ENVOLVING THE FUTURE OF SINGLE PILL COMBINATION IN ANTIHYPERTENSIVE THERAPHY Djanggan Sargowo Shangri-La, Surabaya - Sabtu, 23 Juni 2012 1 Prevalence* of HTN (%) HYPERTENSION IS A PREVALENT DISEASE AFFECTING 1 BILLION PEOPLE TODAY *Among persons aged 35–64 years old; age and sex adjusted HTN = BP 140/90 mmHg or on treatment Wolf-Maier et al. JAMA 2003;289:2363–9 2 CLASSIFICATION OF BLOOD PRESSURE IN US ADULTS: JNC VII GUIDELINES BP category Normal Systolic (mmHg) Diastolic (mmHg) <120 and <80 Pre-hypertension 120–139 or 80–89 Hypertension, stage 1 140–159 or 90–99 Hypertension, stage 2 160 or 100 Chobanian et al. JAMA 2003;289:256072 3 JNC VII AND ESHESC SUMMARY : Target Blood Pressure Goals Type of hypertension Uncomplicated BP goal (mmHg) <140/90 Complicated Diabetes mellitus <130/80 Kidney disease <130/80 Chobanian et al. JAMA 2003;289:256072 Guidelines Committee. J Hypertens 2003;21:101153 4 JNC VII: ALGORITHM FOR TREATMENT OF HYPERTENSION Lifestyle modifications Not at goal BP* HTN without compelling indications HTN with compelling indications Drug(s) for the compelling indications Stage 1 Stage 2 Thiazide-type diuretics for most. May consider ACE inhibitor, ARB, β-blocker, CCB, or combination Two-drug combination for most (usually including thiazide-type diuretic) Other antihypertensive drugs (diuretics, ACE inhibitor, ARB, β-blocker, CCB) as needed If not at goal, optimise dosages or add additional drugs until goal BP is achieved. Consider consultation with hypertension specialist *BP goal <140/90 mmHg or <130/80 mmHg for those with diabetes or chronic kidney disease Chobanian et al. JAMA 2003;289:2560–72 5 ESH–ESC: ALGORITHM FOR TREATMENT OF HYPERTENSION Consider: BP level before treatment Absence or presence of TOD and risk factors Choose between: Single agent at low dose 2-drug combination at low dose If goal BP not achieved Previous agent Switch to at full dose different agent at low dose Previous combination at full dose Add a third drug at low dose If goal BP not achieved 2–3 drug combination Full-dose monotherapy TOD = target organ damage 3-drug combination at effective doses ESH–ESC Guidelines. J Hypertens 2003;21:1779–86 6 APPROXIMATELY 73% OF EUROPEAN PATIENTS WITH HYPERTENSION REMAIN UNTREATED Patients (%) 100 Treated Untreated 75 74 74 74 73 73 68 England Sweden Germany Spain Italy 80 60 40 20 0 Wolf-Maier et al. Hypertension 2004;43:10–17 7 Patients with BP control (%) More than 60% of Patients do not Achieve BP goal of <140/90 mmHg with monotherapy BP < 140/90 mmHg Dickerson et al. Lancet. 1999:353:2008–2013. BP < 135/85 mmHg 8 ESH/ESC JNC VII Also Guidelines worldwide Acknowledge That Most Patients Need Combination Therapy to Achieve BP Goals Most patients with hypertension will require two or more antihypertensive medications to achieve their BP goals – When BP is > 20/10 mmHg above goal, consideration should be given to initiating therapy with two drugs • Combination treatment should be considered as first choice when there is high CV risk – i.e., in individuals in whom BP is markedly above the hypertension threshold (> 20/10 mmHg), or associated with multiple risk factors sub-clinical organ damage, diabetes, renal or CV disease • Many patients will require more than one drug to achieve adequate BP control – Pathophysiological reasoning suggests that adding an ACE-I/ARB to a CCB or a diuretic (or vice versa in the younger group) are logical combinations NICE JSH • The Japanese Society of Hypertension Committee for Guidelines for the Management of Hypertension 2009 • The use of two or three drugs in combination is often necessary to achieve the target BP control – A low dose of a diuretic should be included in this combination Chobanian et al. JAMA. 2003;289:2560–2572; Mancia et al. Eur Heart J. 2007;28:1462–1536; http://www.nice.org.uk/ download.aspx?o=CG034fullguideline (accessed January 2010); Ogihara et al. Hypertens Res. 2009;32:3–107. 9 MANAGEMENT OF HYPERTENSION: GUIDELINE RECOMMENDATIONS FOR COMBINING THERAPIES Multiple antihypertensive agents are needed to achieve BP goals European and US guidelines for combining antihypertensive therapies 10 BENEFITS OF FIXED-DOSE COMBINATION THERAPY Rationale for fixed-dose combinations (FDCs): efficacy; tolerability; compliance and persistence Beneficial impact of FDCs on compliance and persistence, and costs 11 RATIONALE FOR THE USE OF FIXED-DOSE COMBINATIONS: TOLERABILITY FDC therapy may have an improved tolerability profile compared with its single-mechanism components1,2 Low doses of two agents often result in fewer adverse events than high doses of one agent1,2 – Physicians may accept less than optimal BP control to minimise adverse events Compound-specific adverse events can be attenuated, e.g.1,2 – RAS blockers effectively blunt the metabolic effects of diuretics – RAS blockers may attenuate the oedema that is caused by calcium channel blockers (CCBs) 1Sica. Drugs 2002;62:44362; 2Quan et al. Am J Cardiovasc Drugs 2006;6:10313 12 Single-Pill Combinations (SPC) significantly improve Compliance/Treatment adherence (~25%) 30 p < 0.0001 Relative reduction in non-compliance* (%) 26 p < 0.0001 24 20 10 0 Chronic disease (9 studies) Hypertension (4 studies) * With single-pill combination therapy vs free-drug regimens Bangalore et al. Am J Med. 2007;120:713–719. 13 21% MORE PATIENTS ARE FULLY COMPLIANT WITH FIXED-DOSE COMBINATION THERAPY THAN WITH FREECOMBINATION THERAPY Patients fully compliant (%) Cohort study of general practice research data (N=755) 100 Fixed-dose combination therapy 80 Co-administration of two pills 60 40 20 17% 21% 0 0 3 6 9 12 15 18 Months since start of therapy 21 24 27 Patients on free combination had a higher odds ratio (OR) of being non-compliant than patients on FDC: OR 2.09 (95% CI: 1.69, 2.59) Sturkenboom et al. J Hypertens 2005;23(Suppl 2):S236 14 15 Re-appraisal of ESH/ESC Guidelines suggests 4 Preferred Antihypertensive Drug Classes 2009 2007 Diuretics Diuretics β-blockers ARB ARB ONTARGET® ACCOMPLISH HYVET CCB CCB α-blockers ACE-I ACE-I Most rational combinations Combinations used as necessary Mancia et al. Eur Heart J. 2007;28:1462–1536; Mancia et al. J Hypertens. 2009;27:2121–2158. 16 CCB + ARB : The Synergies of Counter-Regulation (2) CCB Arteriodilation Peripheral oedema Effective in low-renin patients Reduces cardiac ischaemia ARB Venodilation Attenuates peripheral oedema Effective in high-renin patients No effect on cardiac ischaemia BP Synergistic BP reduction Complementary clinical benefits 17 et al. Expert Opin Pharmacother. 2006;7:575–581; Sica. Drugs. 2002;62:443–462; Mistry Quan et al. Am J Cardiovasc Drugs. 2006;6:103113. ARB RAS blockade CHF and renal benefits CCB RAS activation No renal or CHF benefits 17 RATIONALE FOR A CCBARB COMBINATION The calcium channel blocker (CCB)angiotensin receptor blocker (ARB) reduces BP by targeting two key BP effector pathways Rationale for a CCBARB: tolerability and efficacy Rationale for CCBARB therapy with Amlodipine/Telmisartan 18 PERIPHERAL OEDEMA ASSOCIATED WITH CCBS Fluid leakage No venous dilation Arterial dilation Fluid leakage Capillary bed Opie et al. In: Opie LH, editor. Drugs for the Heart. 3rd ed. 1991:4273 White et al. Clin Pharmacol Ther 1986;39:438 Gustaffson. J Cardiovasc Pharmacol 1987;10(Suppl 1):S12131 19 COMPLEMENTARY EFFECTS OF A CCB/ARB: REDUCTION OF CCB-ASSOCIATED OEDEMA Arterial dilation (CCB and ARB) Venous dilation (ARB) Capillary bed Opie. In: Opie LH, editor. Drugs for the Heart. 3rd ed. 1991:4273 White et al. Clin Pharmacol Ther 1986;39:438; Gustaffson. J Cardiovasc Pharmacol 1987;10(Suppl. 1):S12131; Messerli et al. Am J Cardiol 2000;86:11827 20 Amlodipine – The longest half-life in class Plasma elimination half-life (h) 35 > 30 30 25 19 20 15 12 10 5 0 5 Lercanidipine 7 Nifedipine 14 16 9 Nimodipine Nisoldipine Nicardipine Felodipine Lacidipine Amlodipine Based on available online product information. 21 Amlodipine - broadest CVP evidence and indication in class PREVENT1 ASCOT-BPLA/CAFE3,4 825 CAD patients (≥ 30%); multicentre, randomized, placebo-controlled 19,257 HTN patients; multicentre, randomized, prospective study vs atenolol CAMELOT2 1,991 CAD patients (≥ 20%); doubleblind, randomized study vs placebo and enalapril 20 mg ALLHAT5 18,102 HTN patients; multicentre, randomized, prospective study vs lisinopril INDICATION: Hypertension Coronary Artery Disease (CAD) Chronic Stable Angina Vasospastic Angina (Prinzmetal’s or Variant Angina) Angiographically documented CAD without heart failure or an ejection fraction < 40% 1. Pitt et al. Circulation. 2000;102:1503–1510; 2. Nissen et al. JAMA. 2004;292:2217–2226; 3. Dahlof et al. Lancet. 2005;366:895–906; 4. Williams et al. Circulation. 2006;113:1213 –1225; 5. Leenen et al. Hypertension.2006;48:374–384. 22 Telmisartan has a Unique Pharmacology Profile in its Class (ARB) … Epro- LoVal- Cande- Olme- Irbe- Telmisartan sartan sartan sartan sartan sartan sartan Highest receptor affinity Receptor dissociation half-life (min) Plasma half-life (h) Longest plasma half-life Losartan Valsartan Candesartan Olmesartan Telmisartan 500 Most lipophilic (high tissue penetration) Cande- Epro- Val- Olme- LoIrbe- Telmisartan sartan sartan sartan sartan sartan sartan 23 Highest selective PPARγ activation † Active metabolite of losartan PPARy fold activation Volume of distribution (L) 500 Epro- Olme- EXP Cande- ValIrbe- Telmisartan sartan 3174† sartan sartan sartan sartan Burnier, Brunner. Lancet. 2000;355:637–645; Brunner. J Hum Hypertens. 2002;16(Suppl 2):S13–S16; Kakuta et al. Int J Clin Pharmacol Res. 2005;25: 41–46; Wienen et al. Br J Pharmacol. 1993;110:245–252; Song, White. Formulary. 2001;36:487–499; Asmar. Int J Clin Pract. 2006;60:315–320; Israili. J Hum Hypertens. 2000;14(Suppl 1):S73–S86; Benson et al. Hypertension. 2004;43:993–1002. 23 … is the Most Studied Amongst ARBs in Mortality and Morbidity Endpoint Trials … 51,878 Number of patients 44,264 19,335 12,565 1,405 Eprosartan MOSES1 4,449 Olmesartan ROADMAP2 6,405 Irbesartan Candesartan Losartan Valsartan IRMA II3 SCOPE6 RENAAL8 Val-HeFT12 TRANSCEND®16 IDNT4 CHARM7 ELITE II9 NAVIGATOR13 PRoFESS®16 OPTIMAAL10 VALIANT14 ONTARGET®16 LIFE11 VALUE15 I-Preserve5 1. Schrader et al. Stroke. 2005;36:1218–1226; 2. http://www.roadmapstudy.org/resident.aspx; 3. Parving et al. N Engl J Med. 2001;345:870–878; 4. Lewis et al. N Engl J Med. 2001;345:851–860; 5. Carson et al. J Card Fail. 2005;11:576–585; 6. Papademetriou et al. J Am Coll Cardiol. 2004;44:1175–1180; 7. www.atacand.com; 8. Brenner et al. N Engl J Med. 2001;345:861–869; 9. Pitt et al. Lancet. 2000;355:1582–1587; 10. Dickstein et al. Lancet. 2002;360:752–760; 11. Dahlof et al. Lancet. 2002;359:955–1003; 12. Cohn et al. N Engl J Med. 2001;345:1667–1675; 13. www.novartis.com; 14. Pfeffer et al. N Engl J Med. 2003;349:1893–1906; 15. Julius et al. Lancet. 2004;363:2022–2031; 15. www.ontarget-micardis.com. 24 Telmisartan 24 … with the broadest CV prevention indication in class (based on the ONTARGET trial program) Patients Based on the Data From The ONTARGET® Trial Program LoEpro- Irbe- Olme- Val- Cande- Telmisartan sartan sartan sartan sartan sartan sartan Hypertension ✔ Treatment of renal disease ✔ ✔ Prevention of stroke in LVH ✔ ✔ ✔ ✔ ✔ ✔ ✔ CV high risk ✔ Atherothrombotic CV disease such as: ✔ ✔ ✔ ✔ ✔ Coronary heart disease Peripheral vascular disease Stroke Type 2 diabetes with target organ damage Heart failure or LV dysfunction Product information provided by EMA (http://www.emea.europa.eu) and eMC (http://emc.medicines.org.uk). ✔ ✔ 25 Telmisartan + Amlodipine® key topics BP efficacy of Telmisartan + Amlodipine BP efficacy of Telmisartan + Amlodipine in added risk patients Safety & Tolerability of Telmisartan + Amlodipine 26 Telmisartan + Amlodipine : Provides consistent BP Reductions across hypertension severities Moderate HTN1 Mild HTN1 140 – <150 150 – <160 160 – <170 170 – <180 180 – <190 190– <200 (n = 39) (n = 34) (n = 31) (n = 13) (n = 305) (n = 71 ) Mean SBP reductions from baseline (mmHg) Baseline SBP = Severe HTN2 T80/A10 1Littlejohn 27 2Neutel et al. J Clin Hypertens. 2009;11:207–213; et al. J Clin Hypertens. 2010: In press; ASH 2010 poster presentation (LB-PO-10). 27 Are you hungry or sleepy ???? Sciences 28 Telmisartan + Amlodipine : 80% of Maximum Effect within 2 Weeks Mean SBP reduction (mmHg) Mean SBP (mmHg) Baseline 80%* – 37.9 mmHg Week 2 – 47.5 mmHg Week 8 A5 and T80/A5 for the first 2 weeks, then forced-titration to A10 and T80/A10, respectively; baseline BP = 185.4/103.2 mmHg Neutel et al. J Clin Hypertens. 2010: In press; ASH 2010 poster presentation (LB-PO-10). 29 Telmisartan + Amlodipine : 83% at goal for a full 24 hour (< 130/80 mmHg) p < 0.0001 100 Patients achieving 24-h ABPM goal* (%) 82.7 80 60 40 37.9 20 0 A10 T80/A10 (n = 58) (n = 52) Littlejohn et al. J Hypertens. 2008;26(suppl 1):S494; White et al. Blood Press Monit. 2010: In press. 30 Telmisartan + Amlodipine key topics BP efficacy of Telmisartan + Amlodipine in added risk patients Safety & Tolerability of Temisartan + Amlodipine 31 Telmisartan + Amlodipine : Consistently High BP reductions in added-risk Hypertensive Patients Mean SBP reductions from baseline (mmHg) Diabetes n = 320 n = 62 Obesity (BMI ≥ 30 kg/m2) n = 189 n = 175 Mild-moderate HTN: SBP ≥150 – <180 mmHg1* *Mean baseline BP = 160,7/90,5 mmHg; **Mean baseline BP = 185.4/103.2 mmHg ***Diabetes, obesity (BMI 30kg/m2), and HTN 1TEAMSTA 2TEAMSTA diabetes study (data on file; Boehringer Ingelheim) severe HTN study (data on file, Boehringer Ingelheim) Metabolic syndrome*** n = 189 n = 36 severe HTN: SBP ≥180 – <200 mmHg2** T80/A10 32 Telmisartan + Amlodipine key topics Safety & Tolerability of Telmisartan + Amlodipine 33 Renal Hyperfiltration Induced by Amlodipine is reduced by Telmisartan Amlodipine L-type Ca channels Amlodipine + Telmisartan L-type Ca channels Increased Decreased Glomerular pressure and filtration Glomerular pressure and filtration Peti-Peterdi; Abstract ESC 2010 (submitted). 34 Telmisartan + Amlodipine : Up to 90% less edema compared to Amlodipine 10mg p < 0.0001 p < 0.0001 20 Patients with peripheral oedema (%) 17.8 15 –90% –71% 10 5.2 5 1.7 0 A10 T40–80+A5 T40–80+A5–A10 (n = 124) (n = 264) (n = 543) Littlejohn et al. J Clin Hypertens. 2009;11:207–213. 35 Why Telmisartan + Amlodipine, because it • Combines the best in class compounds – unique PK/PD evidence – in a single-pill combination • Provides powerful and ‘smart’ BP reductions and high 24h BP control including patients with added-risk such as diabetes and obese • Has a safety & tolerability profile similar to36 37 38 About 50% of hypertensive patients remain uncontrolled (NHANES) -> similar results from EUROSPIRE Percentage of population 100 90 Failed to achieve BP control* 71 75 73 71 68 63 54 ** 50 50 ** ** 25 0 1976– 1980 1988– 1991 1991– 1994 1999– 2000 2001– 2002 2003– 2004 2005– 2006 2007– 2008 Year * BP control defined as BP < 140/90 mmHg; BP < 130/80 mmHg for patients with diabetes or CKD; includes treated and untreated patients, except ** (only treated patients) Chobanian et al. Hypertension. 2003;42:1206–1252; Ong et al. Hypertension. 2007;49:69–75; Ostchega et al. NCHS Data Brief. 2008;3:1–38; Egan et al. JAMA. 2010;303:2043–2050. 39 RATIONALE FOR THE USE OF FIXED-DOSE COMBINATIONS: COMPLIANCE AND PERSISTENCE A single, once-daily pill simplifies the treatment regimen compared with agents given as separate pills – Increases convenience for patients – Reduces the pill burden Increased convenience and lower pill burden likely to improve compliance to and persistence with antihypertensive medications – Overcomes a major barrier to effective BP control Likely to cost less than the individual components prescribed separately Neutel. In: Oparil and Weber, eds. Hypertension. Companion to Brenner & Rector’s The Kidney. 2nd ed. Philadelphia: Elsevier Saunders, 2005. p. 5229 40 CCB + ARB : The Synergies of Counter-Regulation (1) CCB Arteriodilation Peripheral oedema Effective in low-renin patients Reduces cardiac ischaemia BP Synergistic BP reduction Complementary clinical benefits 41 et al. Expert Opin Pharmacother. 2006;7:575–581; Mistry Sica. Drugs. 2002;62:443–462; Quan et al. Am J Cardiovasc Drugs. 2006;6:103113. CCB RAS activation No renal or CHF benefits 41 THE CCBARB TARGETS TWO KEY BP EFFECTOR PATHWAYS (1) Sympathetic nervous system (SNS) SNS activity → noradrenaline binds to α1-adrenergic receptors on vascular smooth muscle → vasoconstriction1 SNS also stimulates renin secretion from the kidney, thereby activating the RAS2 CCBs inhibit SNS-induced vasoconstriction by blocking influx of calcium ions (needed for contraction) through voltage-gated calcium channels → vasodilation3,4 Other effects of CCBs: natriuresis; inhibition of aldosterone release; interference with angiotensin II-mediated vasoconstriction4 1Grassi. J Hypertens 2001;19:1713–16; 2Mancia and Grassi. http://www.sns-web.org/pages/advances/11/article.asp; 3Robertson and Robertson. In: Hardman JG, Limbard JG, editors-in chief. Goodman & Gilman’s The Pharmacological Basis of Therapeutics. 9th ed. 1996. p. 759–79 4Prisant. In: Oparil S, Weber MA, editors. Hypertension: Companion to Brenner & Rector’s The Kidney. 2nd ed. 2005. p. 683–704 42 THE CCBARB TARGETS TWO KEY BP EFFECTOR PATHWAYS (2) Renin angiotensin system (RAS) Release of renin catalyses conversion of angiotensinogen into angiotensin I, which is converted by ACE to angiotensin II → – Vasoconstriction; increased aldosterone and sodium/water retention; SNS activation ARBs block the effects of angiotensin II by binding to AT1 receptors – Arterial and venous dilation – Reduced SNS activity – Reduced secretion of aldosterone and increased secretion of sodium and water Mistry et al. Expert Opin Pharmacother 2006:7:575–81 43 Clinical Evidence With ARBs AFTER ONTARGET® CV high risk ONTARGET® trial programme Heart failure VALIANT CHARM Val-HeFT ELITE II Hypertension MI and stroke LIFE VALUE Microalbuminuria Atherosclerosis and LVH Endothelial dysfunction Remodelling Ventricular dilation/ cognitive dysfunction Macroproteinuria Nephrotic proteinuria Risk factors: hypertension, diabetes, obesity, smoking, age Dzau et al. Circulation. 2006;114:2850–2870; Dzau, Braunwald. Am Heart J. 1991;121:1244–1263; Yusuf et al. Lancet. 2004;364:937–952; The ONTARGET Investigators. N Engl J Med. 2008;358:1547–1559. . ESRD CHF/ secondary stroke Cardio/ cerebrovascular death 44 Telmisartan : Numerically better than Valsartan Agent Baseline BP Telmisartan+Amlodipine (all doses)1 153/102 mmHg 0 T40/A5 T40/A10 T80/A5 T80/A10 0 -5 Agent Baseline BP Valsartan with:2 5 mg amlodipine 10 mg amlodipine 153/99 mmHg 157/99 mmHg V160/A5 V160A10 V320/A10 -16.2 -15.9 mmHg † mmHg † -5 -10 -15 -10 -15 -13.2 -15.5 -20 V320/A5 -19.3 -20 -19.6 -22.2 -25 * Indirect SBP -23.9 -25 SBP comparisons: study design varied; †Placebo-corrected values 1.TWYNSTA™ [prescribing information]. Ridgefield, CT: Boehringer Ingelheim Pharmaceuticals, Inc, 2009; 2. Exforge [prescribing information]. East Hanover, CJ: Novartis Pharmaceuticals Corporation, 2009. 45 Telmisartan + Amlodipine : up to 87% of added-risk hypertensive patients archive BP goal BP goal rate (<140/90 mmHg) after 8 weeks (%) 100 More moderate systolic HTN (baseline BP 160.7/90.5 mmHg)2 More mild systolic HTN (baseline BP 153.2/101.7 mmHg)1 87,0 80 84,6 81,7 71,4 68,2 68,2 60 40 20 (n = 23) (n = 320) (n = 71) (n = 198) (n = 13) (n = 198) 0 Diabetes Obese BMI ≥ 30kg/m2 * Presence of diabetes, obesity (BMI 30kg/m2), and HTN 1Factorial design study (data on file; Boehringer Ingelheim Pharmaceuticals, Inc); diabetes study (data on file, Boehringer Ingelheim) 2TEAMSTA Metabolic syndrome* T80/A10 46 Telmisartan + Amlodipine : Comparable Safety & Tolerability Profile of 80/5-10 and 40/5-10 combinations 100 Patients per 100 patient years 90 T40/A5-101,2 (n=1814) T80/A5-101,2 (n=1008) 3,0 3,9 80 70 60 50 40 30 20 13,2 12,5 6,7 10 0 Drug related AEs AE = Adverse events 1. Neldam et al. ESH 2010 poster presentation (P-95) 2. Neldam et al. ESH 2010 poster presentation (P-90) 6,4 Peripheral edema 2,4 AEs leading to premature discontinuation 3,4 Serious AEs 47