2/2/2015 Diabetes Mellitus & Metabolic Syndrome Classification Prevalence US and worldwide Type 1 Diabetes Type 2 Diabetes Obesity and the Metabolic Syndrome What is Diabetes? • Diabetes is a group of diseases characterized by high levels of blood glucose (blood sugar) • Diabetes can lead to serious health problems and premature death • 2 in 3 people with diabetes die of heart disease or stroke • Diabetes is the #1 cause of adult blindness • Diabetes is the #1 cause of kidney failure • Diabetes causes more than 60% of non-traumatic lowerlimb amputations each year • Typical symptoms are polyuria, polydipsia, and polyphagia National Diabetes Education Project: www.ndep.nih.gov Global Diabetes Prevalence 2014 Three Types of Diabetes • Type 1 diabetes – 5% to 10% of diagnosed cases of diabetes • Type 2 diabetes – 90% to 95% diagnosed cases of diabetes • Gestational Diabetes Mellitus – 7% of all U.S. pregnancies (4% worldwide) – Increased lifelong risk for mother and child for developing type 2 diabetes National Diabetes Education Project: www.ndep.nih.gov Diabetes is a worldwide problem • 8.3% (387 Million people) living with diabetes • Increasing in every country • 77% people with diabetes live in low/middle income countries www.who.int 1 2/2/2015 Number of US adults with diagnosed Diabetes USA Prevalence 2012 – 9.3% US population! – Diagnosed: 21 million people – Undiagnosed: 8.1 million people (28%) http://www.cdc.gov/diabetes/data/statistics/2014StatisticsReport.html Percentage of US adults with diagnosed diabetes (by county) 2008 Age of Adults with Diabetes Newly diagnosed % with diabetes 892,000 25.9 16.2 400,000 371,000 12.3 4.1 Total 20yr + 20‐44 45‐64 20‐44 65+ Estimated percentage of people with diabetes (diagnosed and undiagnosed) by age in US, 2009-2012 45‐64 65 + Number of newly diagnosed cases of diabetes, by age group, US 2012 2009-2012 National Health and Nutrition Examination Survey Gender differences? Age-adjusted* percentage of people aged 20 years or older with diagnosed diabetes, by race/ethnicity, United States, 2010–2012 13.6 11.2 Men Source: 2009-2012 National Health Interview Survey Women Age adjusted % of people 20yr+ diagnosed with diabetes Diagnosed and undiagnosed diabetes among adults (20yr + in USA 2012) 18 16 14 12 10 8 6 4 2 0 15.9 12.8 13.2 9 7.6 Non Hispanic whites Asian Americans Hispanics Non‐Hispanic American blacks Indians/Alaska Natives *Based on the 2000 U.S. standard population. Source: 2010–2012 National Health Interview Survey and 2012 Indian Health Service’s National Patient Information Reporting System. 2 2/2/2015 Estimated lifetime risk of developing diabetes Rate of new cases of type 1 and type 2 diabetes among people younger than 20 years, by age and race/ethnicity, 2008–2009 LIfetime risk of diabetes (%) 60 50 40 Overall 30 Non‐hispanic white Non‐Hispanic black 20 Hispanic 10 0 Men Gregg et al , Lancet, 2014 women for individuals born in the United States in 2000-2011 <10 years 10–19 years Source: SEARCH for Diabetes in Youth Study. NHW=non-Hispanic whites; NHB=non-Hispanic blacks; H=Hispanics; API=Asians/Pacific Islanders; AIAN=American Indians/Alaska Natives. Who is affected? Estimated Cost of Diabetes • US Total: $245 billion in 2012 (41% increase from 2007) • $1 healthcare in $5 in USA • Worldwide: $612 billion in 2014 ($1 healthcare in $9) direct medical cost $69 indrect (lost productivity) $176 Diabetes Care. 2013;36(4):1033- 1046, www.idf.org Acute Problems in Diabetes Hyperglycemia: polyuria, polydipsia, polyphagia with weight loss, Na+ & K+ imbalances, weakness/fatigue, glycosylation of proteins, increased osmolarity of serum (increased concentration of solute), Ketoacidosis: decreases blood pH, HCO3-2, Hb avidity for O2; leads to hypoxic coma &/or tachycardia Hypoglycemia (especially in treated diabetics): lack of brain glucose leads to neuropathy & coma, autonomic hyperactivity Long-term complications of Diabetes Microvascular • Retinopathy: leading cause of blindness in US adults • Nephropathy: leading cause of kidney failure requiring dialysis • Neuropathy: 60-70% of diabetics develop some form of nerve disease • Amputation: diabetes is the major cause of non-trauma leg amputation. Macrovascular • Cardiovascular disease (1.7x higher death rate in diabetics) • Stroke (1.5x higher in diabetes) 3 2/2/2015 Criteria for the Diagnosis of Diabetes Mellitus EVERY 24 HOURS + symptoms • New Cases – 5,200 • Deaths – 810 • Amputations – 230 • Kidney Failure – 120 • Blindness - 55 Oral Glucose Tolerance Test: Drink glucose solution (1.75 g/kg bw or 75 g max). Measure blood glucose at 0, 30, 60, 90 and 120 min. National Diabetes Education Project: www.ndep.nih.gov Characteristics of Type 1 Diabetes What are the 3 symptoms of diabetes? • • • • • • • A. Pain, Polydipsia, Polyuria B. Perspiration, Polyphagia, Polydipsia C. Polyploidy, Psoriasis, Polyuria D. Pain, Polyploidy, Polydactyly E. Polydipsia, Polyphagia, Polyuria Type 1 Diabetes • Beta cell destruction – Usually leading to absolute insulin deficiency • Immune mediated FasL IFN TNF T cell Class I MHC Macrophage TNF IL-1 NO Dendritic cell Etiology of Type 1 Diabetes Inflammation Autoimmune Reaction Class II MHC Hypoinsulinemia (↓insulin levels) ~5-10% of diagnosed diabetes cases Patients require insulin Age of onset: childhood Ketoacidosis (↑ketones in blood) 3 million people with T1DM in US Peak incidence occurs during puberty 10-12 in girls, 12-14 in boys Beta cell CD8+ T cell Beta cell Destruction • • • • Autoimmune disease Selective destruction of β-cells by T cells Both genetic & environmental factors are important Cause of autoimmune attack unknown • Circulating antibodies develop: Islet Cell Cytoplasmic Autoantibodies (ICA) (detected in 70-80% new cases) Glutamic Acid Decarboxylase Autoantibodies (GADA) (80% new IDDM) Insulin Autoantibodies (IAA) (detected in 40% in new kids with IDDM) • >90% destruction of islets needed for symptoms ?? American Diabetes Association. Diabetes Care. 2003;26:S33–S50. 4 2/2/2015 Progression of Type 1 Diabetes Type 1 Diabetes has a strong genetic component Precipitating event Genetic predisposition Antibody formation Normal insulin release Progressive loss of insulin release Glucose normal Beta Cell Mass Overt diabetes C-peptide present No C-peptide present Time • 0.4% risk of occurrence if no family history • 6‐11% if offspring of parent with T1D • 5% in siblings has T1D • 30‐40% risk if twin has T1D (monozygotic = 30‐65%, Dizygotic 6‐10%) Atkinson MA and Eisenbarth GS. Lancet. 2001;358:221–229. Type 1 Diabetes susceptibility loci implicated in T1D Bakay et al, Genes, 2013 Insulitis in islets before onset of T1DM Immune and non immune genes implicated in Type 1 Diabetes 2006 = 6 genes associated with T1D 2012 = 60+ genes associated with T1D Bakay et al, Genes, 2013 What triggers immune destruction? Environmental Factors Viruses Enteroviruses e.g Coxsackie Congenital Rubella (10-20% develop T1DM) Mumps, measles, CMV Normal human islet Insulitis in pre-diabetic (Lymphocytic infiltration) Nutrition Early exposure to Cow’s milk or gluten Vitamin D deficiency 5 2/2/2015 Type 1 Diabetes Genes + Induction of autoimmunity Immune regulation What has not been linked to type 1 diabetes? Environment Trigger A. B. C. D. E. The suspect Cytokines and cytotoxic molecules The weapons Beta cells Gluten Coxsackie Virus Mumps Vitamin D deficiency Lentivirus The victims Blood sugar Regulation Resting state Insulin Glucagon 10 g/h 4 g/h Glucose 4.5 mM 6 g/h Characteristics of Type 2 Diabetes Mellitus Type 1 Diabetes Insulin Glucagon >20 g/h <1 g/h Glucose 8 - 10 mM >14 g/h 6 g/h • • • • • • • • • • • Adult onset Polygenic and environmental influence Normal to low insulin levels Obesity linked (70-90%) May be asymptomatic 3 P’s: polyuria, polydipsia, polyphagia Weakness/fatigue Glycosuria Dry, itchy skin Visual changes Skin and mucous membrane infections 6 2/2/2015 Common genetic variants linked to T2DM Monogenic forms of T2DM (rare) Maturity Onset Diabetes in the Young (MODY) • 1-2% of cases of Diabetes • Usually first occurs during adolescence or early adulthood • Autosomal dominant mutation in genes involved in insulin secretion or insulin action. Risk Factors for Development of T2-DM Risk Factors Age Body Mass Index (BMI) BMI = weight (kg)/Height2 (m) Magnitude 5-10 fold increase age > 40 vs. age ≤ 40 Ethnicity African Americans Hispanic Americans Nauruans, Micronesia Pima Indians, Arizona Increase 1.5-2 fold 2-3 5-7 7 - 10 5-fold Impaired Glucose Tolerance BMI classifications Relationship Between BMI and Risk of T2DM 93.2 Age-Adjusted Relative Risk 100 <18.5 18.5‐24.9 25‐29.9 30‐39.9 >40 Underweight Healthy Grade I overweight Grade II Overweight Grade III Overweight Thin Normal Overweight Obese Morbid Obesity Men 75 obese overweight Women 54.0 50 27.6 25 0 42.1 40.3 1.0 2.9 1.0 4.3 1.0 5.0 1.5 <22 <23 23 23.9 24 24.9 8.1 2.2 15.8 25 26.9 27 28.9 4.4 Body Mass index 6.7 29 30.9 21.3 11.6 31 32.9 33 34.9 35+ (kg/m2) Chan J et al. Diabetes Care 1994;17:961. Colditz G et al. Ann Intern Med 1995;122:481. 7 2/2/2015 Conversion from Impaired Glucose Tolerance to Diabetes The % of abdominal fat rather than the BMI per se is associated with changes in insulin sensitivity 14 12 Rate per year (%) 10 8 6 BMI < 25 BMI > 25 4 Ito, et al. 6932 Japanese with GTT followed for 1-28 years 2 <140 140-169 170-199 2h plasma glucose level (mg/dL) after 75 gm OGTT at baseline Increased BMI and increased baseline glycemia both increase conversion from IGT to Diabetes Men Women Distribution by Metabolic Status Among Converters to T2DM (83% of Prediabetic Subjects are Insulin Resistant) A. B. C. D. E. Both (54%) Insulin resistant; good insulin secretion (28.7%) Waist Circumference Substantially Increased Risk >102 cm Which group has the highest risk of diabetes? Low insulin secretion; insulin sensitive (15.9%) Neither (1.5%) Increased risk >94 cm >88 cm Pima Indians Nauruans Hispanic Americans African Americans Caucasian Americans Haffner SM et al. Circulation. 2000;101:975-980. Mechanism of Hyperglycemia in Diabetes B-cell dysfunction Type 2 Diabetes: Lack on insulin effect on peripheral tissues Glucagon Insulin Resistance Insulin Insulin Insulin Insulin Insulin Increased hepatic glucose production Reduced insulin Liver Adipose Decreased glucose uptake (muscle and adipose) Glycogenolysis Gluconeogenesis Lipogenesis Lipolysis Glucose uptake Protein synthesis Fasting Blood Glucose Plasma FFA and Glycerol Fed Blood Glucose Plasma Amino Acids Hyperglycemia 8 2/2/2015 Insulin resistance: impaired glucose uptake into skeletal muscle and fat in T2DM Natural History of Type 2 Diabetes Insulin resistance increases, then stabilizes, occurs many years prior to Diabetes Glucose Uptake (mg/kg/min) Splanchnic (liver and intestine) 8 Adipose Beta cell – initial compensation for insulin resistance, serum glucose in normal range Muscle 6 Brain Insulin Resistance Insulin Secretion 4 100% 2 -20 -10 0 10 20 30 Years of Diabetes 0 Normal Basal Type 2 Insulin Stimulation 50 Bergenstal RM, et al. Endocrinology 4th ed, 2000. Natural History of Type 2 Diabetes Obesity IGT Diabetes Postmeal Glucose Plasma Glucose Fasting Glucose 100 75 120 mg/dL Insulin Resistance Relative Beta Cell Function Stages of Type 2 Diabetes Uncontrolled Hyperglycemia Insulin Secretion Beta Cell Function 50 (%) 25 -20 -10 0 10 20 Years of Diabetes Type 2 Phase 1 IGT 100% Postprandial Hyperglycemia Type 2 Phase 2 30 0 -12 -10 -6 Secretory dysfunction develops and insulin secretion no longer able to compensate Rise in fasting glucose, further compromises insulin secretion and action -2 Type 2 Phase 3 0 2 6 10 14 Years From Diagnosis Adapted from Lebovitz HE. Diabetes Reviews. 1999;7(3):139–153. 52 Bergenstal RM, et al. Endocrinology 4th ed, 2000. Insulin secretion cannot be understood in isolation but only in relationship to the individuals insulin sensitivity Islet hyperplasia during compensation If subjects with normal glucose tolerance become more insulin resistant by gaining weight, they would move to the left. If they can compensate by increasing their insulin secretion, they may still remain glucose tolerant. Normal islet Insulin resistant Islet from insulin resistant mouse Insulin sensitive S. Kahn, U.W. 9 2/2/2015 Amyloid in islets of T2DM Which tissue takes up the most glucose in the insulin stimulated state? A. B. C. D. Islet showing amyloid deposits in T2DM Normal islet Brain Muscle Adipose Liver & intestines Progressive beta cell dysfunction: Delayed Insulin Secretion Impaired suppression of Hepatic Glucose Production causes postprandial hyperglycemia Patients with T2D have blunted and delayed insulin response, and prolonged glucose excursion Plasma Insulin 60 Fasting Plasma Glucose (FPG) Level (mg/dL) 1.00 Plasma Glucose < 144 < 215 215-270 > 324 Normal 0.80 360 270 (mg/dL) 180 40 (mU/L) 20 Mean Insulin Level (nmol/L) 0.60 0.40 90 0 –1 0 1 2 3 4 5 –1 0 1 2 3 4 0.20 5 Hours After Glucose Ingestion 0.00 Healthy Subjects –30 0 30 60 Patients With Type 2 Diabetes Glucose Excursions in Type 2 Diabetes Meal 120 150 180 210 240 Coates, et al. Diabetes Res Clin Pract. 1994 Dec 31;26(3):177–187. Mitrakou A, et al. Diabetes. 1990;39:1381–1390. 400 90 Time (min) Meal Meal 58 Insulin Secretion in Type 2 Diabetes Meal 800 Meal Meal Normal Type 2 diabetes 300 600 Diabetic Insulin Secretion 400 (pmol/min) Glucose (mg/dL) 200 200 100 Normal 0 0 0600 0600 1000 1400 1800 2200 0200 0600 1400 1800 2200 0200 Time (24hour clock) Time of Day Polonsky KS, et al. NEJM. 1988;21;318(19):1237-1239. 1000 59 Polonsky KS, et al. N Engl J Med. 1996 Mar 21;334(12):777-783. 60 10 2/2/2015 What is the mechanism for the development of Insulin Resistance? Obesity induced inflammation drives insulin resistance Proinflammatory cytokines Immune cell migration Insulin resistance Inhibition of insulin signaling What is the mechanism of Insulin Resistance? 1. Obesity causes chronic low grade inflammation – Increased macrophage infiltration and altered polarization 2. Excess lipid causes lipotoxicity 3. Obesity changes microflora in the intestines – bacterial by products cause resistance Excess lipid accumulation causes insulin resistance Why do some individuals with IGT progress to diabetes? A. B. C. D. E. Islet cells begin to fail Insulin resistance increases Autoimmune reaction occurs Kidneys fail Glucagon increases 11 2/2/2015 Prevalence of Self-Reported Obesity Among U.S. Adults Obesity 2000 1990 2011 2013 WA ME ND MN VT NH MA SD WI N RI MI CT PAY NJ NE IA DE IL IN OH MD VA KS MO KY WV DC NC OK AR TN SC AZ NM MSAL GA TX LA FL OR ID NV CA AK 2010 UT MT WY CO HI 15%–<20% *BMI 30 No Data <10% 10%–14% 15%–19% 20%–24% 25%–29% ≥30% 20%–<25% 25%–<30% GUAM PR 30%–<35% ≥35% • No state had a prevalence of obesity less than 20%. • 2 states (Mississippi and West Virginia) had a prevalence of obesity of 35% or greater CDC’s Division of Diabetes Translation. National Diabetes Surveillance System available at http://www.cdc.gov/diabetes/statistics Age-adjusted Prevalence of Obesity and Diagnosed Diabetes Among U.S. Adults Aged 18 Years or Older Insulin Resistance: Causes and Conditions kg/m2) Obesity (BMI ≥30 1994 No Data 2010 2000 <14.0% 14.0%–17.9% 18.0%–21.9% 22.0%–25.9% 26.0% Activity Obesity / Lipodystrophy Aging Medications Rare Disorders Genetics Insulin Resistance Diabetes 1994 2010 2000 Type 2 Diabetes No Data <4.5% 4.5%–5.9% 6.0%–7.4% 7.5%–8.9% >9.0% CDC’s Division of Diabetes Translation. National Diabetes Surveillance System available at http://www.cdc.gov/diabetes/statistics PCOS Hypertension Dyslipidemia Neurodegeneration Atherosclerosis The Metabolic Syndrome: Historical Perspective Obesity and the Metabolic Syndrome Target population for the prevention of Type 2 Diabetes and Complications (~100 million diagnosed in the U.S.) 1988: Syndrome X Abdominal obesity (waist circumference : men: > 40 in, women: >35 in) Insulin Resistance plus TWO of the following: • • • • Fasting glucose > 100mg/dL Blood pressure > 130/85 mm Hg Triglycerides > 150 mg/dl High-density lipoprotein cholesterol (good cholesterol) (men: <40 mg/dl, women: < 50 mg/dl) Glucose Intolerance Hyperinsulinemia TG HDL-C Hypertension CORONARY HEART DISEASE Reaven G. Diabetes. 1988;37:1565-1607. 12 2/2/2015 Insulin Sensitivity Improves with Weight Loss in Patients with Type 2 Diabetes Modest Weight Loss Prevents Diabetes in Overweight and Obese Persons with IGT 150 100 * 30 * * 0 *P<0.01 vs before. 0-2.4 2.5-6.9 7.0-14.0 Placebo 20 50 Before Cumulative Incidence of Diabetes (%) Insulin (pmol/L) 40 >15 Weight Loss at 1 Year (%) Wing et al. Arch Intern Med 1987;147:1749. 10 Lifestyle 0 0 0.5 1.0 1.5 2.0 2.5 Year 3.0 3.5 4.0 Diabetes Prevention Program Research Group. N Eng J Med 2002;346:393. Copyright © 2002. Massachusetts Medical Society. All rights reserved. What is not associated with the Metabolic Syndrome? A. B. C. D. E. Atherosclerosis Polycystic Ovary Syndrome Diabetes Hypertension HIV infection 13