is noteworthy to point out that a relative quantification of the O-linked oligosaccharides was determined and compared to the most abundant component within the egg jelly coats, and it was found that the most abundant oligosaccharides within the combined J1 and J2 layers contained terminal galactose and fucose residues, further corroborating previous NMR and MS findings [18]. To circumvent these limitations, a superior method to isolate and quantify underivatizated oligosaccharides is needed. Recently, a charged aerosol based detection (CAD) method coupled with HPLC has been developed that has the potential to 16 quantify underivatized oligosaccharides independently of their structural properties [31,32]. The direct detection without fluorescent derivatization of biologically relevant oligosaccharides has been achieved by employing this novel HPLC-CAD device utilizing a hydrophilic interaction liquid chromatography column [30]. This detection method has successfully demonstrated sensitivity in the picomolar range or mass detection limits of 0.3 to 0.7 ng with regard to monosaccharides and oligosaccharides [33,34]. Both UV and derivatization procedures have demonstrated sensitivities in the picomolar range as well, however the HPLC-CAD method was demonstrated to be approximately five times more sensitive than conventional UV absorbance detection. Conversely, the HPLC-CAD was demonstrated to be approximately ten times less sensitive than derivatization with fluorescent detection with regard to oligosaccharides [30]. Thus, this HPLC-CAD system is likely to provide a universal detection method along with greater sensitivity than most conventional HPLC-detection based methods while circumventing complications associated with derivatization procedures. Since the detection method is based on detecting non-volatile charged particles, which can be applied more universally to compounds, quantification is predicted to be possible without exact oligosaccharide standards [30,31,33]. Surrogate oligosaccharide standards possessing similar properties as the compounds to be analyzed are utilized and thus a relationship between calibration standards and the output signal of the instrument is expected to be quantifiable and translatable to biologically-derived oligosaccharides. 17 The aim of this research is to accurately determine the relative quantities of Olinked oligosaccharides present on the CGL ligand and to utilize isolated oligosaccharides in functional binding assays to determine which oligosaccharides function in the CGL-ligand binding interaction. HPLC-CAD profiles and purification thereof of the CGL ligand oligosaccharides will assist in elucidating the preferential oligosaccharides that participate in CGL binding and their relative abundance. Separation and quantification of the ligand oligosaccharide constituents can be used to generate an oligosaccharide profile of the ligand and reveal the predominate components. Predominate peaks will be isolated, quantified and then used in an enzyme-linked lectin assay (ELLA) to assess whether these particular oligosaccharides can bind to CGL. This in-vitro functional binding assay may be able to estimate the relative binding affinity of particular isolated oligosaccharides to purified CGL. In addition, this research will re-evaluate the inhibition effects of commercially available saccharides (i.e. galactose, lactose, melibiose, etc.) using our refined ELLA assay. This research has two major implications. Firstly, the contribution of this developed oligosaccharide isolation and quantification methodology may have many other applications throughout the scientific community. This novel HPLC-CAD technique should allow sensitive and universal detection of any sugar and allow quantification of biologically relevant oligosaccharide concentrations in their native state thus circumventing any derivatization procedures that may interfere with 18 subsequent biological assays. Secondly, this research will assist in identification of the ligand oligosaccharides that functionally bind to CGL and thus participate in the block to polyspermy. Further implications with regard to the molecular binding mechanism of CGL homologues may be deduced since compelling evidence suggests its calciumdependent, galactose-specific binding properties are conserved in this lectin family. Provided all this information, the following hypothesis and objectives have been set forth. Hypothesis: HPLC-CAD will allow the isolation and quantification of O-linked oligosaccharides released from the CGL ligand which can then be utilized in functional binding assays to assess which oligosaccharides function in the lectin-ligand binding interaction during the Xenopus laevis block to polyspermy. Objectives: 1) Develop an HPLC-CAD methodology for quantification and isolation of biologically relevant oligosaccharides. 2) Apply the developed methodology to profile, quantify and permit the purification of X. laevis CGL ligand O-linked oligosaccharides. 3) Develop and perform enzyme-linked lectin assays (ELLA) to assess whether isolated CGL ligand oligosaccharide fractions are involved in the CGL binding interaction. 19 MATERIALS AND METHODS Purification of X. laevis CGL Ligands Recently, an Alcian blue dye binding methodology has proven advantageous for the purification of the X. laevis CGL ligands [6,25]. Cationic dyes, such as Alcian blue have been demonstrated to selectively stain the highly glycosylated acidic ligand glycoproteins within X. laevis egg jelly which can be visualized after separation by SDS-PAGE [25]. This method provides a rapid and effective way to distinguish acidic glycoproteins from other proteinaceous components which can be utilized for subsequent purification of these components. The Alcian blue dye preferentially binds to the sulfated ligands under acidic conditions within the crude egg jelly extract. An Alcian blue precipitation procedure was developed by Dr. Peavy so as to generate a resin of purified ligands bound to the Alcian blue dye which can then be separated by either electrophoresis (SDS-PAGE and electroelution) or used directly in the alkalineborohydride reduction methodology described below since this chemical procedure disrupts dye binding to the oligosaccharides. Release and Purification of X. laevis CGL Ligand O-linked Oligosaccharides Alcian blue pellets complexed with the CGL ligands were subjected to a protocol for the release and purification of O-linked oligosaccharides, thus dissociating the protein and carbohydrate moieties [18,22]. This protocol utilizes alkalineborohydride reduction to achieve the desired dissociation. The Alcian blue pellets were 20 dissolved in a 1.0 M NaBH4/0.1 M NaOH solution which was prepared by dissolving the appropriate amount of NaBH4 solid into 0.1 M NaOH solution and incubated for 24 hours in a water bath at 45°C. Following the reduction protocol, the resulting solution was neutralized with a 1.0 M HCl solution to stop the reaction and destroy the excess NaBH4 in an ice bath. The resulting neutralized solution consisting of reduced oligosaccharides was stored at 4°C. Removal of impurities along with isolation of the O-linked oligosaccharides was performed utilizing centrifugation and column separation using porous graphitized carbon solid-phase extraction (PGC-SPE) 4.0 mL cartridges (Grace Davison Discovery Science, Deerfield, IL) [18,35]. Neutralized solution was centrifuged at 10,000 rpm for 12 minutes and the resulting supernatant was aspirated and applied to a PGC-SPE cartridge. Most of the Alcian blue is not retained in this neutralized supernatant solution. Prior to use, the PGC-SPE cartridge was conditioned with three column volumes (5 mL) of 80% acetonitrile in 0.1% trifluoroacetic acid followed by three column volumes of water. When applied, monosaccharides and salts pass through the cartridge (flow through fraction), whereas peptides, oligosaccharides and the remaining Alcian blue dye bind to the solid-phase matrix [25,35]. The cartridge was washed with three column volumes of water to completely remove salts while the O-linked oligosaccharides remain bound to the stationary carbon phase. The neutral and acidic CGL ligand O-linked oligosaccharides were successfully eluted from the PGC-SPE cartridge with three column volumes of 25% acetonitrile/75% water solvent and 25% 21 acetonitrile/0.05% trifluoroacetic acid/water solvent, respectively, while the peptides and Alcian blue dye remained entrapped [18,35]. After preliminary HPLC analysis of the CGL ligand oligosaccharides (described below), it was observed that an early eluting, large peak suspected to be comprised of salts, monosaccharides and other impurities was consistently present. Therefore, in an effort to rid subsequent GCL ligand oligosaccharide samples of this initial contaminant, an additional “clean-up” step consisting of a 5% acteonitrile/95% water wash was added to the PGC-SPE procedure prior to the 25% acetonitrile/75% water solvent in order to reduce the amount of this initial peak. Furthermore, the resulting PGC-SPE neutral oligosaccharide fractions were subjected to a Millex-LG 0.20µm hydrophilic 4mm syringe driven filtration unit (Millipore, Billerica, MA) for fine particle removal. Purified neutral oligosaccharide samples were centrifuged under heated conditions to evaporate the acteonitrile in the sample followed by a subsequent round of centrifugation under a vacuum (speed-vac). The resulting dried oligosaccharide samples were stored at –20°C for subsequent HPLC analysis. HPLC-CAD Methodology Development for the Quantification of Oligosaccharides An Agilent (Santa Clara, CA) 1100 series high performance liquid chromatograph outfitted with a custom-built charged aerosol detection system (HPLCCAD) in tandem was employed to develop a sensitive method for quantification of 22 neutral oligosaccharides (Figure 2). Chem Station software was used to operate the instrument. A Prevail Carbohydrate ES HPLC column (250 x 4.6 mm – 5µm particle size) along with a Prevail guard column (Grace Davison Discovery Science, Deerfield, IL) was used for HPLC separation of neutral oligosaccharides. 23 Figure 2 – A diagrammatic representation of the HPLC-CAD system and associated components. 24 The custom-built CAD system utilizes similar equipment as described in Dixon and Peterson [31] but with some modifications. Following separation, analytes from the HPLC column enter the nebulizer (Meinhard, Santa Ana, CA) which in turn produces spray droplets along with a flow of nitrogen gas. Solvent is evaporated away from the droplets in the heated drift zone and converted into particles, upon which, detection of aerosol particles occur (Figure 2). The HPLC-CAD system detects particles that have been charged during the nebulization stage, in a process termed spray electrification. Spray electrification produces approximately equal amounts of both positively and negatively charged particles. Aerosol detection is carried out with an electrical aerosol size-analyzer (EAA) (TSI, Shoreview, MN) (Figure 3). The ion filter includes a negatively charged rod and grounded surrounding wall that is necessary to preferentially remove negatively charged particles. The ion filter permanently removes small positivity charged and most negatively charged particles that travel to the rod or walls. The greater efficiency in removal of negatively charged particles occurs as a result of the particles entering the ion filter close to the wall. The remaining charged aerosol particles that reach the aerosol filter are trapped and subsequently detected with an electrometer. The flux of charged aerosol particles of net positive charge produces a current that is measured by the electrometer. Greater voltages applied to the EAA’s ion filter result in a decreased signal due to removal of more positively charged particles prior to reaching the detector, resulting in a decreased overall positive charge flux reaching the electrometer. Thus, the 25 sensitivity of chromatographic analyses as well as the dynamic range (minimum detectable concentration to maximum detectable concentration) can be modulated by adjusting voltage. 26 Sample Aerosol In (stays in shaded region) EAA Sheath Air Flow 1 Corona Discharge Ion Filter Sheath Air Number 2 Aerosol Filter To Electrometer Figure 3 – A diagrammatic representation of the electrical aerosol size-analyzer (EAA) with associated components. 27 Surrogate standards consisting of cyclodextrins (α-cyclodextin, β-cyclodextrin and 6-O-α-maltosyl-β-cyclodextrin) and linear chain oligosaccharides ranging from glucose to maltooctaose (all α1→6 linked glucose-containing oligosaccharides with a degree of polymerization from one to eight) were prepared at 1, 4, 10, and 25 µg/mL concentrations in 50% water/50% acetonitrile mixtures for calibration purposes. Prepared samples were transferred to 2 mL amber autosampler vials using 9 mm closure vial caps (Fisher Scientific, Pittsburgh, PA) for HPLC analysis. Initial testing of the developed quantification methodology was explored with four test standards consisting of three trisaccharides and one tetrasaccharide, which were prepared at 10 µg/mL concentrations (isomaltotriose, raffinose, melezitose and stachyose). The linear chain oligosaccharide standards ranging from a degree of polymerization from three to seven and the initial four test standards were prepared from a Supelco oligosaccharide kit (Bellefonte, PA), whereas maltooctaose was prepared from Carbosynth (Beedon Newbury, Berkshire, UK). The cyclodextrins, glucose and maltose were prepared from Sigma-Aldrich (St. Louis, MO). All sample runs with regard to quantification work were performed at -300 volts (ion filter voltage reading on the EAA) utilizing 20 µL injection volumes during each chromatographic analysis on the HPLC-CAD system. Two methods were developed for quantification analysis: an isocratic method in which solvent conditions remained constant and a gradient method in which solvent conditions changed gradually over time throughout the chromatographic runs. The isocratic method consisted of 62% 28 acetonitrile/38% water solvent conditions over 30 minutes, while the gradient method was performed with a decreasing percentage of acetonitrile from 65% to 50% over 25 minutes throughout the sample runs. The flow rates were 1.0 mL/min for both developed methodologies. Additional oligosaccharide standards more representative of typical structures found on glycoproteins including branched structures of comparable molecular structure relative to the CGL ligand oligosaccharides were prepared to test the developed quantification methods. These commercially available branched oligosaccharides contained specific residues (monosaccharides) expected to be present in our selected fraction isolates, such as terminal fucose and galactose residues. Additionally, core glycoprotein structures such as branched N-acetylglucosamines and mannose hybrids were utilized to test the quantification method. All biological test structures were prepared at 10 µg/mL concentrations and consisted of Lacto-N-hexose (LNH), Lacto-NFucopentaose (LNFP II), oligomannose-3 (MAN-3), Asialo- galactosylated- biantennary (NA2), Asialo- galactosylated- tetraantennary (NA4), mannopentaose and lactodifucotetraose (LDFT). LNH, LNFP II and NA4 were prepared from Prozyme/Glyco (San Leandro, CA). NA2 and MAN-3 were prepared from V-labs (Covington, LA). Mannopentaose was prepared from Sigma-Aldrich (St Louis, MO) and LDFT was prepared from Glycotech (Gathersburg, MD). 29 Multiple sugar standards, including the various branched structures were prepared at different concentrations to serve in calibrating and optimizing the HPLC technique for quantification of these oligosaccharides. The optimization consisted of adjusting the eluent program and the CAD’s ion filter voltage, where ion voltage has an inverse relationship to response sensitivity. Once all the necessary standards were completed and methodology optimized, the selected neutral O-linked oligosaccharides derived from the CGL ligand were analyzed on the HPLC-CAD system to quantify the specific oligosaccharide constituents of interest. Separation, Fractionation and Isolation of X. laevis CGL Ligand Oligosaccharides Separation of CGL ligand oligosaccharide constituents was performed on a Hypercarb PGC (100 x 4.6 mm – 3µm particle size) HPLC column (Thermo Scientific, Waltham, MA) utilizing a gradient method consisting of an increasing percentage of acetonitrile from 5% to 35% over 45 minutes. The purified CGL ligand neutral oligosaccharide samples were reconstituted in 100% water for the Hypercarb PGC chromatographic analysis. Prepared oligosaccharide samples were transferred to 100 µL polyspring inserts and placed into 1.5 mL autosampler vials (National Scientific, Rockwood, TN). The flow rate was 0.800 mL/min and 10 µL injection volumes were used for each chromatographic analysis when separating and isolating the neutral oligosaccharides derived from the CGL ligands. 30 Fraction collections from the HPLC-CAD system were permitted by an analytical flow splitter (Grace Davison Discovery Science, Deerfield, IL) with a split ratio of 3:1. This split ratio allowed fraction collection of 75% of the sample while the other 25% was used for detection on the CAD instrument. Installation of the analytical flow splitter and its effects on operating efficiency were determined and compensated for, such as the flow rates and initial pressure in the HPLC-CAD system. Collection of oligosaccharide fractions was accomplished by an Agilent 1200 series fraction collector on a time-based trigger mode by accounting for lag times between the CAD and the fraction collection. The Agilent 1200 series fraction collector was interfaced with the Agilent 1100 series instrument. Selected peaks were collected and individual fractions were pooled together and centrifugally evaporated for subsequent HPLC-CAD quantitative analysis and competitive plate binding assays. Quantification and Secondary Purification of Selected CGL Ligand Oligosaccharides Selected X. laevis oligosaccharide fractions were isolated, corresponding to specific peaks and respectively pooled together throughout multiple chromatographic analyses on the Hypercarb PGC HPLC column. A secondary purification (as necessary) along with quantification of specific fractions was performed on the Prevail Carbohydrate ES column. Specific fractions that displayed more than one peak with significant peak area were selected to undergo a secondary purification on the Prevail Carbohydrate ES column. The different modes of separation and selectivity between the two HPLC columns provided further fraction purity as indicated by the presence of a 31 single oligosaccharide constituent. Pooled fractions from the Hypercarb PGC chromatographic runs were dried under a vacuum using centrifugation and subsequently reconstituted in a 50% acetonitrile/50% water solvent. Aliquots were removed from each selected fraction for HPLC-CAD quantification analysis and the remaining sample, if needed underwent a secondary round of purification performed in an identical manner as described in the previous section with regard to fractionation and isolation of the CGL ligand oligosaccharides. The quantification analysis was performed under identical conditions as described for the developed Prevail Carbohydrate ES HPLC gradient methodology. The purity and amount of oligosaccharide mass remaining within each respective fraction vial was determined and used in subsequent competitive plate binding assays. Procurement and Preparation of X. laevis Egg Jelly and CGL Egg jelly samples, enriched for CGL ligands, were obtained along with purified CGL prior to this research by Dr. Tom Peavy. CGL was biotinylated utilizing a Biotin Tag Micro Biotinylation Kit (Sigma-Aldrich, St Louis, MO). CGL in the amount of 0.37 mg (quantified as described below) was solubilized in 0.500 mL of 0.1 M NaHCO3, pH 8.4. To this, 13 µL of biotinamidohexanoic acid 3-sulfo-Nhydroxysuccinide ester (5 mg/mL in 30 µL DMSO and 970 µL of 0.1 M sodium phosphate buffer pH, 7.2 prepared fresh) was added at a molar ratio of 13:1. The resulting solution was incubated at 4°C for 2 hours with gentle agitation and subsequently dialyzed in 4 liters of TBS (10 mM Tris-HCl, 150 mM NaCl, pH 7.5). The 32 buffer was exchanged three times within a 24 hour period. Afterwards, the sample was removed from the dialysis bag and stored at -20°C. The CGL was quantified by a Bradford assay prior to and following the biotinylation procedure for determination of protein concentration using Bovine Serum Albumin (BSA) as the standard. BSA standards ranged from 0.1 to 1.4 mg/mL for all calibration curves and absorbance was measured at 595 nm. X. laevis egg jelly was quantified based on carbohydrate and protein concentration by a phenol-sulfuric acid assay using galactose as the standard and a Bradford assay, respectively [6,25]. The galactose standard used in the phenol-sulfuric acid assay was prepared at 1 µg/µL, in which calibration curves were generated in the range of 10 µg to 60 µg and absorbance was measured at 490 nm. SDS-PAGE Gel Characterization of X. laevis Egg Jelly and CGL Additionally, egg jelly preparation and CGL were further characterized by SDSPAGE analysis. A Bio-Rad Multi-Casting chamber and a Mini-Protean 3 Electrophoresis Module Assembly was used to cast all gels and conduct the electrophoresis runs, respectively (Hercules, CA). X. laevis egg jelly was analyzed on a 3.25% stacking gel (63.5% water/25% 0.5 M Tris-HCl pH 6.8/11% Acrylamide/Bis/1% SDS) and 7.5% resolving gel (48.5% water/25% 1.5 M Tris-HCl pH 8.8/25% Acrylamide/Bis/1% SDS). Egg jelly samples were heated for 10 minutes at 95°C in loading sample buffer prior to loading wells for a total loading sample volume of 100 µL. Egg jelly SDS-PAGE gels were run at 10 mA at 4°C until the tracking dye 33 approached the bottom of the gel. Gels were stained utilizing a thiosulfate-silver/Alcian blue staining procedure as described by Bonnell et al. (1999) [25]. Gels were fixated in 40% methanol/10% acetic acid for three 15 minutes incubations. Gels were then washed in 40% methanol for 10 minutes and soaked in 0.05% sodium thiosulfate for 45 seconds. Gels were rinsed in distilled water for 2 seconds and subsequently soaked in 0.12% silver nitrate for 5 minutes followed by another rinse with distilled water for 2 seconds. Gels were developed with 60 µL of 36.5% formaldehyde in 100 mL 3% sodium carbonate. The reaction was stopped with 20% acetic acid for 5 minutes. Finally, the gels were soaked in 0.05% Alcian blue in 40% methanol/10% acetic acid for 60 minutes and destained in 40% methanol/10% acetic acid overnight or until clear. CGL was analyzed on a 4% stacking gel (61% water/25% 0.5 M Tris-HCl pH 6.8/13% Acrylamide/Bis/1% SDS) and 10% resolving gel (41% water/25% 1.5 M TrisHCl pH 8.8/33% Acrylamide/Bis/1% SDS). CGL samples were heated for 10 minutes at 95°C in loading sample buffer prior to loading wells for a total loading sample volume of 50 µL. CGL gels were stained utilizing Coomassie Brilliant Blue stain (0.1% R250/46% methanol/7% acetic acid) for 1 hour and destained (40% methanol/10% acetic acid) until clear. The CGL gels were run at 50 mA for 90 minutes or until the tracking dye reached the bottom of the gel. All reagents used were electrophoretic grade and purchased from Fisher Scientific (Pittsburgh, PA). Bio-Rad broad range molecular weight standards (200 kDa – 6.5 kDa) were utilized for both egg jelly and CGL gel analyses. 34 Competitive Enzyme-Linked Lectin Assays Once isolation and quantification of the selected neutral CGL ligand oligosaccharide fractions were completed, further elucidation of these oligosaccharides and their role in the block to polyspermic fertilization were investigated by a competitive enzyme-linked lectin assay (ELLA). These competitive plate binding assays were based on previous protocols utilized in the detection and disruption of the CGL-ligand binding, where sensitivity in detection of the CGL ligand was demonstrated to be at 1-2 ng/mL [11,12]. Initial tittering and optimization of the enzyme-linked lectin assays were performed utilizing a standard dilution series approach of the biotinylated CGL and ExtrAvidin Peroxidase conjugate and incorporating selected monosaccharide and disaccharide inhibitors as positive and negative controls, respectively. The tittering consisted of a starting concentration of 10 µg/mL and 5 µg/mL of biotinylated CGL and ExtrAvidin Peroxidase, respectively. Serial dilutions of the biotinylated CGL were performed from 10 µg/mL to 0.04 µg/mL across columns 1 through 10 which were incubated with a fixed concentration of ExtrAvidin Peroxidase at 5 µg/mL. Serial dilutions of ExtrAvidin Peroxidase were performed from 5 µg/mL to 0.08 µg/mL down rows A through H which were incubated with a fixed concentration of biotinylated CGL at 10 µg/mL. Monosaccharide and disaccharide controls were selected based on previous research involving the binding specificity of the CGL. Selected monosaccharides included galactose, glucosamine, glucose and fucose. Selected 35 disaccharides consisted of maltose, lactose, lactulose, sucrose and melibiose. All monosaccharides and disaccharides were purchased from Sigma-Aldrich (St. Louis, MO) with the exception of lactulose, which was purchased from ACROS organics (New Jersey, USA). Egg jelly test samples (500 ng carbohydrate/well) were bound to an Immulon 4HBX ultra-high binding 96 well flat bottom polystyrene microtiter plate (Thermo Scientific, Waltman, MA) in 100 µL of 100 mM Na2CO3, pH 9.5 at 4°C overnight. The plate was washed three times with CTBST dilution/wash buffer (10 mM Tris-HCl, 150 mM NaCl, 10 mM CaCl2, 0.05% Tween 20, pH 7.5). Blocking buffer (10 mM TrisHCl, 150 mM NaCl, 3% BSA, 0.05% Tween, pH 7.5) was added for 30 minutes to 1 hour at room temperature. Biotinylated CGL, 0.74 mg/mL was diluted to 0.75 µg/mL with dilution/wash buffer and a 100 µL aliquot was added to each well and incubated for 1 hour at 25°C. Selected inhibitors (monosaccharides, disaccharides, isolated/quantified CGL ligand oligosaccharide fractions and SPE derived neutral and acidic whole CGL ligand oligosaccharide fractions) were solubilized in CTBST and included during the biotinylated CGL incubation to assess inhibitive properties. The excess biotinylated CGL was removed by washing three times with dilution/wash buffer, followed by an additional blocking step as described above. A 100 µL aliquot of 0.2% (v/v) ExtrAvidin Peroxidase conjugate was diluted to 500 ng/mL in dilution/wash buffer and added to each well and incubated for 1 hour at 25°C. The excess ExtrAvidin Peroxidase conjugate was removed by washing three times with dilution/wash buffer. 36 Following the washing procedure, 100 µL of TMB (3,3’,5,5’-tetramethylbenzidine) Blue (Lab Vision, Fremont, CA) substrate was added to all wells and incubated for 1020 minutes. The chromophore, which was cleaved by the enzyme conjugate, was developed and measured at 630 nm using an Opsys MR (DYNEX Technologies, Chantilly, Virginia) microplate reader. TMB Blue product formation measured at an optical density (OD) of 630 nm is directly proportional to the binding activity of the CGL to its ligand partners contained in the egg jelly. 37 RESULTS Quantification of Oligosaccharides To investigate the functional role of Xenopus laevis CGL ligand oligosaccharides in the block to polyspermic fertilization, a novel method for quantification of biologically relevant oligosaccharides was developed. The quantification methodology was developed without derivatization agents or exact standards utilizing the HPLC-CAD system. The HPLC-CAD system demonstrated excellent sensitivity, separation and a relatively uniform response in the analysis of surrogate oligosaccharide standards ranging from a degree of polymerization (DP) of one to eight (glucose to maltooctaose) and 6-O-α-maltosyl-β-cyclodextrin, respectively (Figure 4). 38 15.390 500 17.748 14.210 12.953 11.575 600 10.040 8.507 5.930 7.109 ADC1A, ADC1CHANNELA(NOAH\052009000002.D) mV 400 300 200 100 DP 1 DP 2 2 4 6 DP 3 8 DP 4 10 DP 5 DP 6 12 DP 7 DP 8 14 16 18 min Figure 4 – A gradient method chromatogram comprising a mixed linear oligosaccharide standard (glucose to maltooctaose at retention times of 5.930 through 15.390 minutes) and 6-O-α-maltosyl-β-cyclodextrin (last peak at 17.748 minutes) at 25 µg/mL. 39 Multiple surrogate oligosaccharide analyses were performed and calibration curves were generated from each linear glucose oligomer and the cyclodextrin standard throughout their respective concentrations (Figure 5). It is noteworthy to point out that maltosyl-β-cyclodextrin was utilized as an additional surrogate oligosaccharide standard despite its structural dissimilarity to the other glucose oligomers. This was deemed necessary in order to extend the quantification calibration curves to accommodate the quantification of the larger biological test oligosaccharide structures. Although it would have been preferred, a linear glucose oligomer possessing a degree of polymerization (DP) of nine was not commercially available therefore this compound was selected in an effort to substitute for the projected retention time that a linear DP 9 would possess. A non-linear calibration scheme was generated and utilized since the response of the surrogate standards did not display a true linear relationship utilizing the traditional linear equation (y = mx + b). Therefore, response curves were fitted utilizing a power-fit model: y = ACb Where y is the peak area, C is the concentration in µg/mL, and ‘A’ and ‘b’ values are fixed parameters that are derived from the calibration power-fit equations. The non-linear relationship is observed utilizing the power-fit model as well, demonstrated by ‘b’ terms (power variable) possessing values significantly greater than 1.0 (Figures 5 and 7). Although the three standards highlighted in figure 5 display R 2 40 values of 1.0, these values were rounded from 0.999 and the R2 range of all nine standards was 0.993 to 0.999 (Figure 5). 41 Gradient Calibration Plot 12000 10000 Maltotetraose 8000 y = 288.31x1.1049 R2 = 1 Glucose y = 325.61x1.0474 R2 = 1 Maltose Peak Area Glucose y = 292.18x R2 = 1 Maltotriose Maltotetraose 1.0836 Maltopentaose 6000 Maltohexaose Maltosyl-β-cyclodextrin Maltoheptaose Maltooctaose 4000 Maltosyl-cyclodextrin 2000 0 0 5 10 15 20 25 30 Concentration (ug/mL) Figure 5 – Representative plot of peak area to concentration relationship. Power-fit calibration equations derived from throughout the prepared concentration range (1, 4, 10 and 25 µg/mL) for glucose (DP 1), maltotetraose (DP 4) and 6-O-α-maltosyl-βcyclodextrin. 42 Therefore, a correlation between ‘A’ and ‘b’ terms and retention times were applied as the appropriate quantification calibration terms (Figures 6 and 7). Each individual surrogate oligosaccharide ‘A’ and ‘b’ values, collectively obtained from 1 through 25 µg/mL concentrations, were plotted from the power-fit calibration equations (Figure 5) with respect to retention time (Figures 6 and 7). ‘A’ and ‘b’ parameters showed definitive trends as a function of retention time, allowing the prediction of calibration parameters for test and unknown oligosaccharides of interest. 43 Figure 6 – ‘A’ terms derived from the surrogate oligosaccharide standards and corresponding 2nd order polynomial curve relative to retention time. ‘A’ values for glucose (325), maltotetraose (288) and maltosyl-β-cyclodextrin (292) are highlighted. 44 Figure 7 – ‘b’ terms derived from the surrogate oligosaccharide standards and corresponding 2nd order polynomial curve relative to retention time. ‘b’ values for glucose (1.047), maltotetraose (1.105) and maltosyl-β-cyclodextrin (1.084) are highlighted. 45 Figures 6 and 7 demonstrate that changes in sensitivity and linearity (‘A’ and ‘b’ terms) changed relativity smoothly with a change in retention time, allowing the use of equations to fit the variation of ‘A’ and ‘b’ terms with retention time. While the R 2 values were less than 1.0 (Figures 6 and 7), the range in both ‘A’ and ‘b’ values is not very large, displaying ranges of 230 to 340 and 1.05 to 1.13, respectively. The overall objective of this developed quantification scheme was to accurately determine concentrations of unknown oligosaccharides and in particular X. laevis CGL ligand oligosaccharides. Thus, employing this non-linear calibration scheme, an unknown sample lying within the surrogate oligosaccharide standard range is based on observed retention time and peak area along with ‘A’ and ‘b’ fixed parameters (‘A’ and ‘b’ terms are determined for unknown compounds by using the unknown compounds’ retention time together with the 2nd order polynomial fit equations given in Figures 6 and 7) as determined from standards (Figures 6 and 7) using the following equation: C = (y/A) 1/b Prior to oligosaccharide HPLC-CAD analyses, all commercially available oligosaccharide standards (i.e. surrogate and biological test standards) in large enough quantities were prepared by weighing out the required mass on an analytical balance (mg or µg) to create a stock solution, from which appropriate dilutions were performed. Although preferred, it was not possible to weigh out some of the test oligosaccharides since the commercially available amount was only in the tens of micrograms. Therefore 46 in these circumstances, the amount of mass determined by the manufacturer was utilized in concentration calculations. Selected dilutions were then transferred to sampling vials for ensuing HPLC-CAD analysis (Figure 4). Additionally, purity of each standard, as reported by the manufacturer, was compensated for in all final calculations. Employing this non-linear calibration scheme, surrogate oligosaccharide standards displayed very low average percent errors to within 5% (excluding maltooctaose) and excellent reproducibility (Figure 8). Furthermore, a relatively uniform distribution with regard to variation in instrument response throughout each surrogate oligosaccharide standard was observed. With regard to average percent error, six of the surrogate oligosaccharide standards displayed positive values, while two displayed negative values. There were no correlative relationships between the degree of polymerization and the average percent error or standard deviation. Interestingly, maltooctaose displayed the poorest response in average percent error, however the reproducibility was excellent (-10.7 +/- 1.51). 47 Surrogate Oligosaccharide Standards 35 15 -35 al to te tr a os e M al to pe nt os e M al to he xo se M al to he pt ao se M al to oc M ta al os to e sy l-c yc lo de xt r in -25 M M M -15 al to se -5 al to tr i os e 5 G lu co se Average Percent Error 25 Figure 8 – The mean and standard deviation for three separate trials of surrogate standards are shown (one trial excluded the maltotetraose data due to contamination). Non-linear calibration terms used for concentration calculations were based on 10 µg/mL test samples. 48 Once accurate and precise quantification was achieved by the non-linear calibration scheme for the surrogate oligosaccharide standards under optimized conditions, four short chain oligosaccharide structures were tested. These short chain oligosaccharides consisted of three trisaccharides (isomaltotriose, raffinose and melezitose) and a tetrasaccharide (stachyose), which were utilized in testing the developed quantification methodology (Figure 9). 49 Isomaltotriose Melizitose Stachyose Raffinose Figure 9 – Short chain oligosaccharide structures analyzed by the developed HPLCCAD methodology. 50 Collectively, accurate quantification to within less than 11% average error was obtained, however the reproducibility was more variable relative to the surrogate oligosaccharide standards (Figure 10). Isomaltotriose and raffinose produced comparable responses and variations of -10.8 +/- 7.07 and -10.2 +/- 8.18, respectively. Conversely, stachyose and melezitose produced similar responses and variations of 1.58 +/- 13.7 and -3.81 +/- 11.9, respectively; however the variation was greater relative to isomaltotriose and raffinose. Increased variance was observed with regard to the quantification analysis of the initial short chain test oligosaccharides in relation to the surrogate oligosaccharide standards (Figure 8); however a definitive range of variation, in excellent agreement to that in Figure 10, was established for each initial test standard by previous work performed under both the isocratic and gradient conditions used for quantification methodologies. In brief, the developed quantification methodologies consisted of isocratic and gradient conditions where the mobile phase remained constant or changed gradually over time throughout the chromatographic runs, respectively (data not shown for the isocratic method but the method is described in the materials and methods section). The gradient solvent conditions affected the elution of samples from the HPLC column as compared to the isocratic method, and thus the retention times and distribution of peak areas were significantly different. The gradient method demonstrated superiority to the isocratic method in the chromatographic analysis of oligosaccharides due to the decrease of retention times for later eluting peaks, thus 51 providing sharper peak shapes while the signal-to-noise ratio in later eluting peaks was greatly improved. Therefore, all data collected with regard to the quantification analysis of oligosaccharide standards (with the exception of LNFP II and LNH, which were quantified by both developed methodologies) and with regard to the neutral oligosaccharides derived from the CGL ligand glycoprotein were analyzed by the developed gradient methodology. 52 Initial Test Oligosaccharide Standards 35 Average Percent Error 25 15 5 -5 Isomaltotriose Stachyose Raffinose Melezitose -15 -25 -35 Figure 10 – The mean and standard deviation for three separate trials of initial test standards are shown. Non-linear calibration terms used for concentration calculations were based on 10 µg/mL test samples. 53 Once a defined set of parameters were determined that optimized accuracy and reproducibility of the test oligosaccharides, oligosaccharides more representative of biological structures found on glycoproteins were analyzed by the developed HPLCCAD quantification methodology (Figure 11). Seven oligosaccharide structures of varying complexity were analyzed by the developed HPLC-CAD quantification methodology (Figures 11 and 12). These core and branched oligosaccharide structures are characteristic of typical O- and N-linked oligosaccharides found on biological proteins and thus were selected as biological test standards. O-linked oligosaccharides are characterized by the addition of sugars to the hydroxyl (OH) groups of selected serine or threonine side chains, whereas N-linked oligosaccharides are conjugated to amine (NH2) groups on asparagine amino acids which occur in the tripeptide sequence Asn-X-Ser or Asn-X-Thr (where X can be any amino acid except proline). 54 Galβ1-4GlcNAcβ1 6 Galβ1-4GlcNAcβ1-2Manα1 Manα1 2 Galβ1-4GlcNAcβ1 6 6 Manβ1-4GlcNAcβ1-4GlcNac Manβ1-4GlcNAcβ1-4GlcNAc Galβ1-4GlcNAcβ1 3 3 Galβ1-4GlcNAcβ1-2Manα1 4 Manα1 2 Asialo, galactosylated, biantennary oligosaccharide (NA2) Galβ1-4GlcNAcβ1 Asialo, galactosylated, tetraantennary oligosaccharide (NA4) Galβ1-4GlcNAcβ1 Manα1 6 6 Galβ1-4Glc Manβ1-4GlcNAcβ1-4GlcNac 3 Galβ1-3GlcNAcβ1 3 Manα1 Lacto-N-hexaose (LNH) Fucα1 I 3 Galβ1-4GlcNAcβ1 I 6 Fucα1 Galβ1-4Glc I 3 4 I Galβ1-4GlcNAcβ1 Oligomannose 3 (MAN-3) Galβ1-3GlcNAcβ1-3Galβ1-4Glc I Fucα1 Lacto-N-Fucopentaose (LNFP II) Lactodifucotetraose (LDFT) Figure 11 – Subset of branched oligosaccharide structures representative of typical Oand N-linked oligosaccharide moieties found on glycoproteins, which were analyzed by the developed HPLC-CAD quantification methodology. 55 Collectively, accurate quantification to within less than a 19% average error was obtained along with comparable variance to the initial test oligosaccharide standards (Figures 10 and 12). There were no correlative relationships between core oligosaccharides (MAN-3 and LNH) and complex high-mannose type oligosaccharides (NA2 and NA4) with regard to absolute average percent errors (7.31 vs. 6.99), however standard deviations increased as complexity increased (4.1 vs. 11.6). Structures containing residues found to exist in the CGL ligand oligosaccharides by NMR and MS [19,21,22] such as core glycoprotein oligosaccharide N-acetylglucosamine structures with terminal fucose residues (LDFT) and N-acetylglucosamine structures with terminal fucose and galactose residues (LNFP II), displayed very low average percent errors and high-quality reproducibility (6.63 +/- 8.51 and 3.46 +/- 3.69, respectively). Mannopentaose, a five-chain high-mannose structure fragment commonly found among N-linked oligosaccharides displayed excellent reproducibility (-14.3 +/- 3.78). Notably, both NA2 and NA4 displayed the greatest range in variance 18.4 +/- 7.37 and -4.42 +/15.9, respectively. 56 Biological Test Oligosaccharide Standards 35 15 II* * FP H* LN an no pe n M -25 LN ta os e* * FT LD NA 4* -15 NA 2* -5 AN -3 * 5 M Average Percent Error 25 -35 Figure 12 – Results of biological test standards representing typical branched oligosaccharides present on glycoproteins. The mean and standard deviation for three separate trials of biological test standards are shown (two separate trials are shown for LNFP II and LNH). Non-linear calibration terms used for concentration calculations were based on 10 µg/mL test samples. * Based on assumed weight from manufacture. ** Normalized as a result of manufacturer error in sample quantity verified by freeze dry gravimetric analysis. 57 An even distribution and impartial response from the HPLC-CAD system with regard to specific biological test structures was observed (Figure 12). With regard to average percent error, three of the biological test standards displayed positive values, while four displayed negative values. Taken together, surrogate, short chain and biological test oligosaccharide standards were quantified to within less than a 19% average error with excellent reproducibility by the developed HPLC-CAD methodology (Figures 8, 10 and 12). Profiling, Selection and Isolation of CGL Ligand Neutral Oligosaccharides Initial characterization of the CGL ligand neutral oligosaccharides was performed employing the Prevail Carbohydrate ES HPLC column (Figure 13 and Table 1). These chromatographic runs were intended to profile CGL ligand oligosaccharides and to subsequently isolate some of the major oligosaccharide constituents. Due to an unstable/elevated baseline, injection volumes exceeding column capacity limited the ability to resolve oligosaccharides. Thus, a Hypercarb PGC HPLC column was substituted for subsequent profiling and isolation of the CGL ligand neutral oligosaccharides as described in materials and methods. However, the Prevail analysis demonstrated the presence of approximately 17 oligosaccharide peaks. Both profiles display four major oligosaccharide peaks, however a specific major oligosaccharide peak observed on the Prevail column is not correlative to a specific major oligosaccharide peak observed on the Hypercarb column as a result in their differences in separation/selectivity mechanisms (Figures 13 and 14). 58 Table 1 – Initial characterization and profiling of the CGL ligand neutral oligosaccharides on the Prevail Carbohydrate ES HPLC column. Estimated concentration of the major oligosaccharide peaks are shown along with associated calibration terms. Retention Time (minutes) 7.485 9.061 11.455 12.660 14.377 16.533 17.577 18.663 18.696 20.545 21.693 21.721 23.517 24.409 25.584 28.114 29.685 31.298 32.619 Peak Area ‘A’ Term ‘b’ Term 339 535 2971 2769 928 374 777 1220 1630 1779 1065 1320 653 398 619 1914 1385 3548 372 316 296 274 268 264 267 272 280 280 298 313 314 342 359 383 445 490 541 587 1.08 1.10 1.12 1.12 1.12 1.11 1.11 1.09 1.10 1.07 1.05 1.05 1.01 0.99 0.95 0.88 0.82 0.75 0.70 Predicted Concentration (µg/mL) 1.07 1.72 8.42 8.00 3.06 1.35 2.58 3.84 5.00 5.32 3.22 3.95 1.90 1.11 1.65 5.30 3.56 12.15 0.52 Percentage of Oligosaccharide Mass 1.45 2.33 11.42 10.85 4.15 1.83 3.50 5.21 6.78 7.22 4.37 5.36 2.58 1.51 2.24 7.19 4.83 16.48 0.71 59 The Hypercarb analysis demonstrated the presence of approximately 20 oligosaccharide peaks which was comparable to the Prevail chromatogram and taken together, these HPLC profiles illustrate the abundance and complexity of CGL ligand oligosaccharides consistent with previous NMR and MS studies [19,21,22]. Employing the Hypercarb PGC column, CGL ligand oligosaccharide constituents that displayed the greatest peak area (greatest overall oligosaccharide mass) and good baseline resolution were targeted for fractionation and isolation (Figure 14 and Table 2). Since oligosaccharide standards and subsequent calibration curves were not performed with the PGC Hypercarb column, estimation of their concentrations could not be determined. Although the separation mechanism between the Prevail Carbohydrate ES HPLC and the Hypercarb PGC HPLC column differ significantly, the chromatographic profiles are reasonably comparable with regard to the number of major oligosaccharide peaks and their abundance. The separation mechanism of the Prevail column functions under normal phase characteristics, exploiting hydrophilic interactions for the primary basis of interaction. The Hypercarb PGC column on the other hand possess a unique separation/selectivity mechanism based on a polar retention effect on graphite producing a highly efficient separation of polar compounds of structural similarity. 60 mV 2.419 ADC1A, ADC1CHANNELA(NOAH\021909000001.D) 11.455 12.660 225 31.298 29.685 28.114 23.516 24.538 25.585 20.545 21.721 14.377 100 9.059 7.487 125 16.5 .662 3 17.762 18.696 150 32.617 175 34.104 200 75 50 5 10 15 20 25 30 35 min Figure 13 – Prevail Carbohydrate ES HPLC chromatogram of a 1 µL injection of X. laevis CGL ligand neutral O-linked oligosaccharides. Gradient method consisted of a water/acetonitrile mobile phase with a decreasing percentage of actonitrile from 65% to 50% over 40 minutes. 61 Figure 14 – Hypercarb PGC HPLC chromatogram of a 10 µl injection of X. laevis CGL ligand neutral oligosaccharides. Gradient method consisted of a water/acteonitrile mobile phase with an increasing percentage of acetonitrile from 5% to 35% over 45 minutes. * Indicates peaks that were fraction collected. 62 Table 2 – HPLC-CAD profile of X. laevis CGL ligand oligosaccharides comprising all targeted major peaks and their relative abundance. Fraction Retention Time (minutes) Peak Area 1 * * 2 3 10.428 11.596 12.983 14.150 26.420 1986 1056 3438 2391 2302 Estimated Percentage of Oligosaccharide Mass (Based on Peak Area) 12 6 20 14 13 63 It is notable to point out that the initial large broad peak observed in the X. laevis Prevail chromatogram (Figure 13) has been attributed to unretained non-oligosaccharide material derived from the PGC-SPE purification procedure and stationary phase degradation. This identical HPLC profile constituting this large abrupt peak was observed employing a PGC-SPE blank and to a lesser extent an HPLC solvent blank which accounted for all solvents, any stationary phase degradation and salts involved with the SPE and HPLC procedures. Some of these unretained peaks were attributed to autosampler vials and associated cap debris. Therefore, in an effort to focus on the oligosaccharide profiles, all subsequent HPLC figures have been fitted to exclude the large abrupt peak consisting of this unretained material (Figures 13 and 14). Figures 15 and 16 were fitted in the same manner for a different reason based on experimental observations during the lyophilization procedure of the CGL ligand oligosaccharide fractions. During this procedure, it was observed that the sample vials selected were incompatible with the lyophilization apparatus, which caused minor etching of the centrifudge lid, which subsequently caused unretained shards of plastic to enter the sample vials. This unretained material produced an initial large abrupt peak, similar to that observed in Figure 13 (however to a lesser extent) in all chromatograms analyzing the collected fractions. Therefore, employing a lyophilization control for the isolated fractions in Figures 15 and 16 a blank subtraction method was utilized for purity and concentration analysis. 64 The PGC Hypercarb CGL ligand oligosaccharide peaks displaying retention times of 10.428, 14.150 and 26.420 minutes (fractions 1 through 3, respectively) were selected for isolation, fractionation and subsequent quantification for plate binding assays since they fit the following criteria: major peaks, good baseline resolution and minimal interference by overlapping compounds (Figure 14 and Table 2). Initially, two additional major oligosaccharide peaks were targeted (with a retention times of 11.596 and 12.983) however subsequent analysis via a secondary purification resulted in multiple oligosaccharide peaks on the Prevail Carbohydrate ES HPLC column. Resolution of any predominate components within these oligosaccharide aggregates to homogeneity was difficult given the amount of starting material; thus, adequate mass for subsequent biological assays was projected to be unattainable. As a consequence, attempts to isolate these oligosaccharide peaks were abandoned. Selected CGL ligand oligosaccharides were isolated by collecting fractions at the specified time intervals relative to their maximum peak. By means of conducting numerous rounds of chromatographic runs, an adequate amount of each oligosaccharide fraction was collected for subsequent analysis and secondary purification (if deemed feasible and necessary). This was accomplished by utilizing an analytical flow splitter which was interfaced with a fraction collector, whereby 75% of the sample was collected and the remaining 25% was consumed in the HPLC-CAD detection. 65 Quantification of Selected CGL Ligand Oligosaccharide Constituents Prior to quantification analysis, purified CGL ligand oligosaccharides were run in parallel to the surrogate quantification standards on the Prevail Carbohydrate ES HPLC column to ensure complete coverage of the overall X. laevis CGL ligand oligosaccharide mass (Figure 15). 66 ADC1 A, ADC1 CHANNEL A (NOAH\021909000002.D) VWD1 A, Wavelength=205 nm (NOAH\021909000002.D) ADC1 A, ADC1 CHANNEL A (NOAH\021909000001.D) VWD1 A, Wavelength=205 nm (NOAH\021909000001.D) 10 34.104 32.617 31.298 32.677 28.761 29.685 28.114 25.585 23.516 24.538 21.721 20.545 15 39.376 39.408 18.501 17.762 16.562 16.663 14.377 12.676 11.250 50 4.843 100 9.120 9.059 7.487 150 18.696 200 12.660 11.455 250 24.420 19.509 300 35.679 14.652 350 10.477 7.453 mV 20 25 30 35 min Figure 15 – Prevail Carbohydrate ES HPLC chromatogram overlay of surrogate oligosaccharide quantification standards (glucose to maltooctaose at retention times of 7.453 through 35.679) and X. laevis CGL ligand oligosaccharide profile (displaying retention times of 7.487 through 34.104). Gradient method consisted of a water/acetonitrile mobile phase with a decreasing percentage of actonitrile from 65% to 50% over 40 minutes. 67 The developed HPLC-CAD quantification methodology was applied to the selected neutral CGL ligand O-linked oligosaccharide fractions as described previously. CGL ligand oligosaccharide fractions (fractions 1 through 3) were reconstituted to produce approximate fraction concentrations at 10 µg/mL, thus allowing accurate quantification by the non-linear calibration scheme. Additionally, utilizing a blank subtraction method, to account for any SPE or intrinstic HPLC contaminates as discussed previously, purity of each CGL ligand oligosaccharide fraction was determined (Figures 16 and 17). 68 *ADC1A, ADC1CHANNELA(NOAH\060209000007.D- NOAH\060209000002.D) 6.879 mV 250 200 150 100 50 0 6 8 10 12 min 14 A. Fraction 1 with associated CAD signal. *ADC1A, ADC1CHANNELA(NOAH\060209000009.D- NOAH\060209000002.D) 7.157 mV 300 250 200 150 100 50 0 6 8 10 12 14 16 min 18 min B. Fraction 2 with associated CAD signal. *ADC1A, ADC1CHANNELA(NOAH\060209000011.D- NOAH\060209000002.D) 12.994 mV 200 150 100 6.355 50 0 8 10 12 14 16 C. Fraction 3 with associated CAD signal. Figure 16 – Prevail Carbohydrate ES HPLC chromatogram purity and quantification analysis utilizing a blank subtraction method with manual integration for fractions 1 through 3 (from A to C panels, respectively). Fractions 1, 2 and 3 correspond to retention times of 10.428, 14.150 and 26.420 on the Hypercarb HPLC column. 69 Additionally, fractions 1 through 3 were measured by UV for the presence of Nacetyl groups of the hexosamine residues of the isolated oligosaccharides at 205nm (Figure 17). The UV signals generated for fractions 1 through 3 indicate the presence of N-acetyl groups within these oligosaccharide fractions, thus further corroborating the presence of oligosaccharide components in agreement with that of the CAD signal (Figure 16). In addition to the CAD signal, the UV data demonstrated a single predominate oligosaccharide component for fractions 1 through 3. Collectively, the UV and CAD data demonstrate the absence of any significant additional interfering oligosaccharide components within the isolated and quantified CGL ligand oligosaccharide fractions 1 and 2. However, fraction 3 did contain an additional, yet significant oligosaccharide component, Figure 16C at observed retention time of 12.994 minutes. 70 *VWD1A, Wavelength=205nm(NOAH\060209000007.D- NOAH\060209000002.D) mAU 6.705 5 4 3 2 1 0 5 6 7 8 9 10 12 min 11 A. Fraction 1 with associated UV signal. *VWD1A, Wavelength=205nm(NOAH\060209000009.D- NOAH\060209000002.D) mAU 6.981 6 5 4 3 2 1 0 -1 6 7 8 9 10 11 min B. Fraction 2 with associated UV signal. *VWD1A, Wavelength=205nm(NOAH\060209000011.D- NOAH\060209000002.D) 12.805 mAU 3 2.5 2 1.5 1 0.5 0 -0.5 10 11 12 13 14 15 16 min C. Fraction 3 with associated UV signal. Figure 17 – Prevail Carbohydrate ES HPLC chromatogram of UV signals for fractions 1 through 3 (from A to C panels, respectively). 71 The isolated CGL ligand fractions were respectively pooled together and subsequently lyophilized (freeze dried). The lyophilized powder was reconstituted in volumes that yielded approximately 10 µg/mL concentrations in efforts to provide an accurate quantification analysis utilizing the middle portion of the calibration curve. Aliquots were removed and subjected to the developed HPLC-CAD quantitative analysis scheme. Based on the concentrations produced from the quantification analysis of the removed aliquots, total mass of the reconstituted vials was calculated. The remaining volume containing known oligosaccharide mass was then lyophilized again for forthcoming biological assays. Overall, the successful isolation of hundreds of nanograms to microgram quantities along with quantification and purity greater than 85% of the three fractions was achieved with the initial separation and isolation by the Hypercarb PGC HPLC column (Table 3). Utilizing a blank subtraction method, fractions 1 and 2 demonstrated excellent purity (> 90%), while fraction 3 had a significant amount of an additional oligosaccharide component. Thus, fraction 3 was subsequently enriched for the major oligosaccharide component via a secondary purification (see materials and methods) to attain approximately 92% purity. 72 Table 3 – CGL ligand oligosaccharide fractions with corresponding concentrations as determined by the developed HPLC-CAD quantification methodology and oligosaccharide mass isolated, accounting for removed quantification aliquots and estimated purity. * Fraction containing significant additional oligosaccharide components and subjected to a secondary purification. Fraction Retention Time (minutes) 1 2 3 6.879 7.157 12.994 Predicted Concentration (µg/mL) 9.11 13.1 10.34 Mass Collected (µg) Estimated Purity (%) 1.53 2.06 0.567 96 90 92* 73 Characterization of X. laevis Egg Jelly and CGL Fertilization Constituents Prior to biological assays involving the isolated and quantified CGL ligand oligosaccharides, characterization of the X. laevis fertilization constituents (i.e. egg jelly and CGL) involved in the block to polyspermic fertilization were analyzed by means of SDS-PAGE gel analysis. X. laevis egg jelly (extracted and enriched for CGL ligands by Dr. Peavy) was separated and selectively stained for the sulfated CGL ligands utilizing a thiosulfate silver/Alcian blue staining protocol as described by Bonnell et al. (Figure 18) [25]. The SDS-PAGE analysis of the egg jelly preparation demonstrates the presence of two heavily glycosylated, high-molecular weight components greater than 200 kDa which stained intensely for the Alcian blue dye and appeared blue on the gel (lane 2). As a reference, lane 3 contains dextran sulfate, a high-molecular weight sugar polymer possessing charged sulfated residues exhibiting a molecular weight range in excess of 500 kDa. The dextran sulfate contained in lane 3 also stained intensely for the Alcian blue dye and appeared blue on the gel. This work corroborates previous findings by Bonnell et al., which meticulously demonstrated the presence of two high-molecular weight glycoconjugates within the J1 egg jelly component possessing molecular weights of 450 kDa and 630 kDa by means of Alcian blue staining (Figure 18) [6,25]. Taken together, the current study, along with previous research are in agreement in demonstrating the two CGL ligand glycoproteins of interest, exhibiting molecular weights of ~ 450 kDa and ~ 630 kDa are present in the egg jelly (Figure 18 lane 2). Additionally, previous SDS-PAGE analyses of the egg jelly extract demonstrated the 74 presence of multiple jelly components in addition to the two CGL ligands [25]. Figure 18 demonstrates the absence of these additional jelly components demonstrating the preparation is highly enriched for the CGL ligands. 75 200 kDa 116 kDa 97 kDa 66 kDa 45 kDa 31 kDa 1 Molecular Weight Standards 2* X. Laevis Egg Jelly 3* Dextran Sulfate Figure 18 – Thiosulfate-silver/Alcian blue staining of a 7.5% SDS-PAGE gel comprising X. laevis egg jelly illustrating the presence of the CGL ligands (lane 2) and as a reference, dextran sulfate (lane 3). Lane 1 contains 10µL of broad range molecular weight protein standards (myosin, 200,000; β-galactosidase, 116,000; phosphorylase b, 97,000; serum albumin, 66,000; ovalbumin, 45,000; and carbonic anhydrase, 31,000). Lane 2 contains 44 µg of X. laevis egg jelly extract (enriched for the CGL ligands) based on carbohydrate content and lane 3 contains 5 µg of dextran sulfate (> 500,000). * In addition to staining for silver, these lanes stained intensely for Alcian blue and appeared blue on the gel. 76 X. laevis CGL has been isolated and well characterized from chemical analysis to be a metalloglycoprotein, composed of 84% protein, 15.8% carbohydrate and 0.19% calcium [9]. Additionally, the CGL metalloglycoprotein is composed of 10-12 subunits which form a tertiary structure composed of non-covalently bound monomers with identical polypeptide backbones [36]. These 10-12 subunits form an oligomeric complex comprising a molecular weight of approximately 450 kDa whereas the monomeric subunit size is between 46-58 kDa [9,36]. In this work, purified X. laevis CGL (provided by Dr. Peavy) was biotinylated (refer to materials and methods) in an attempt to provide a sensitive detection method for subsequent biological binding assays involving the isolated and quantified CGL ligand oligosaccharides [11,12]. Figure 19 is an SDS-PAGE gel image consisting of purified CGL (lane 2) and biotinconjugated CGL (lane 4) for comparison purposes. Lane 2 contains the native CGL possessing an apparent molecular weight of approximately 47-55 kDa in agreement with previous work [9,15,36] It has been postulated that microheterogeneity in CGL glycosylation is the cause for the observed broad diffuse bands in SDS-PAGE separations of the CGL. This heterogeneity appears to be due to variation in N-linked glycosylation since PNGaseF (enzyme that cleavages off N-linked oligosaccharides from the asparagine residue) treatment results in a single distinct CGL band [15,36]. The molecular weight of the CGL polypeptide chain after deglycoslyation by SDS-PAGE was found to be 39 kDa [9,15,36]. Comparison between the native CGL and the biotinylated CGL via SDS- 77 PAGE analysis, demonstrates a modest increase in molecular weight of the native CGL as a result of the incorporated biotinylation reagent (Figure 19 lane 2 vs. 4) as indicated by an upward shift in band migration. 78 200 kDa 116 kDa 97 kDa 66 kDa 45 kDa 31 kDa 1 Molecular Weight Standards 2 Native CGL 3 4 Biotinylated CGL Figure 19 – Coomassie Brilliant Blue staining of a 10% SDS-PAGE gel comprising X. laevis native CGL (lane 2) and biotinylated CGL (lane 4). Lane 1 contains 10µL of broad range molecular weight protein standards (myosin, 200,000; β-galactosidase, 116,000; phosphorylase b, 97,000; serum albumin, 66,000; ovalbumin, 45,000; and carbonic anhydrase, 31,000). Lane 2 contains 7µg of native X. laevis CGL and lane 4 contains 9µg of biotinylated CGL. 79 Competitive Enzyme-Linked Lectin Assays (ELLA) and CGL Binding Specificities After obtaining the preparations of the X. laevis egg jelly ligands, isolated oligosaccharides and biotinlyated CGL, a plate binding assay (ELLA) was developed based on the modification of methodology utilized in previous studies [11,12]. In brief, the refined ELLA was set-up by coating the wells of a 96-well plate with the preparation of X. laevis egg jelly ligands, blocking all other available binding sites, and then subsequently incubating with biotinlyated CGL. During the biotinlyated CGL incubation period, potential inhibitors of the CGL-ligand binding interaction were included in the binding buffer to measure the relative inhibition of biotinlyated CGL bound to ligand. This is in essence a competitive inhibition binding assay such that if a particular sugar (or oligosaccharide) inhibits CGL binding, then it is assumed to be competing with the ligand oligosaccharides for the binding pocket. After the incubation period (with or without test inhibitors), the relative amount of biotinylated CGL bound to the ligand was detected by secondary incubation with an avidin-peroxidase enzyme conjugate which forms a biotin-avidin complex. The amount of avidin-peroxidase enzyme bound is then measured by using a peroxidase substrate that when cleaved will be colorimetrically detected. Since similar plate binding assays have been performed on CGL (albeit using different reagents that are predicted to be less sensitive for detection purposes), the optimal binding conditions with respect to the specific buffer and salt composition (10mM Tris-HCl, 150mM NaCl, 10mM CaCl2, 0.05% Tween 20, pH 7.5) were adapted 80 from prior studies [11,12]. The positive control for these ELLA studies is the relative amount of colorimetric product generated when biotinylated CGL is bound to its ligands in this optimal binding buffer, and is considered maximal or 100% binding. All other treatments or additions (e.g. potential inhibitors) to the incubation media are then compared to the positive control to determine the decrease or percent inhibition of binding. Other appropriate controls were performed to define the most optimal binding assay parameters such as omitting specific constituents from the reaction wells such as the biotinylated CGL, egg jelly, calcium ions (via chelation with EGTA) or the detection reagents (i.e. ExtrAvidin Peroxidase). Figure 20 demonstrates that binding between the CGL and its ligand (coating the well) was nearly abolished when any of the above constituents were omitted. Notably, there was a modest signal in the wells lacking egg jelly (~ 10% signal relative to the native lectin-ligand binding). However, this was anticipated to some extent since the biotinylaed CGL itself may exhibit some adherence (despite the blocking and washing steps) to the microtiter well surfaces, and thus produce a false-positive signal via non-specific binding. Nevertheless, this nonspecific binding was deemed insignificant. 81 Reactivty of Enzyme-Linked Lectin Assay Absorbance (630 nm) 1.2 1 0.8 0.6 0.4 0.2 0 Lectin-Ligand (100% Binding) No Egg Jelly No Peroxidase No CGL EGTA Treatment Figure 20 – Reactivity of the enzyme-linked lectin assay in response to omitting specific fertilization constituents pivotal in the lectin-ligand binding interaction. The mean and standard deviation for triplicate trials are shown with regard to each experimental condition. 82 Furthermore, the calcium dependent binding interaction between the CGL to its ligand partners was demonstrated by the incorporation of 10 mM EGTA into the binding buffer with biotinylated CGL. EGTA is a chelating agent (binds to or complexes with metal ions so they are unavailable for other interactions) that is related to the chemical EDTA. EDTA chelates divalent metal cations in general (e.g. Mn2+, Mg2+ and Ca2+) wheras EGTA specifically chelates Ca2+ which has been shown to be an essential co-factor in the lectin-ligand binding interaction. EGTA proved to be a potent inhibitor, resulting in total inhibition of the CGL-ligand interaction and thus corroborating this observation from prior studies (Figure 20) [9,11,12]. Plate binding assays were also performed with selected monosaccharide and disaccharide inhibitors as appropriate controls to establish selectivity and sensitivity as a comparison to previous studies. Selected inhibitors at varying concentrations were incorporated during the biotinylated CGL incubation [9,11,12]. Galactose, lactose and melibiose were utilized since they have all been shown to be potent inhibitors of the lectin-ligand binding interaction. In particular, galactose has been well established and widely utilized as a potent and specific inhibitor of the lectin-ligand binding interaction. Figure 21 illustrates the percent inhibition of CGL binding (as compared to the positive control) in a dosedependent manner when the binding media includes either galactose or glucosamine. Increasing concentrations of galactose resulted in increased inhibition of CGL binding 83 to the egg jelly ligands with maximal inhibition (nearly 100%) achieved at approximately 75 mM galactose. At 10 mM galactose, approximately 50% inhibition was obtained. When glucosamine (a suspected non-inhibitor) was substituted for galactose, a < 5% inhibition was obtained at 12 mM, however increasing the concentration of this monosaccharides up to 100 mM did not result in a significant increased inhibitory effect (< 20%) as observed with galactose (Figure 21). 84 CGL-Ligand Monosaccharide Inhibition Percent Inhibition 100 80 60 Galactose 40 Glucosamine 20 0 0 20 40 60 80 100 Concentration (mM) Figure 21 – Monosaccharide inhibition of the enzyme-linked lectin assay for CGL ligand. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of the indicated concentrations of monosaccharide. Each point represents the average of triplicate assays. 85 Glucose was demonstrated to possess intermediate inhibitory characteristics, increasing concentrations of glucose resulted in increased inhibition of CGL binding to the adsorbed egg jelly with maximal inhibition of 55% achieved at 100 mM (Figure 22). Interestingly, fucose (6-deoxy-L-galactose) demonstrated near identical reactivity compared to galactose at each concentration (Figures 22 and 23). At 5, 12 and 25 mM identical inhibitory activity was observed, however at 50, 75 and 100 mM a slightly decreased inhibition was obtained. At concentrations of 50 mM and greater, fucose was able to inhibit the lectin-ligand binding to greater than 90% however unlike galactose, fucose was unable to completely inhibit the CGL-ligand binding reaction (Figures 22 and 23). 86 CGL-Ligand Monosaccharide Inhibition Percent Inhibition 100 80 60 Fucose 40 Glucose 20 0 0 20 40 60 80 100 Concentration (mM) Figure 22 – Monosaccharide inhibition of the enzyme-linked lectin assay for CGL ligand. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of the indicated concentrations of monosaccharide. Each point represents the average of triplicate assays. 87 CGL-Ligand Monosaccharide Inhibition Percent Inhibition 100 80 Galactose 60 Fucose 40 Glucosamine 20 0 0 20 40 60 80 100 Concentration (mM) Figure 23 – Monosaccharide inhibition of the enzyme-linked lectin assay for CGL ligand. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of the indicated concentrations of monosaccharide. Each point represents the average of triplicate assays. 88 Previous research has also demonstrated that the galactose containing disaccharides lactose and melibiose were potent inhibitors of the lectin-ligand binding interaction so these were also examined. Figure 24 illustrates the percentage of CGL binding that was inhibited when incubated with the disaccharides lactose, melibiose and sucrose (a suspected non-inhibitor). Both lactose and melibiose elicited a greater inhibitory effect than galactose at concentrations of 5, 12 and 25 mM. Increasing concentrations of lactose and melibiose resulted in increased inhibition of CGL binding to the adsorbed egg jelly. Both lactose and melibiose reached a 50% level of inhibition at approximately 5 mM and obtained maximal inhibition of 100% at 75 and 100 mM, respectively (Figure 24). Although lactose and melibiose displayed a greater inhibitory response at lower concentrations relative to galactose, ultimately all three compounds obtained maximal inhibition at or near 75 mM. Sucrose achieved ~15% inhibition at 12 mM, however increasing the concentration of this disaccharide up to 100 mM did not result in a significant increase (< 20%) (Figure 24). 89 CGL-Ligand Disaccharide Inhibition Percent Inhibition 100 80 Lactose 60 Melibiose 40 Sucrose 20 0 0 20 40 60 80 100 Concentration (mM) Figure 24 – Disaccharide inhibition of the enzyme-linked lectin assay for CGL ligand. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of the indicated concentrations of disaccharide. Each point represents the average of triplicate assays. 90 The disaccharides maltose and lactulose were also tested and were found to possess an intermediate level of inhibitory activity (Figure 25). Increasing concentrations of both maltose and lactulose resulted in increased inhibition of CGL binding to the adsorbed egg jelly with a maximal inhibition achieved at ~50 and ~75% at 100 mM, respectively. Increasing the concentrations of these disaccharides from 5 mM out to 100 mM resulted in a relatively dose-dependent increase in inhibitory activity, however inhibitory activity reached an upper limit near 75 mM for both disaccharides (Figure 25). 91 CGL-Ligand Disaccharide Inhibition Percent Inhibition 100 80 Lactose 60 Lactulose 40 Maltose 20 0 0 20 40 60 80 100 Concentration (mM) Figure 25 – Disaccharide inhibition of the enzyme-linked lectin assay for CGL ligand. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of the indicated concentrations of disaccharide. Each point represents the average of triplicate assays. 92 Collectively, the refined ELLA exhibited a modest background signal with regard to the presumed non-inhibitory mono- and disaccharide controls (glucosamine and sucrose). The effects of these controls elicited less than a 20% reduction in the lectin-ligand binding interaction at 100 mM. Additional controls (glucose, maltose and lactulose) elicited an intermediate level of inhibitory activity in the range of 50-75% at 100 mM levels. To discern specific from non-specific inhibition and to distinguish whether or not the modest background signal elicited by these controls were an artifact of the experiment, a 3% BSA treatment (inclusion in the binding media) was performed. The BSA treatment yielded comparable CGL-ligand binding inhibition activity as did the controls glucosamine and sucrose, eliciting a ~ 20% reduction in lectin-ligand binding activity (data not shown). Therefore, the minor inhibitory response elicited by both glucosamine and sucrose was deemed non-specific. Taken together, both monosaccharide and disaccharide competitive binding assay analysis revealed CGL binding specificities for fucose, galactose and galactose containing disaccharides (lactose, melibiose and lactulose) (Figures 26 and 27). No definitive anomeric specificity with regard to glycosidic linkages was discerned at the disaccharide level, however. The disaccharide melibiose [α- galactopyrasoyl(1,6)glucose] was slightly more inhibitory than galactose, however lactose [β-galactopyransoyl(1,4)glucose] was significantly more inhibitory than galactose and melibiose at 5, 12 and 25 mM. The disaccharide lactulose [βgalactopyransoy(1,4)fructose] was less inhibitory than galactose, lactose and melibiose 93 at all tested concentrations. Therefore, both 1-4 and 1-6 glycosidic disaccharide linkages comprising galactose and glucose monomers were capable of inhibiting the CGL lectin-ligand binding, and the β-derivative (lactose) appeared to be marginally more effective than the α-derivative (melibiose) in inhibiting the CGL-ligand binding interaction. Interestingly, the 1-4 glycosidic linkage between galactose and fructose monomers, which constitute the disaccharide lactulose was significantly less inhibitory than disaccharides comprised of galactose and glucose monomers (Figure 27). 94 6 CH2OH 5 O H 4 OH 1 OH 3 2 H OH H NH2 H Galactose Glucosamine C-2 Position H O H H CH3 H OH OH OH OH Glucose H Fucose Figure 26 – Monosaccharide structures illustrating the anomeric binding specificity of the CGL in the lectin-ligand binding reaction, highlighting the importance of the C-2 position and orientation of various hydroxyl groups, notably carbon positions 2-4 within these monosaccharide structures. 95 Lactulose Gal(β1-4)Fru Figure 27 – Disaccharide structures illustrating specific glycosidic linkages and anomeric specificity of the CGL in the lectin-ligand binding reaction. 96 Competitive Plate Binding Assays Involving CGL Ligand Oligosaccharide Fractions Initially, CGL ligand oligosaccharide inhibition analysis was performed utilizing the whole oligosaccharide fractions released from the SPE cartridge in order to obtain a relative semi-quantitative measurement of CGL ligand oligosaccharide inhibition characteristics and whether or not these whole fractions possessed biological activity. This analysis involved both neutral, acidic and a neutral and acidic combination in an effort to relatively assess the inhibitory properties of these aggregate fractions (Figure 28). A relative comparison between these SPE fractions was performed by combining two SPE fractions of eluted neutral CGL ligand oligosaccharides for one treatment. Another treatment consisted of combining two SPE fractions of eluted acidic CGL ligand oligosaccharides. The final treatment consisted of combining one SPE fraction of neutral oligosaccharides and one SPE fraction of acidic oligosaccharides to assess if there was a combined inhibitory effect. It is noteworthy to point out that amount of neutral oligosaccharide mass contained in the SPE fractions is likely not comparable to the amount of acidic oligosaccharide mass, thus equal proportions may not have been incubated together. Therefore, this inhibitory analysis is relative and only semiquantitative. 97 100 75 50 25 SPE Combination SPE Acidics SPE Neutrals SPE/HPLC Treatment Glucosamine 100 mM Sucrose 100 mM Galactose 100 mM 0 EGTA Treatment Percent Inhibition SPE Released CGL Ligand Oligosaccharides Experimental Condition Figure 28 – Inhibition of the enzyme-linked lectin assay for whole SPE released CGL ligand oligosaccharide fractions. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of neutral, acidic and a combination of neutral and acidic CGL ligand oligosaccharide fractions. All controls represent the average of triplicate assays. 98 Qualitatively, the whole CGL ligand oligosaccharide inhibition analysis revealed strong inhibition characteristics from the SPE derived neutral oligosaccharides, eliciting a 95% inhibition of CGL binding to the adsorbed egg jelly. Conversely, the acidic oligosaccharides displayed substantially less inhibitory properties, nevertheless, elicited a 35% reduction in lectin-ligand binding. The combined neutral and acidic oligosaccharide SPE fraction mixture did not achieve an intermediate value between the two, but was higher than the acidic fraction alone (39% inhibition). Taken together, this data indicates a prominent role of the neutral CGL ligand oligosaccharides in the specificity for the CGL in preventing binding to its ligand partners contained in the adsorbed egg jelly. To further assess the biological role of the isolated and quantified CGL ligand oligosaccharides derived from the CGL ligand, fractions 1, 2 and 3 (Figures 16 and 17) were incubated with the native lectin-ligand interaction to determine whether any of these fractions exhibited inhibitory effects. Initially, the molecular weight of each fraction was estimated based on the HPLC chromatograms of the surrogate oligosaccharide standards with respect to retention times. Fractions 1 and 2 possessed retention times of 6.705 and 6.981 and thus were estimated to be an approximate degree of polymerization (DP) equivalency of maltotriose (MW ~ 540 kD). Fraction 3 had an observed retention time of 12.805 and thus was estimated to be an approximate DP equivalency of maltohexaose (MW ~ 1080 kD). 99 Molecular weights of the CGL ligand oligosaccharide fractions were estimated based on the retention times observed by the DP surrogate standards, however it is notable to point out that branched structures containing the same number of monomer subunits did not possess the same elution profiles. Branched structures such as LNFP II (5 subunits) and LNH (6 subunits) displayed retention times equivalent to DP 3 and DP 5, respectively. Once estimated molecular weights were established, the biological activity of fractions 1, 2 and 3 were prepared and analyzed at identical micromolar concentrations for a true comparative analysis to observe relative binding inhibition between the three CGL ligand oligosaccharide fractions. In addition to mono- and disaccharide inhibition controls (galactose, glucosamine and sucrose), a separate control was deemed necessary to test whether there were any inhibitive compounds potentially in the isolated oligosaccharides derived from the chemical release of the oligosaccharides and their separation using the HPLC-CAD instrument. Thus, a mock sample (no glycoprotein) was processed in an identical fashion from borohydride chemical release to HPLC-CAD fraction collection and used in the ELLA (see materials and methods). No inhibitory effect was noted for this mock sample control (Figure 29; labeled as SPE/HPLC treatment) All three ligand oligosaccharide fractions were prepared at 10 µM concentrations (due to the limiting mass isolated from fraction 3) and separately 100 incorporated during the biotinylated CGL incubation as usual to determine if any of these had an inhibitory effect on CGL binding (Figure 29). No inhibitory effects were observed beyond that of the negative controls (e.g. glucosamine and sucrose) for any of the CGL ligand oligosaccharide fractions at 10 µM concentrations. CGL Ligand Oligosaccharide Comparative Analysis (10 uM) 100 75 50 25 ct os e Tr ea tm G al a EG TA 10 0 Su m M cr os e G 10 lu co 0 m sa M m in e SP 10 E/ 0 m HP M LC Tr CG ea L tm Li en ga t nd Fr CG ac L t io Li n ga 1 nd Fr CG ac L t io Li n ga 2 nd Fr ca t io n 3 0 en t Percent Inhibition 101 Experimental Condition Figure 29 – Inhibition of the enzyme-linked lectin assay for CGL ligand oligosaccharide fractions 1, 2 and 3. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of 10 µM concentrations of CGL ligand oligosaccharide fractions 1, 2 and 3. All controls represent the average of triplicate assays. 102 Fractions 2 and 3 were subsequently analyzed at 45 µM concentrations while fraction 3 was excluded due to being the limiting fraction based on mass (and thus was consumed during the 10 µM comparative analysis). No significant inhibition was also observed for the 45 µM inhibition assay for these two oligosaccharide fractions (Figure 30). 103 100 75 50 25 2 Fr ac t io n 1 Li L CG CG L Li ga nd Fr ac t io n en t ga nd Tr ea tm M HP LC SP E/ G lu co sa m in e 10 0 10 0 m m m M Su cr os e 10 0 ct os e G al a Tr ea tm EG TA M 0 en t Percent Inhibition CGL Ligand Oligosaccharide Comparative Analysis (45 uM) Experimental Condition Figure 30 – Inhibition of the enzyme-linked lectin assay for CGL ligand oligosaccharide fractions 1 and 2. Xenopus laevis egg jelly, 500 ng carbohydrate, was adsorbed to a microtiter plate and incubated with 75 ng biotinylated CGL in the presence of 45 µM concentrations of CGL ligand oligosaccharide fractions 1 and 2. All controls represent the average of triplicate assays. 104 DISCUSSION The block to polyspermic fertilization in Xenopus laevis is mediated by a calcium-dependent, galactose specific binding reaction between a lectin derived from the cortical granules and its ligand partners located in the immediate surroundings within the egg extracellular matrix. The cortical granule lectin (CGL) ligands have been shown to possess O-linked oligosaccharides as the functional moieties in binding activity with binding specificity for the CGL in producing the functional block to polyspermy. In the current work, an HPLC based oligosaccharide isolation and quantification methodology was developed in an attempt to directly isolate and accurately quantify functionally relevant ligand O-linked oligosaccharides. Isolation and quantification of specific oligosaccharide constituents derived from the CGL ligands were subsequently analyzed via a refined competitive enzyme-linked lectin assay (ELLA) in an attempt to assess their biological activity. Elucidation of the CGL ligand oligosaccharide constituents and determining whether they can bind to the CGL will likely advance our understanding of fertilization and cell-cell binding interactions involving the CGL and the eglectin family of CGL-like proteins since the binding properties and biological role appear to be evolutionarily conserved. This work was centered on contributing to a more definitive molecular mechanism and role in the block to polyspermic fertilization involving the lectin-ligand binding interaction. 105 The current work has substantially expanded on the utility of the HPLC-CAD device for the detection, quantification and isolation of underivatized biologically derived oligosaccharides for subsequent biological assays. The isolation and quantification HPLC-CAD method presented in the results section demonstrated excellent sensitivity in the analysis of oligosaccharides. This detection method has successfully demonstrated sensitivity in the picomolar range or mass detection limits of 0.3 to 0.7 ng with regard to oligosaccharides under optimized conditions. In comparison, both UV and oligosaccharide derivatization procedures have demonstrated sensitivities in the picomolar range as well, however the HPLC-CAD method was demonstrated to be approximately five times more sensitive than conventional UV absorbance detection. Conversely, the HPLC-CAD was demonstrated to be approximately ten times less sensitive than derivatization detection with regard to oligosaccharides [30]. This developed HPLC-CAD system provided a universal detection method along with greater sensitivity than previous HPLC-detection based methods. Also, since the detection method is universal (non-volatile charged particle detection), quantification was demonstrated to be possible without exact oligosaccharide standards [20,21,23]. This developed HPLC-CAD quantification methodology has proven to be superior to conventional HPLC-detection based methods in its ability to quantify and isolate underivitized biologically relevant oligosaccharides. This circumvents 106 previously encountered limitations with current derivitization methodologies since removal of these derivitization agents is required for subsequent biological assays. With regard to the HPLC-CAD quantitative work, a non-linear calibration scheme was generated and utilized as a result of surrogate oligosaccharide standards not displaying a true linear response. Therefore, ‘A’ and ‘b’ terms derived from power-fit calibration equations were employed as appropriate calibration terms for the quantification of oligosaccharides. The surrogate oligosaccharide standards displayed definitive trends in ‘A’ and ‘b’ terms as a function of retention time, allowing the prediction of calibration parameters for test and unknown oligosaccharides. Therefore, based on observed retention time, ‘A’ and ‘b’ values are established and along with peak area, concentration of an unknown oligosaccharide was determined. Interestingly, surrogate oligosaccharide standards maltohexaose (DP 7) and maltooctaose (DP 8) displayed a significantly decreased response compared to the other standards, glucose though maltohexaose and maltosyl-β-cyclodextrin in the power-fit concentration to peak area relationship. Additionally, both DP 7 and DP 8 displayed significant deviations from both ‘A’ and ‘b’ calibration trend lines as well, indicating that these standards may be somewhat suspect with regard to purity considering the discontinuous nature in response at the latter portions of these calibration curves involving these larger DP surrogate standards. Furthermore, maltooctaose was the only surrogate oligosaccharide standard that displayed an absolute average percent error in 107 excess of 5%, suggesting that purity may be an issue as indicated by consistently decreased response by the HPLC-CAD instrument. Collectively, the developed HPLC-CAD quantitative work involving surrogate, short chain and biological test oligosaccharide structures were accurately quantified to within less than a 19% average error with excellent reproducibility. Employing the nonlinear calibration scheme, all surrogate oligosaccharide standards (glucose through maltooctaose and maltosyl-β-cyclodextrin) were accurately quantified to within a 5% error, with the exception of maltooctaose, which displayed an average percent error of 10.7%. There were no correlative relationships among degree of polymerization and average percent error or standard deviation. The developed HPLC-CAD methodology appeared to possess an impartial response in the quantification of these surrogate oligosaccharide standards. It is noteworthy to point out that maltosyl-β-cyclodextrin was utilized as an additional surrogate oligosaccharide standard despite its structural dissimilarity to the other glucose oligomers. This was deemed necessary in order to extend the quantification calibration curves to accommodate the quantification of the larger biological test oligosaccharide structures. Although it would have been preferred, a linear glucose oligomer possessing a degree of polymerization (DP) of 9 was not commercially available therefore this compound was selected in an effort to substitute for the projected retention time that a DP 9 would possess. 108 The initial test oligosaccharides (isomaltotriose, stachyose, raffinose and melezitose) were all accurately quantified to within less than an absolute average percent error of 11%. Stachyose and melezitose displayed comparable responses and variations of 1.58 +/- 13.7 and -3.81 +/- 11.9, respectively. The variations between both of these compounds spanned both negative and positive territories and thus the responses were not consistently clustered in either direction, suggesting some intrinsic variability in response by the HPLC-CAD instrument. Isomaltotriose and raffinose on the other hand displayed comparable responses and variations of -10.8 +/- 7.07 and 10.2 +/- 8.18, respectively. The response of both of these compounds consistently resulted in negative values and thus the variations were clustered in negative territory. Considering these two compounds always elicited a negative response in quantification from the HPLC-CAD instrument, this may signify a decrease in water retention by these compounds, which may have affected nebulization efficiency in relation to oligosaccharide standards, thus underestimating the quantification of these oligosaccharides [31]. Despite the observed intrinsic variability in HPLC-CAD response of these initial test oligosaccharides, low average percent errors along with a defined range of variability in response demonstrated potential for the quantification of more complex oligosaccharides translatable to functional moieties found on the CGL ligand oligosaccharide moieties. Biological test oligosaccharide standards of varying complexity, representative of oligosaccharide moieties found on glycoproteins displayed a modest overall increase 109 in average percent error and variation in relation to both the surrogate and initial test oligosaccharides. There were no correlative relationships between core oligosaccharides (MAN-3 and LNH) and complex high-mannose type oligosaccharides (NA2 and NA4) with regard to absolute average percent errors (7.31 vs. 6.99), however variation in response appeared to increase as complexity increased (4.1 vs. 11.6). Additionally, structures containing residues found to exist in the CGL ligand oligosaccharides by NMR and MS [19,21,22] such as core glycoprotein oligosaccharide N- acetylglucosamine structures with terminal fucose residues (LDFT), and Nacetylglucosamine structures with terminal fucose and galactose residues (LNFP II), displayed very low average percent errors with excellent reproducibility (6.63 +/- 8.51 and 3.46 +/- 3.69, respectively). Mannopentaose, a five-chain high-mannose structure fragment commonly found among N-linked oligosaccharides displayed excellent reproducibility, however the average percent error was relatively high (-14.3 +/- 3.78). Notably, both NA2 and NA4 displayed the greatest range in variance 18.4 +/- 7.37 and 4.42 +/- 15.9, respectively. Therefore, there appears to be a correlation between quantification of larger and more complex oligosaccharides and an increase in response variability, but not necessarily absolute average percent error. The overall variability in response with regard to the HPLC-CAD quantitative analysis results may be attributed to a variety of reasons involving but not limited to experimental errors associated with sample preparation, purity, transferring, solubility issues and/or obtaining standards from different manufacturers, in which often may not 110 be accurate with amounts provided. Additionally, a significant contributor to possibly explain some of the differences in response and thus quantification errors of specific compounds may be due to differences in water retention or hydrates. It has be postulated that water retention by some oligosaccharides and/or an increase in the percent water during the HPLC gradients for later eluting compounds, may negatively affect nebulization efficiency in producing optimal charged droplets for detection. The CGL ligands contain both neutral and acidic oligosaccharides attached to their polypeptide backbone, however the current work was focused on solely analyzing the neutral oligosaccharides. A variety of reasons limited this research to strictly elucidating neutral CGL ligand oligosaccharides as opposed to the collective charged and neutral species in a quantitative manner. Firstly, the HPLC-CAD quantification methodology was originally exploratory in its nascent stages in an effort to demonstrate proof of concept. This was achieved utilizing only neutral surrogate oligosaccharide standards to demonstrate its application towards biologically derived oligosaccharides. Secondly, the analytical Prevail Carbohydrate ES HPLC column employed for this initial work may not be optimal for the separation of oligosaccharides spanning both neutral and acidic glycans. Thus, an additional methodology involving less available charged surrogate and charged biological test oligosaccharides would have been needed to be developed on a potentially different HPLC column that was robust enough to withstand the acidic modifier needed to elute charged oligosaccharide species. Thirdly, it was largely unknown how much oligosaccharide mass could be processed for 111 isolation following quantification analysis utilizing a flow splitter and using only analytical HPLC columns. Therefore, time and resources were invested to develop and optimize this isolation and quantification methodology and demonstrate its application for future applications. X. laevis O-linked oligosaccharide HPLC profiles were optimized for initial separation and isolation with a Hypercarb PGC HPLC column. This was due to the robustness of the column with its ability to process greater injection volumes while the different mechanism of separation yielded better selectivity of structurally similar compounds and better resolution as opposed to the Prevail Carbohydrate ES HPLC column. Additionally, the Hypercarb PGC column provided a high-resolving HPLC separation of the CGL ligand oligosaccharide mixture. Therefore, the Prevail Carbohydrate ES HPLC column was utilized for quantification work and secondary purification only. Although the separation mechanism between the Prevail Carbohydrate ES HPLC and the Hypercarb PGC HPLC column differ significantly, the chromatographic profiles are reasonably comparable with regard to the number of major oligosaccharide peaks and their abundance. Both profiles display four major oligosaccharide peaks, however a specific major oligosaccharide peak observed on the Prevail column is not correlative to a specific major oligosaccharide peak observed on the Hypercarb column as a result in their differences in separation/selectivity mechanisms. In comparison, the 112 Prevail analysis demonstrated the presence of approximately 17 oligosaccharide peaks whereas the Hypercarb analysis demonstrated the presence of approximately 20 oligosaccharide peaks. The differences observed between the two HPLC profiles with regard to number of peaks may be attributed to unresolved peaks co-migrating in the chromatograms. Taken together, these HPLC profiles illustrate the abundance and complexity of CGL ligand oligosaccharides consistent with previous NMR and MS studies [18,21,22]. Hypercarb PGC X. laevis HPLC profiles indicate the variety and complexity of the neutral oligosaccharide moieties released from the CGL ligand polypeptide backbone. The X. laevis chromatograms presented here suggests that there is an abundant amount of oligosaccharide species possessing different structural properties which are all in the molecular size range of trisaccharides to octasaccharides, which corroborates previous NMR/MS analyses [18,21,22]. The X. laevis chromatograms highlighted approximately five major peaks which were targeted for isolation and quantification for subsequent ELLA analysis. Two of the major oligosaccharide peaks initially targeted could not be resolved to homogeneity with a single separation. An attempt at a secondary purification resulted in multiple peaks on the Prevail Carbohydrate ES HPLC column, therefore adequate mass for subsequent biological assays was unattainable from these fractions. As a consequence, attempts in isolation of these peaks were abandoned. 113 Despite the obstacles in obtaining single purified oligosaccharide components for two of the isolated oligosaccharide peaks, the successful isolation and quantification was attainable with three other major oligosaccharide peaks. These three peaks illustrated the presence of one predominate oligosaccharide component free of any significant interfering oligosaccharides when measured by both the CAD and the UV signals. Employing a blank subtraction method, all three fractions were ultimately determined to be greater than 90% purity. These three fractions were subsequently equilibrated to a molarity equivalency for an ELLA comparative analysis. The refined ELLA, adopted from previous work by Hedrick et al., demonstrated greater sensitivity than previous assays with regard to monosaccharide and disaccharide inhibition analysis of the lectin-ligand binding interaction [11]. The refined ELLA demonstrated that 75 mM galactose was sufficient to completely inhibit the lectinligand binding interaction. Previously, the most sensitive ELLA reported by Quill and Hedrick required 150 mM galactose to completely inhibit the lectin-ligand binding interaction [11]. Additionally, the sensitivity is greater than that reported by Nishihara et al., which demonstrated that 100 mM galactose only inhibited the lectin-ligand reaction by 75%, utilizing a CGL-J1 precipitin reaction assay [9]. Additional analysis by Nishihara and co-workers utilizing the disaccharide inhibitors lactose and melibiose exhibited significantly less sensitivity than the refined ELLA as well. Specifically with regard to lactose, the refined ELLA demonstrated inhibition activity of 85 and 95% at 25 and 50 mM, respectively, whereas Nishihara et al., achieved inhibition activity of 50 114 and 75% at the two corresponding concentrations. It is noteworthy to point out that both assays achieved total inhibition with lactose at 100 mM. With regard to melibiose, the refined ELLA demonstrated inhibition activity of 80 and 90% at 25 and 50 mM, respectively, whereas Nishihara et al., achieved inhibition activity of 0 and 50% at the two corresponding concentrations. Therefore, specifically at lower concentrations of selected inhibitors, the refined ELLA was demonstrated to be substantially more sensitive with regard to the specific inhibitors galactose, lactose and melibiose. Some discrepancies in the developed ELLA did arise with regard to glucose and lactulose in comparison to work by Nishihara et al., which may be a result of the enhanced sensitivity of the developed assay as observed with melibiose. At 100 mM concentrations, Nishihara and co-workers reported that no inhibitory activity was observed with glucose or lactulose during the CGL-J1 precipitin reaction assay. In contrast, the data reported here demonstrates that these two compounds possess some intermediate inhibitory activity, thus suggesting these compounds may possess a weak affinity towards the CGL binding pocket. This weak affinity may not have been detectable with previous assays as a result of the decreased sensitivity. Interestingly, the refined ELLA demonstrated that the monosaccharide fucose displayed nearly identical inhibitory activity to that of the well established inhibitor, galactose. Previous MS and NMR analysis of both neutral and acidic oligosaccharides derived from whole egg jelly and specifically from the combined J1 and J2 segments 115 revealed that terminal fucose residues are vastly abundant throughout these discerned oligosaccharide structures and thus may be a biologically relevant structure recognized by the CGL. Additionally, the ligand O-linked oligosaccharide structures responsible for ligand activity contained terminal galactose residues associated with fucose and sulfate residues [11,13,18,22,25]. The biological significance of these terminal fucose residues attached to the CGL ligand has been partially investigated by Quill and Hedrick via ELLA analysis [11]. Treatment of purified CGL ligand with α-fucosidase to remove terminal fucose residues revealed that no significant decrease in lectin-ligand binding was obtained. However, in this treatment the fucosidase utilized may not have released the relevant fucose residues since these enzymes are highly specific. Also, there is a possibility that the reactions may not have been taken to completion and thus not released all the fucose residues. Therefore, the data presented by Quill and Hedrick suggests that from a biological standpoint, fucose residues may possess a limited ability to act independently in eliciting a binding interaction/specificity for the CGL since the removal of these fucose residues did not significantly reduce binding as measured by the ELLA. However, considering the in-vitro ELLA assay data demonstrated here, it is apparent that fucose is a strong and specific inhibitor. Therefore, biologically these fucose structures may act in concert with galactose within the CGL ligand oligosaccharide moieties in order to capture and bind to the CGL in producing the block to polyspermy. 116 Thus, the evidence from these studies suggests that fucose is likely involved in the oligosaccharide chains that participate in lectin-ligand binding. The ELLA data obtained in the current work suggests that the CGL possesses anomeric binding specificity for galactose, fucose and galactose containing disaccharides lactose and melibiose. Collectively, both 1-4 and 1-6 glycosidic disaccharide linkages comprising galactose and glucose monomers were capable of inhibiting the CGL lectin-ligand binding, however the β-derivative (lactose) appeared to be marginally more effective than the α-derivative (melibiose) in inhibitive properties. Additionally, configurations of hydroxyl groups at carbons 2-4 of galactose were demonstrated to be central to the observed inhibitory properties. Sugars that differ from that of galactose in specific orientation of the hydroxyl groups at carbon positions 2-4 displayed substantially decreased or insignificant inhibition characteristics (e.g. lactulose). In addition to the observed anomeric specificity of the CGL, MS and NMR analysis revealed that the combined J1 and J2 layers contained all the sulfated species within the egg jelly extract and the CGL ligands themselves possess sulfated oligosaccharides. Along with previous studies, the incorporation of a calcium-specific chelating agent (EGTA) resulted in complete inhibition of the lectin-ligand binding interaction. Thus, these sulfated oligosaccharides may be essential for interactions with calcium so as to facilitate binding, whereas terminal galactose and fucose residues may 117 serve in the molecular recognition and physical binding/capture of the CGL. Collectively, fucose appears to be underappreciated as a critical constituent involved in the lectin-ligand binding reaction. The comparative analysis of the isolated and quantified CGL ligand oligosaccharides at concentrations of 10 and 45 µM were unable to elicit an inhibitory response of the lectin-ligand binding interaction. Conversely, a semi-quantitative assessment of whole CGL ligand oligosaccharide fractions released from the SPE cartridge possessed strong inhibition properties. Whole SPE neutral CGL ligand oligosaccharide fractions demonstrated strong lectin-ligand inhibition characteristics eliciting a 95% reduction in binding. The acidic CGL ligand SPE released oligosaccharides elicited substantially decreased inhibition properties, while the combined neutral and acidic oligosaccharide treatment yielded a modest increase over that of the acidic oligosaccharides. Molecular weights of the CGL ligand oligosaccharide fractions were estimated based on the retention times observed by the DP surrogate standards, however it is notable to point out that branched structures containing the same number of monomer subunits did not possess the same elution profiles. Branched structures such as LNFP II (5 subunits) and LNH (6 subunits) displayed retention times equivalent to DP 3 and DP 5, respectively. Therefore, the estimated molecular weights of the CGL ligand oligosaccharides may have been underestimated since branched structures appear to 118 interact with the stationary phase with less surface area and thus display a decrease in retention times compared to their monomeric DP equivalent counterparts. A number of hypotheses arise as a result of the ELLA analysis with regard to the isolated and quantified CGL ligand oligosaccharides as well as the SPE released whole fractions. From the data presented here, it may be possible that the CGL ligand polypeptide backbone may be essential in maintaining the three-dimensional integrity of the CGL ligand glycoprotein and thus be integral in displaying a specific orientation of the oligosaccharide moieties since lectins are known to bind with spatial specificities. Such an orientation may be central to the CGL-ligand binding, where one oligosaccharide moiety may not necessarily be dominant. Conversely, the collective orientation of oligosaccharides dictated by the polypeptide backbone may act in concert to produce the binding specificity and affinity via multiple binding interactions (multivalancy) to its CGL partner in producing the functional block to polyspermy. It is a possibility that chemical and HPLC separation treatments following the SPE procedure may have resulted in some loss of biological activity. However, since the SPE fractions (neutral and acidic) elicited significant inhibitory activity (i.e. 95% for neutral fraction), it can be assumed that the released oligosaccharides have retained their biological activity. In this study, there was no conclusive evidence of any isolated oligosaccharide fraction possessing an inhibitory effect on lectin-ligand binding. This is likely due to an 119 inability of the developed methodology to yield large enough quantities to assess binding inhibition in a dose-response manner. The CGL oligosaccharide mass obtained was only adequate enough to produce micromolar concentrations or a 1000-fold less concentrated samples than all of the analyzed mono- and disaccharide inhibitors. It may have also been possible that strong interacting CGL ligand oligosaccharides were not isolated, thus it is likely necessary to employ semi-preparative or preparative sized HPLC columns in order to enable the purification of enough of the oligosaccharide fractions to observe an inhibitory effect in the binding assays developed. However, compelling evidence suggests that at perhaps greater concentrations, specific CGL ligand oligosaccharides may have a preferential role in CGL binding as observed with the whole SPE fraction inhibition analysis (i.e. neutral fraction). Therefore, future work should involve a preparative HPLC column for acquiring adequate oligosaccharide mass for subsequent biological assays. In summary, this research has successfully developed an oligosaccharide isolation and quantification methodology applicable to biologically derived glycans. This developed methodology circumvents previously encountered complications in utilizing derivatization agents while maintaining detection limits at the picomolar level. This methodology can ultimately be applied to a wide range of neutral oligosaccharide containing glycoproteins. This work has also expanded on the lectin-ligand ELLA analysis via developing a more sensitive assay to assess biological activity of selected compounds. It was found that whole neutral oligosaccharide fractions derived from the 120 ligands appears to inhibit binding more strongly than the acidic oligosaccharide fractions. And finally, further specificity of the CGL-ligand binding has been deduced from the refined ELLA analyses, specifically with regard to fucose monomers. 121 LITERATURE CITED [1] Brooker, J. R., Genetics: Analysis & Principles 2nd ed. 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