Taking the tablets, Do we / should we? Slides courtesy of David Marin March 2011 | TAS11-003c • It’s one thing to take a tablet over a short period • It’s another thing to take it for life March 2011 | TAS11-003c There is a great variability in the response to imatinib. I wonder why BCR-ABL/ABL ratio (%) 100 10 CCyR 1 3 log 0.1 0.01 0.001 0.0001 Time from start of imatinib March 2011 | TAS11-003c Slide courtesy of Dr David Marin Study design BCR/ABL/ABL ratio (%) 100 Imatinib plasma level 10 1 MEMS 0.1 0.01 0.001 TKD mutations Time from start of imatinib • hOCT1 level • MDR-1 polymorphisms • BCR-ABL transcript type • BCR-ABL transcript level • Sokal score • Haemoglobin • White blood cell count • Sex • Age March 2011 | TAS11-003c We correlated all these variables with the molecular response achieved by the patient Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. Slide courtesy of Dr David Marin Microelectronic Monitoring System (MEMS 6 Trackcap) • Records the time of opening the container • Most reliable method of measuring adherence • Our patients: not told about the chip March 2011 | TAS11-003c Slide courtesy of Dr David Marin March 2011 | TAS11-003c Slide courtesy of Dr David Marin Long-term adherence to imatinib 100 Proportion of patients (%) 90 80 70 60 50 40.2% 40 30 20 25.3% 13.8% 10 0 <80% 12.6% 8% 80–90% 90–95% 95–99% ≥100% Percentage of intended dose March 2011 | TAS11-003c Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. Slide courtesy of Dr David Marin Lack of adherence is underestimated by conventional methods Proportion of patients (%) 100 90 80 70 60 Self reporting Pill count MEMS 50 40 30 20 10 0 <80% 80–90% 90–95% 95–99% ≥100% Percentage of intended dose March 2011 | TAS11-003c Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. Slide courtesy of Dr David Marin Unintentional non-adherence 13/21 patients “And sometimes you just forget. It’s very strange. It’s almost a surprise when you don’t take it” “They [the pharmacy] had no medication for me, so I went for nearly a week with no medication.” March 2011 | TAS11-003c Slide courtesy of Dr David Marin Intentional non-adherence 10/21 patients “Oh I can’t be bothered tonight, it’s not going to kill me [to miss a dose] – sort of thing, so I just go to sleep” “I thought there was no way I was going [on holiday] and being tired. So I did actually stop taking the tablets for a week before I went, and I didn’t take them for the first half of the week I was there” March 2011 | TAS11-003c Slide courtesy of Dr David Marin 12/21 patients said: “The odd missed dose doesn’t matter” “I suppose, I’m not a doctor, but I don’t think missing one pill, or 3 pills, in a month affects me at all” “So I don’t feel I am putting myself in any danger by not taking an odd dose now and again” March 2011 | TAS11-003c Slide courtesy of Dr David Marin Reasons for poor adherence Theme Sub-theme 1.1 Unintentional non-adherence Forgetting Accidentally taking too much Prescribing error No imatinib availability at pharmacy Frequency of unintentional non-adherence 1.2 Intentional non-adherence Because of side effects Because of socialising / dining out / drinking alcohol Because of travelling Because of diversion from planned activities Because of temporary illness (bug / cold) Because of risk of pregnancy Because of side negative emotions & feelings Because of “no real reason / lack of discipline” Changed doses Frequency intentional Contemplating future non-adherence March 2011 | TAS11-003c Slide courtesy of Dr David Marin 6-year probability of MMR according to the measured adherence rate P<0.001 Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. March 2011 | TAS11-003c Slide courtesy of Dr David Marin 6-year probability of CMR according to the measured adherence rate P=0.002 Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. March 2011 | TAS11-003c Slide courtesy of Dr David Marin Other variables are also predictive for the achievement of molecular response Variables n MMR (%) 4-log (%) CMR (%) 40 47 P=0.036 59.2 80.7 1.186, P=0.012 P=0.03 39.5 69.1 1.323, P=0.01 P=0.011 14.7 47.6 1.209, P=0.07 Leukocytes ≤140 x 109/l >140 x 109/l RR 44 43 P=0.012 78.8 63.1 0.996, P=0.008 P=0.022 56.7 37.6 0.996, P=0.015 P=0.17 35.4 28.1 0.996, P=0.11 BCR-ABL1/ABL1 ratio ≤100% >100% RR 44 43 P=0.25 71.4 52.6 0.996, P=0.44 P=0.038 53.0 26.6 0.971, P=0.002 P=0.1 32.7 8.4 0.979, P=0.13 hOCT1 transcript level ≤0.16 >0.16 RR 30 30 P<0.001 55.2 81.4 2.199, P<0.001 P=0.01 42.0 64.8 1.990, P=0.001 P=0.02 16.6 45.3 1.665, P=0.04 Imatinib plasma level ≤1 g/ml >1 g/ml RR 43 41 P=0.02 60.1 83.2 2.11, P=0.01 P=0.07 53.0 68.0 2.50, P=0.06 P=0.14 23.3 44.4 2.25, P=0.09 64 23 P<0.001 93.7 13.9 1.093, P<0.001 P<0.001 76.0 4.3 1.104, P=0.002 P=0.002 43.8 0 RR= 1.135, P=0.012 Haemoglobin ≤115 g/l >115 g/l RR Adherence rate >90% ≤90% RR Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. March 2011 | TAS11-003c Slide courtesy of Dr David Marin The level of hOCT1 measured at diagnosis is predictive for achievement of molecular response 1.0 CMR Cumulative incidence of CMR incidence of CMR Cumulative Cumulativeincidence incidence of MMR of MMR Cumulative MMR p<0.001 p=0.0003 P<0.001 0.9 hOCT1 0.8 0.7 0.6 0.5 hOCT1 0.4 0.3 0.2 0.1 0.0 0 6 12 Months 18 24 30 36 42 48 54 60 66 72 Months startof of imatinib therapy from from start imatinib therapy 1.0 P=0.02 p=0.02 0.9 0.8 0.7 0.6 hOCT1 0.5 0.4 0.3 0.2 hOCT1 0.1 0.0 0 6 12 18 24 30 36 42 48 54 60 66 72 Months from start of imatinib therapy Months from start of imatinib therapy hOCT1=human organic cation transporter 1 March 2011 | TAS11-003c Slide courtesy of Dr David Marin But adherence to therapy is the critical factor for achieving molecular response • MMR – Adherence to imatinib therapy, RR=11.17 (P=0.001) – hOCT1 transcript level, RR=1.79 (P=0.038) • CMR – Adherence to imatinib therapy, RR=19.35 (P=0.004) RR: relative risk March 2011 | TAS11-003c Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. Slide courtesy of Dr David Marin Imatinib plasma levels are not an independent predictor of molecular response P=0.003 P=0.68 Total population Adherent patients Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. March 2011 | TAS11-003c Slide courtesy of Dr David Marin Study design BCR/ABL/ABL ratio (%) 100 10 1 MEMS 0.1 0.01 0.001 Time from start of imatinib • hOCT1 level • MDR-1 polymorphisms • BCR-ABL transcript type • BCR-ABL transcript level • Sokal score • Haemoglobin • White blood cell count • Sex • Age March 2011 | TAS11-003c We correlated all these variables with the molecular response achieved by the patient Marin D et al. J Clin Oncol 2010; 28(14): 2381–2388. Slide courtesy of Dr David Marin Poor adherent patients have a higher probability of losing the CCyR and a lower EFS 1.0 P<0.0001 p<0.0001 0.9 0.9 0.8 0.8 Probability of imatinib failure Cumulate incidence of loss of CCyR 1.0 Adherence rate ≤85%, n=18 0.7 Adherence rate >85%, n=69 0.6 0.5 0.4 0.3 0.7 p<0.0001 P<0.0001 0.6 0.5 0.4 0.3 0.2 0.2 Adherence rate ≤85%, n=18 0.1 0.1 Adherence rate >85%, n=69 0.0 0.0 0 March 2011 | TAS11-003c 6 12 Months from enrolment 18 24 0 6 12 Months from enrolment 18 24 Slide courtesy of Dr David Marin Probability of loss of CCyR according to the level of molecular response 1.0 CCyR no MMR, n= 92 n=92 CCyrwith with no MMR, 0.9 0.8 CCyR with MMR, n= 32 n=32 CCyR with MMR, 0.8 0.7 P=0.04 p= 0.04 0.6 0.5 0.4 0.3 23.9% 0.2 Probability of loss of CCyR Probability of loss of CCyR 1.0 12 months 0.9 18 months CCyR with nono MMR, n=91 n=91 CCyr with MMR, CCyR with MMR, n= 41n=41 CCyR with MMR, P=0.04 p= 0.006 0.7 0.6 0.5 0.4 24.6% 0.3 0.2 0.1 2.6% 0.0 0.1 0% 0.0 0 6 12 18 24 30 36 42 48 Months from starting imatinib therapy 54 60 0 6 12 18 24 30 36 42 48 54 60 Months from starting imatinib therapy Marin D et al. Blood 2008; 112(12): 4437–4444. March 2011 | TAS11-003c Slide courtesy of Dr David Marin On multivariate analysis, the adherence rate and having failed to achieve a major molecular response are the only independent predictors for loss of CCyR and discontinuation of imatinib therapy. March 2011 | TAS11-003c Slide courtesy of Dr David Marin Adherence and the achievement of MMR are the only independent predictors for outcome 1.0 1.0 P<0.0001 p<0.0001 0.9 MMR, n=53 0.8 Probability of imatinib failure Cumulate incidence of loss of CCyR 0.9 CCyR, no MMR, Adherence Rate ≤85%, n=11 0.7 CCyR, no MMR, Adherence Rate >85%, n=23 0.6 0.5 0.4 0.3 p<0.0001 P<0.0001 0.2 p=0.0009 P=0.0009 0.7 0.5 0.4 0.3 0.0 0.0 March 2011 | TAS11-003c 12 Months from enrolment 18 24 MMR, n=53 0.2 0.1 6 p<0.0001 P<0.0003 P<0.0001 0.6 0.1 0 p=0.003 P=0.003 0.8 CCyR, no MMR, Adherence Rate ≤85%, n=11 CCyR, no MMR, Adherence Rate >85%, n=23 0 6 12 18 24 Months from enrolment Slide courtesy of Dr David Marin Conclusions • A significant proportion of patients fail to take the prescribed dose of imatinib • Adherence to therapy is the critical factor for optimal response • Poor adherence is the main reason for imatinib failure in patient on long term therapy • Intentional and unintentional reasons for non-adherence • Poor understanding of consequences March 2011 | TAS11-003c Slide courtesy of Dr David Marin