Handout H6 The scope of meta-analysis: Meta-analysis of observational studies 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Objectives • Understand the importance of systematic reviews of observational studies • Understand the limitations of meta-analysis in observational studies • Understand the difficulties of avoiding publication bias in observational studies 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Why do we need observational studies? • Randomisation may be – impossible – unnecessary – inappropriate Black, BMJ 1996 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Potentials of systematic reviews • More objective appraisal of the evidence than traditional narrative reviews applies equally to OS & RCT • May resolve uncertainty when original research, reviews and editorials disagree applies equally to OS & RCT • May generate promising research questions to be addressed in future studies applies equally to OS & RCT • Meta-analysis will enhance the precision of effect estimates, leading to reduced probability of false negative results BUT in OS may be a precise biased result 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Meta-analysis • A statistical analysis which combines the results of several independent studies considered by the analyst to be ‘combinable’ Huque 1988 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Assumptions in meta-analysis • “Fixed-effects model”: Underlying effect is the same value (fixed) in each study. The differences between study results are solely due to the play of chance. • “Random-effects model”: Treatment effect for the individual studies are assumed to vary around some overall central effect 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Fundamental difference in assumptions & how they apply to MA of RCT or observational studies • In meta-analysis of observational studies confounding, residual confounding and bias: – May introduce heterogeneity – May lead to misleading (albeit very precise) estimates • In well-conducted RCT there should not be confounding 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Trial (Year) Barber (1967) Reynolds (1972) Wilhelmsson (1974) Ahlmark (1974) Multicentre International (1975) Yusuf (1979) Andersen (1979) Rehnqvist (1980) Baber (1980) Wilcox Atenolol (1980) Wilcox Propanolol (1980) Hjalmarson (1981) Norwegian Multicentre (1981) Hansteen (1982) Julian (1982) BHAT (1982) Taylor (1982) Manger Cats (1983) Rehnqvist (1983) Australian-Swedish (1983) Mazur (1984) EIS (1984) Salathia (1985) Roque (1987) LIT 91987) Kaul (1988) Boissel (1990) Schwartz low risk (1992) Schwartz high risk (1992) SSSD (1993) Darasz (1995) Basu (1997) Aronow (1997) Mortality results from 33 trials of beta-blockers in secondary prevention after myocardial infarction Adapted from Freemantle et al BMJ 1999 0.80 (0.74 - 0.86) Overall (95% CI) 0.1 0.2 0.5 1 2 5 10 Relative risk (95% confidence interval) Results from 29 studies examining the association between intact foreskin and the risk of HIV infection in men Study Allen Barongo Bollinger Bwayo Bwayo Cameron Carael Chao Chiasson Diallo Greenblatt Grosskurth Hira Hunter Konde-Luc Kreiss Malamba Mehendal Moss Nasio Pepin Quigley Sassan Sedlin Seed Simonsen Tyndall Urassa 1 Urassa 2 Urassa 3 Urassa 4 Urassa 5 Van de Perre 0.2 0.5 1 2 Relative risk (95% confidence interval) 5 10 Adapted from Van Howe Int J STD AIDS 1999 Formaldehyde exposure and lung cancer SMR (95% CI) 150 100 50 0 Anatomists, Funeral Directors Pathologists Embalmers (3 Cohorts) (7 Cohorts) Industrial Workers (14 Cohorts) Blair et al Scan J Work Environ Health 1990 Dietary fat and breast cancer Relative Risk (95% CI) 1.8 1.6 1.4 1.2 1.0 0.8 0.6 12 Case-Control Studies 6 Cohort Studies Boyd et al Br J Cancer 1993 Intermittent sunlight exposure and melanoma Odds Ratio (95% CI) 3 2 1 0 7 Case-Control Studies with Blinding 9 Case-Control Studies without Blinding Nelemans et al J Clin Epidemiol 1995 Test of homogeneity • Examines the possibility of excess variability between the results of the different studies • Has low power if the number of studies is small • Can get a set of homogeneous but spurious findings 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Beta-carotene and cardiovascular mortality Cohort Country Male health workers USA Social insurance, men Finland Social insurance, women Finland Male chemical workers Switzerland Hyperlipidaemic men USA Nursing home residents USA Cohorts combined 0.1 0.5 0.75 1 1.25 1.5 Relative risk (95% CI) Jah et al Ann Intern Med 1995 Beta carotene and cardiovascular disease Cohorts Male health workers USA Social insurance, men Finland Social insurance, women Finland Male chemical workers Switzerland Hyperlipidaemic men USA Nursing home residents USA Trials Cohorts combined Male smokers Finland Skin cancer patients USA (Ex)-smokers, asbestos workers USA Male physicians USA Trials combined 0.1 0.5 0.75 1 1.25 Relative risk (95% CI) Egger et al. BMJ 1998;316:140-4 1.5 1.75 “Well, so much for antioxidants.” Smoking and suicide No of cigarettes MRFIT screenees 1-14 14-24 25+ Whitehall I 1-14 14-24 25+ North Karelia men 1-14 14-24 25+ Kuopio men 1-14 14-24 25+ Meta-analysis 1-14 14-24 25+ 0.2 1 2 5 10 25 Relative rate (95% CI) Davey Smith et al Lancet 1992 Smoking and homicide • Non-smoker 1.00 • 1-2 packs/day 1.71 (1.29-2.28) • 2+ packs/day 2.04 (1.32-3.15) 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Fundamental difference in assumptions • In meta-analysis of observational studies confounding, residual confounding and bias: – May introduce heterogeneity – May lead to misleading (albeit very precise) estimates 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme What is the appropriate weighting factor? Inverse of variance? Case-control studies of Helicobacter pylori infection and CHD Study Cases +ve Controls +ve Cases -ve Controls ve Crude OR Adjusted OR Weight Danesh 1999a 472 272 650 850 2.3 1.9 44% Danesh 1999b 134 294 112 348 1.4 1.3 17% Patel 1995 56 135 27 170 2.6 2.8 6% Murray 1995 102 1117 33 863 2.4 1.5 9% McDonagh 1997 315 625 134 353 1.3 0.9 m 1.0 f 25% 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Two case-control studies of Helicobacter pylori infection and CHD Danesh et al 1999 a Danesh et al 1999 b Numbers in study 2224 888 Response rate controls <20% 60% Response rate cases ~60% 56% Adjustment for social position + +++ Other adjustments + +++ Representative cases? No Fairly representative Representative controls? No Fairly representative OR sex/age adjusted 2.3 1.4 OR fully adjusted 1.9 1.3 Weight in meta-analysis 44% 17% 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Prospective and nested case-control studies of Helicobacter pylori infection and CHD Study Cases +ve Controls +ve Cases -ve Controls -ve Crude OR Strachan 1998 204 1061 82 449 1.05 1.02 17% Wald 1997 308 595 340 701 1.07 1.06 37% Aromaa 1998 229 411 47 116 1.38 - 9% Folsom 1998 111 257 106 241 0.98 0.97 13% Ossewaarde 1998 39 84 15 24 0.74 - 2% Whincup 2000 401 740 104 285 1.48 1.30 20% 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Adjusted Weight OR Erasmus Summer Programme In RCT meta-analyses the appropriate study weights should relate to precision of effect estimates (e.g. inverse of variance). In observational meta-analyses this may not generally be the case. 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Inverse of variance weighting • Can lead to magnification of pooled effect estimates when confounding and bias involved (e.g. H pylori) • Can lead to under-estimation of effect estimates when measurement error is important 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Huxley, Lancet 2002 Publication bias in MA / SR of observational studies Reporting bias in observational research Data collected (e.g cohort study) Data analysed Report written Paper published “I regret to inform you that the Journal of xxx will not be able to use your manuscript … We think the study is welldesigned, with a fair follow-up and appropriate statistical analysis, but the negative results found can only be published as a Letter to the editor …” Rejection of ‘negative’ prospective cohort study finding of association of d-dimer with CHD. May 2006 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Genetic meta-analysis may be an exception … To the homogeneity and “spurious precision” problems… But may be particularly prone to publication bias 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Funnel plot of meta–analysis of ACE I/D and CHD Standard error 0.0 0.1 0.2 0.3 0.4 0.33 0.5 0.66 1.0 1.5 Odds ratio 2.0 3.0 Conclusions • The principles of systematic reviews are applicable to any research design • Reviews of observational studies should always be systematic • Much attention should be given to exploring possible sources of heterogeneity • HOWEVER: Meta-analysis of observational studies will often produce misleading and spuriously precise estimates • Trial registers should solve much of the problems of publication bias in RCT, but trying to solve publication bias in observational studies impossible? 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme Future work • We need to define optimal search strategies to identify epidemiological studies in the literature • We need validated instruments to assess the study quality at the design, conduct and analysis level • We need to improve the quality of reporting of epidemiological studies • We need to facilitate individual patient data analyses • We need to better define the place of meta-analysis in systematic reviews of epidemiological studies 11 August 2010 Topics in Meta-Analysis (Matthias Egger) Erasmus Summer Programme