Case-Based Workshop With the Experts: Evolving Management Strategies in Non-Hodgkin’s Lymphoma This program is supported by educational grants from Multidisciplinary Approaches for the Diagnosis and Optimal Treatment of MCL Owen A. O’Connor, MD, PhD Professor of Medicine and Pharmacology Deputy Director for Clinical Research and Cancer Treatment NYU Cancer Institute Chief, Division of Hematologic Malignancies and Medical Oncology NYU Langone Medical Center New York, New York Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology About These Slides Our thanks to the authors who gave permission to include their original data Users are encouraged to use these slides in their own noncommercial presentations, but we ask that content and attribution not be changed. Users are asked to honor this intent These slides may not be published or posted online without permission from Clinical Care Options Disclaimer The materials published on the Clinical Care Options Web site reflect the views of the authors of the CCO material, not those of Clinical Care Options, LLC, the CME providers, or the companies providing educational grants. The materials may discuss uses and dosages for therapeutic products that have not been approved by the United States Food and Drug Administration. A qualified healthcare professional should be consulted before using any therapeutic product discussed. Readers should verify all information and data before treating patients or using any therapies described in these materials. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Program Faculty Program Director Owen A. O’Connor, MD, PhD Mary Jo Lechowicz, MD Professor of Medicine and Pharmacology Deputy Director for Clinical Research and Cancer Treatment NYU Cancer Institute Chief, Division of Hematologic Malignancies and Medical Oncology NYU Langone Medical Center New York, New York Assistant Professor Hematology/Oncology Emory University Atlanta, Georgia Core Faculty Christopher R. Flowers, MD, MS Director, Lymphoma Program Medical Director, Oncology Data Center Assistant Professor Bone Marrow and Stem Cell Transplantation Department of Hematology and Oncology Emory University Atlanta, Georgia Julie M. Vose, MD Neumann M. and Mildred E. Harris Professor Chief, Section of Hematology/ Oncology Professor of Medicine University of Nebraska Medical Center Omaha, Nebraska Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Faculty Disclosures Christopher R. Flowers, MD, MS, has disclosed that he has received consulting fees from Celgene and Prescription Solutions and research funding from Millennium, Pfizer, and Spectrum. He has also disclosed that he has other (nonpaying advisory boards) relationships with Biogen Idec and Genentech. Mary Jo Lechowicz, MD, has no significant financial relationships to disclose. Owen A. O’Connor, MD, PhD, has disclosed that he has served as consultant for Allos, Astellas, Lilly, and Millennium and has received research support from Allos, Astellas, Lilly, Merck, Millennimum, and Spectrum. Julie M. Vose, MD, has disclosed that she has received research funding from Allos Therapeutics, AstraZeneca, Bristol-Myers Squibb, Celgene, Exelixis, Genentech, Genzyme, GlaxoSmithKline, Novartis, Pharmacyclics, and US Biotest. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Mantle Cell Lymphoma Median age: 58 yrs M:F ratio: 3:1 Typically advanced stage B symptoms: < 50% cases 90% extranodal involvement: BM, blood, liver, GI Generalized adenopathy: 70% to 90% CNS involvement at relapse: 4% to 22% (↑ with blastoid) Fisher RI. Ann Oncol. 1996;7(suppl 6):S35-S39. Armitage JO. Oncology (Williston Park). 1998;12 (10 suppl 8):48-55. Romaguera JE, et al. Cancer. 2003;97:586-591. Gill S, et al. Leuk Lymphoma. 2008;49:2237-2239. Frontline MCL Therapy Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology R-CHOP vs CHOP in Untreated MCL 64 patients randomized in each arm Response, % R-CHOP CHOP P Value RR 94 75 .005 CR 34 7 .0002 No differences observed in PFS or OS between treatment arms Lenz G, et al. J Clin Oncol. 2005;23:1984-1992. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology STiL: Frontline B-R vs R-CHOP CD20+ FL, SLL, MZL, MCL, LPL, stage III-IV, untreated, 18 yrs of age or older (N = 549) Bendamustine-Rituximab (n = 260) B 90 mg/m2 on Days 1, 2 + R 375 mg/m2 on Day 1 Max 6 cycles q4w R-CHOP (n = 253) Max 6 cycles q3w Primary endpoint: PFS (noninferiority B-R < 10% at 3 yrs) Secondary endpoints: ORR, CR, toxicity, stem cell mobilization Rummel MJ, et al. ASH 2009. Abstract 405. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology STiL: BR vs R-CHOP, All Disease Types 513 evaluable patients > 1/2 FL/18% MCL No difference in ORR between treatment arms CR PFS – B-R: 40% – B-R: 55 mos – R-CHOP: 31% – R-CHOP: 35 mos – P = .03 – P < .05 BR toxicity profile: alopecia, neutropenia, thrombocytopenia, infections Rummel MJ, et al. ASH 2009. Abstract 405. Dose-Intensive Approaches Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology MCL: High-Dose Therapy/ASCT—CHOP Backbone 1.0 ASCT IFN P = .0108 0.8 0.8 P (EPS) Survival Probability 1.0 0.6 0.4 0.2 0.6 0.4 0.2 0 0 1 2 3 4 5 Yrs After End of Induction Therapy Pts at Risk, n ASCT 62 38 IFN 60 33 Response, Yrs 31 19 17 9 10 6 6 3 2 IFN Arm ASCT arm P Value Median DOR 1.6 3.7 .0004 Median TTF (ITT) 1.4 2.6 .0001 OS 5.4 7.5 .075 0 0 10 20 30 Mos 40 50 60 Tripled CR rate after DHAP (12% vs 61%)[2] Median EFS: 84 mos vs 51 mos prior to rituximab[1] 1. Lefrere F, et al. Leukemia. 2002;16:587-593. 2. Delarue R, et al. ASH 2008. Abstract 581. 3. Dreyling M, et al. ASH 2008. Abstract 769. Dreyling M, et al. Blood. 2005;105:2677-2684. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology MCL: High-Dose Therapy/ASCT—More Intensive Induction B EFS R-HDS low risk R-HDS int-high risk 80 60 40 20 0 EFS 100 Percent Survival 100 Percent Survival A P < .0001 MCL2 (n = 160) MCL1 (n = 41) 80 60 40 20 P < .0001 0 0 12 24 36 48 60 72 84 96 108 120 Mos 0 2 4 6 8 10 Yrs Small series EFS, PFS, OS, and mol CR/previous CHOP—ASCT Long follow-up Bias? (toxic regimen) Preemptive rituximab maintenance based on QPCR MCL3/similar + ibritumomab tiuxetan prior ASCT[3] Magni M, et al. Bone Marrow Transplant. 2009;43:509-511. 2. Geisler et al. Blood. 2008;112:269-293. 3. Kolstadt, et al. ASH 2009. Abstract 932. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology EU Trial: MCL Younger Protocol Design Patients younger than 65 yrs of age with MCL, ECOG PS < 2, Ann Arbor stage II-IV, eligible for highdose therapy (2 + 1) x R-CHOP/DHAP alternating (stem cell mobilization after course 6) 4 x R-CHOP 2 x R-CHOP TBI 10 Gy Ara-C 4 x 1.5 g/m2 + Melphalan 140 mg/m2 + PBSCT DexaBEAM (stem cell mobilization) Primary endpoint: time to treatment failure Secondary endpoints: response rates, OS, toxicity Hermine O, et al. ASH 2010. Abstract 110. Cyclo 120 mg/kg + TBI 12 Gy PBSCT Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology EU Trial: Results Time to Treatment Failure PP MCL Younger: Remission Duration After ASCT Median follow-up: 32 mos R-DHAP, median not reached R-CHOP, median: 49 mos 1.0 Median follow-up: 30 mos R-DHAP, median not reached R-CHOP, median: 48 mos 1.0 HR: 0.68 0.8 Probability Probability 0.8 0.6 0.4 0.2 0.6 0.4 0.2 P = .0382 (1-sided sequential test) P = .0059 0 0 0 12 24 36 48 60 Mos Since Randomization Pts at Risk, n R-DHAP 208 147 99 67 29 11 R-CHOP 212 134 95 66 36 11 Hermine O, et al. ASH 2010. Abstract 110. 72 0 0 0 Pts at Risk, n R-DHAP 133 R-CHOP 133 12 24 36 48 60 Mos Since Retransfusion 99 92 69 66 45 43 19 15 0 1 72 0 Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology High-Dose Therapy/ASCT: Summary No difference in ORR (97%) or CR/CRu (79/82%) postASCT Measure, n (%) R-CHOP R-CHOP/ R-DHAP P Value CR 54 (26) 72 (36) .032 CR or CRu 83 (40) 111 (55) .0028 CR or CRu or PR 186 (90) 188 (94) .14 Relapse after CR/CRu/PR 49 (23) 22 (10) -- Hermine O, et al. ASH 2010. Abstract 110. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Comparison of Dose-Intensive/High-Dose Therapy in MCL Ara-C–containing induction regimens for MCL Study Therapy N Age Limit, Yrs 5-Yr EFS, % 5-Yr OS, % Follow-up, Mos Nordic[1] MCL-2 (R + Maxi-CHOP + HD Ara-C + Maint R) 160 < 66 63 74 40 GITIL[2] (R) HDS-ASCT* 77 < 61 61 74 50 R-HyperCVAD 97 Up to 80 (1/3 > 65) 48 (FFS) 65 50 ≤ 65 60 (FFS) 76 50 MDACC[3,4] CALGB R-Maxi-CHOP-MTX/ VP16-Ara-C/CBV 78 18-69 56 (PFS 64 50 EU younger patients R-CHP/DHAP-TAM → ASCT 208 < 65 65 (TTF) 78 32 *4 MDS and 3 solid tumors. Compare to R-CHOP PFS 25% at 52 yrs 1. Geisler CH, et al. ASH 2007. Abstract LBA1. 2. Cortelazzo S, et al. ASH 2007. Abstract 1282. 3. Romaguera JE, et al. J Clin Oncol. 2005;23:7013-7023. 4. Fayad L, et al. Clin Lymphoma Myeloma. 2007;8(suppl 2):S57-S62. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology SWOG 0213: R-HyperCVAD in MCL Outcome 100 Median age, yrs 57 80 Mantle zone variant, % 57 Grade 3/4 infection, % 34 Discontinued Rx/toxicity, %* 42 Patients (%) Measure OS PFS 60 40 20 0 0 1 Efficacy, n (%) ORR 35 (88) Survival, % CR/CRu 23 (58) PR 12 (30) *No details on dose reductions Epner EM, et al. ASH 2007. Abstract 387. 2 3 4 5 Yrs From Registration 1 Yr 2 Yrs PFS 89 64 OS 91 76 6 Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Modified R-HyperCVAD: Design A S S E S S Rituximab 375 mg/m2 on Day 1 + Cyclophosphamide 300 mg/m2 q12 hrs on Days 1-3 + Doxorubicin 50 mg/m2 48-hr CI on Days 1-2 + Vincristine 2 mg IV on Day 3 + Dexamethasone 40 mg PO on Day 1-4 Rituximab 375 mg/m2 once wkly × 4 q6m × 4 CR, CRu, PR No vincristine or steroids on Day 11/no methotrexate, no Ara-C/monthly cycles x 6 Median follow-up: 37 mos 22 untreated MCL Toxicity mainly hematologic Patients ORR (n = 22) 77 CR/CRu 64 PR 14 Patients Alive (%) Clinical Response, % 100 OS 80 60 PFS 40 Median PFS: 37 mos 20 0 0 Kahl BS, et al. Ann Oncol. 2006;17:1418-1423. Median OS: not reached 10 20 30 Mos 40 50 60 Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology NCCN Study in MCL: PFS PFS K-M 2-Group Log Rank P Value R-hyperCVAD vs R-CHOP < .001 R-CHOP+HDT/ASCR vs R-CHOP < .001 R-hyperCVAD vs R-CHOP + HDT/ASCR LaCasce A, et al. ASH 2009. Abstract 403. .58 Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology NCCN Study in MCL: OS OS K-M 2-Group Log Rank P Value R-hyperCVAD vs R-CHOP .02 R-CHOP+HDT/ASCR vs R-CHOP .20 R-hyperCVAD vs R-CHOP + HDT/ASCR .64 LaCasce A, et al. ASH 2009. Abstract 403. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology FCM vs R-FCM in Relapsed Indolent Lymphoma 4 cycles FCM vs R-FCM Relapsed indolent lymphoma R Fludarabine Cyclophosphamide Mitoxantrone + Rituximab Fludarabine Cyclophosphamide Mitoxantrone 128 patients evaluable with relapsed indolent NHL; 48 evaluable patients with MCL Outcome in MCL Patients FCM (n = 24) FCM-R (n = 24) P Value ORR, % 46 58 .282 CR, % 0 29 NR Median PFS, mos 4 8 .3887 Median OS, mos 11 Not reached .0042 Forstpointner R, et al. Blood. 2004;104:3064-3071. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Frontline Radioimmunotherapy in MCL Study MSKCC 01029[1] ECOG 1499[2] Design Tositumomab CHOP x 6 No rituximab Results/Comments Feasible 35% eval pts had mol CR post-RIT Not improved post-CHOP R-CHOP x 4 56 pts/med age: 61 yrs Ibritumomab tiuxetan Tripled CR rate: 45% (14% after R-CHOP) Med FFS at 27 mos (> R-CHOP alone) 1. Zelenetz A, et al. ASCO 2006. Abstract 7560. 2. Smith M, et al. ASH 2007. Abstract 389. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Radioimmunotherapy in MCL Study Design Results/Comments I131Tositumomab + HDT cyclophosphamide + etoposide + ASCT FHCRC[1] 34 pts heavily pretreated Med number of previous Rx: 3 (106) 50% refractory to last Rx 5-yr PFS: 42% High-dose Ibritumomab Tiuxetan + ASCT in DLCL and MCL City of Hope[2] 42 pts, 1/3 MCL Med number of previous Rx: 2 (1-6) 1. Gopal AK, et al. Blood. 2002;99:3158-3162. 2. Krishnan A, et al. J Clin Oncol. 2008;26:90-95. Relapsed/Refractory MCL Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Relapsed/Refractory MCL Agent Cladribine Regimen Outcomes Single agent[1] 25 pts with recurrent disease ORR: 46%; CR: 21% Median PFS: 5.4 mos Single agent[2] Bendamustine + rituximab[3] 16 MCL patients ORR: 75%; CR: 50% Median PFS: 18 mos Bendamustine + rituximab[4] 12 MCL patients ORR: 92%; CR/CRu: 59% Median DOR: 19 mos Bendamustine 1. Inwards DJ, et al. Cancer. 2008;113:108-116. 2. Ogura M, et al. ASH 2009. Abstract 3694. 3. Rummel MJ, et al. J Clin Oncol. 2005;23:3383-3389. 4. Robinson KS, et al. J Clin Oncol. 2008;26:4473-4479. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Single-Agent Y-90 Ibritumomab Tiuxetan for Relapsed/Refractory MCL N = 34 Median age: 68 yrs; median previous regimens: 3 Dosed by platelet count – ≥ 150,000 cells/mm3: 0.4 mCi/kg – < 150,000 to ≥ 150,000 cells/mm3: 0.3 mCi/kg ORR: 31% Median EFS: 6 mos (28 mos for patients with response) Median OS: 21 mos Grade 3/4 thrombocytopenia: 24%; grade 3/4 neutropenia: 32% Wang M, et al. J Clin Oncol. 2009;27:5213-5238. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology 1.3 mg/m2 1.5 mg/m2 Bortezomib: Summary of Efficacy in Mantle Cell Lymphoma Study N CR, n (%) PR, n (%) ORR, % (n) O’Connor[1] 40 5 (13) 14 (35) 47 Goy[2] 29 6 (21) 6 (21) 41 Strauss[3] 24 1 (4) 6 (24) 29 Belch, n[4] 13 untreated/ 15 relapsed 0 1 6 6 46 47 PINNACLE[5] 141 11 (8) 36 (26) 47 (33) Total 262 24 (9) 74 (28) 98 (37) Similar ORR across studies and for untreated/relapsed 1. O’Connor OA, et al. Br J Haematol. 2009;145:34-39. 2. Goy A, et al. J Clin Oncol. 2005;23:667-675. 3. Strauss SJ, et al. J Clin Oncol. 2006;13:2105-2112. 4. Belch A, et al. Ann Oncol. 2007;18:116-121. 5. Fisher RI, et al. J Clin Oncol. 2006;24:4867-4874. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology PINNACLE Trial Update Response/Subsets Analysis Parameter Response: Evaluable (n = 141) Refractory MCL* (n = 51) Previous High-Intensity Therapy† (n = 52) ORR, % 32 29 25 CR/CRu, % 8 6 10 9.2 5.9 Not reached Median DOR, mos *Refractory subgroup: no response or response with TTP < 6 mos to last previous line of therapy. †High-intensity subgroup: ASCT or therapies containing high-dose cytarabine or ifosfamide/carboplatin etoposide. Among patients who achieved CR/CRu: median DOR not reached at 26.4 mos Goy A, et al. Ann Oncol. 2009;20:520-525. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Early Data of Combination Bortezomib With Common MCL Regimens Combination Design Results Comment R-CHOP GELA[1] 2 arms Wkly vs biwkly Dose escalation in each arm MCL, FL, MZL, DLCL IPI 0 48 pts 4 MCL ORR 100% biwkly Need longer follow-up Grade 3 neurotoxicity > 20% 9/10 in biwkly + highest dose R-CHOP Cornell[2] R-CHOP + bortz Days 1 and 4 only ++ DLCL and MCL 36 MCL Well tolerated Modified R-hyperCVAD[3] Modified R-hyperCVAD + bortz Days 1, 4 30 pts ORR: 90% CR: 77% Neuropathy excessive at 1.5 dose; capped VCR at 1.0 and bortz at 1.3 Modified R-hyperCVAD[4] Modified R-hyperCVAD + bortz 1.3 mg/m2 Days 1, 4 Classic R-hyperCVAD[5] Full R-hyperCVAD Bortezomib Days 1, 4 cycle A and Days 2, 5 cycle B 16 pts phase I No unexpected toxicity so far Including PFTs Bendamustine + Rituximab[6] 1. Mounier N, et al. ASCO 2007. Abstract 8010. 2. Ruan J, et al. ASH 2009. Abstract 2682. 3. Kahl B, et al. ASH 2008. Abstract 265. 4. Kahl BS, et al. ASH 2009. Abstract 1661. 5. Romaguera J. ICML 2008. Abstract 444. 6. Friedberg JW, et al. ASH 2009. Abstract 924. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Lenalidomide: IMiDs Lenalidomide mechanism of action remains poorly understood Antiangiogenic, microenvironment, direct antiproliferative, NK, and T-regs List AF. N Engl J Med. 2007;357:2183-2186. Copyright © 2007 Massachusetts Medical Society. All rights reserved. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Lenalidomide in MCL: Phase II NHL-003 Trial N = 203; MCL pts, n = 53 Median number of previous Rx: 3 (1-8) DOR: NR (13.7 mos in previous NHL-002 trial) Results % Response ORR 41 14 patients previous bortezomib 57 CR/CRu 13 PR 28 SD 26 PD 33 Toxicity (myelotoxicity)* Dose reductions 38 Zinzani PL, et al. ASH 2008. Abstract 262. Reeder CB, et al. ASH 2008. Abstract 1560. Czuczman MS, et al. ASH 2008. Abstract 268. Habermann TM, et al. Br J Haematol. 2009;145:344-349. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology CALGB 50501: Bortezomib + Lenalidomide in Rel/Ref MCL—Planned Interim Analysis Eligibility – Histologically documented MCL (CD5+, CD23-, cyclin D1+) – Measurable disease – PD 0-2 – Previous treatment with ≥ 1 regimen (including autologous SCT) – No previous radioimmunotherapy – No ≥ 3 grade 3 PN Morrison VA, et al. ASCO 2010. Abstract 8106. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology CALGB 50501: Bortezomib + Lenalidomide in Rel/Ref MCL—Planned Interim Analysis Induction therapy given every 21 days for 8 cycles – Lenalidomide 20 mg PO QD on Days 1-14 – Bortezomib 1.3 mg/m2 on Days 1, 4, 8, 11 Responding patients at 6 mos continued to maintenance therapy Primary endpoint: ORR Secondary endpoints: TTP, DFS/OS, correlating changes in activate NK/T cells and plasma cytokines with response Morrison VA, et al. ASCO 2010. Abstract 8106. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology CALGB 50501: Bortezomib + Lenalidomide in Rel/Ref MCL—Planned Interim Analysis Target accrual: 54 patients Planned interim analysis performed at 19 patients Grade 3/4 toxicity data for 31 patients – Anemia: 3/0 – Infection: 6/0 – Leukopenia: 3/0 – Motor neuropathy: 13/0 – Thrombocytopenia: 19/13 – Sensory neuropathy: 3/0 – Fatigue/asthenia: 19/0 – Hypotension: 13/0 – Dyspnea: 16/0 Morrison VA, et al. ASCO 2010. Abstract 8106. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Targeting the PI3K/mTOR Pathway Key pathway for multiple receptor tyrosine kinases/cell proliferation and protein translation Activated Ras PI3K PIP2 PIP3 PTEN ILK PDK1 Akt pAkt ppAkt pTSC2 + TSCI TSC1-TSC2 Rheb.GTP eIF4E.4EBP-1 complex Rheb.GTP Rapamycin + FKBP12 p70S6k Rapamycin + FKBP12 P 4E-BP1 + eIF4E Cyclin D1 mRNA P p70S6k Protein S6 P S6 Cyclin D1 protein Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Temsirolimus (CCI-779) in MCL Multicenter, open-label, phase III trial Relapsed/refractory MCL Temsirolimus 175 mg QW x 3 then 75 mg QW Required rituximab anthracycline alkylating agent Temsirolimus 175 mg QW x 3 then 25 mg QW (N = 162) Hess G, et al. J Clin Oncol. 2009;27:3822-3829. Investigators’ choice single agent Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Temsirolimus (CCI-779) in MCL Temsirolimus 175/75 (n = 54) Temsirolimus 175/25 (n = 54) Investigators’ Choice (n = 54) ORR, % 22* 6 2 Median DOR, mos 7.1 3.6 NA Median PFS, mos 4.8† 3.4 1.9 Median OS, mos 11.1 8.8 9.5 Response *P vs investigator choice = .0019; †P vs investigators’ choice = .0009 Hess G, et al. J Clin Oncol. 2009;27:3822-3829. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Targeting Cyclin/CDK complexes Flavopiridol Semisynthetic flavone analogue of rohitukine (Indian tree) that blocks several CDKs, including complex CDK4-cyclin D1 Initial schedules: ORR 11% (only PR)/strong binding to human proteins – LC50 required 5 x higher with human serum Pharmacologically modified schedules very promising – 30-min bolus followed by 4-hr infusion CLL – ORR 45%, med DOR > 12 mos, even in p53-deleted pts – 55% grade 3/4 lysis syndromes +++, thrombocytopenia Other CDK inhibitors coming: PD0332991 ++ Kouroukis CT, et al. J Clin Oncol. 2003;21:1740-1745. Lin TS, et al. Leuk Lymphoma. 2002;43:793-797. Byrd JC, et al. Blood. 2007;109:399-404. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Gemcitabine in MCL Single-agent gemcitabine (N = 18; 9 newly diagnosed, 9 relapsed)[1] – Response rate: 5/18 (28%) – CR: n = 1; PR: n = 4 – Median treatment response duration: 10.6 mos Gemcitabine/mitoxantrone/rituximab for relapsed/refractory (N = 16)[2] – Best responses – CR: 20%; PR: 27% – Grade 3/4 toxicities: neutropenia (100%), thrombocytopenia (67%), leukopenia (53%), anemia (33%) – Median PFS and OS not reached at 10.7 mos 1. Hitz F, et al. Hematol Oncol. 2009;27:154-159. 2. Garbo LE, et al. Invest New Drugs. 2009;27:476-481. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology MIPI and Survival in Patients Receiving RHCVAD and R-MTX-Ara-C Single-agent, retrospective cohort study Study designed to identify predictors of survival on patients on first-line RHCVAD therapy Primary endpoints: OS and PFS assessed by chart review Analysis included 53 patients with advanced MCL receiving RHCVAD alternating with R-MTX-Ara-C every 21 days (median: 6 cycles) Mato AR, et al. ASCO 2010. Abstract 8092. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology MIPI and Survival in Patients Receiving RHCVAD and R-MTX-AraC: Results Median OS and PFS not yet reached (median follow-up: 18 mos [range: 35-74]) MIPI classified 47%, 29%, and 24% of patients as low, intermediate, and high risk – MIPI did not identify 3 distinct categories by K-M analysis for OS or PFS Univariate analysis showed blastoid variant only significant predictor for OS (HR: 9.4; 95% CI: 1.2-53.1) Age, ECOG PS, WBC, LDH, β2-microglobulin not predictive of OS Blastoid variant (HR: 8.8; P .05) and β2-microglobulin (HR: 1.9; P .01) were independent predictors for PFS Mato AR, et al. ASCO 2010. Abstract 8092. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Risk-Adapted Transplantation in MCL Retrospective study of mature results of 17 yrs of transplantation experience in 121 MCL patients at M. D. Anderson Cancer Center – AUTO1 (n = 50): patients who received autologous SCT during first CR or PR – AUTO2 (n = 36): patients who received autologous SCT for relapsed/refractory disease – NST (n = 35): patients who received nonmyeloablative SCT for relapsed/refractory disease Tam CS, et al. Blood. 2009;113:4144-4152. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology 1.0 AUTO1 (n = 50) AUTO2 (n = 36) NST (n = 35) P = .01 P = .01 0.8 1.0 Proportion Alive Proportion Alive Without Progression MCL: ASCT/Allogeneic Transplantation 0.6 0.4 0.2 0 0.8 AUTO1 (n = 50) P = .02 AUTO2 (n = 36) P = .10* NST (n = 35) *P = .006 at 4 yrs landmark 0.6 0.4 0.2 0 0 12 24 36 48 60 72 84 96 108120 132 144 PFS (Mos) 0 12 24 36 48 60 72 84 96 108120 132 144 OS (Mos) Single institution/not very large numbers ASCT in first CR > ASCT in relapse (but no plateau either way) Mini-allo ~ 50% at 5 yrs: prediction is PBSCT and chimerism ≥ 95% Tam CS, et al. Blood. 2009;113:4144-4152. This research was originally published in Blood. © American Society of Hematology. Evolving Management Strategies in Non-Hodgkin’s Lymphoma clinicaloptions.com/oncology Other Novel Agents in MCL Drug Mechanisms/Study Other antiangiogenesis agents Thalidomide/rituximab/bevacizumab/VEGF Trap Anti-TRAIL antibodies (TRM-1) Fully human Mab agonistic to the TRAIL receptor 1 Induction apoptosis/extrinsic pathway HSP inhibitors 17AAG (geldamycin) Rationale to overcome bortezomib resistance IKK inhibitors Inhibitors of Raf/MEK signaling pathway HDAC inhibitors (SAHA, depsipeptide) Farnesyl transferase inhibitors BL22 immunotoxin Others Stabilization of NF-κB Sorafenib, orally administered Small-molecule signal transduction inhibitor SAHA showed activity in MCL in preclinical models Tipifarnib/ongoing Calicheamicin/CD22 (CMC-544) Bcl-2 inhibitors Go Online for More CCO Hematology/Oncology Activities! 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