Intermittent PrEP Opportunities and Challenges of Oral iPrEP Jean-Michel Molina Department of Infectious Diseases Saint-Louis Hospital, INSERM U941 University of Paris 7, France CHU Saint Louis Paris Conflicts of Interest Research Grants: Merck, Sanofi Advisory boards: Merck, Gilead, BMS, Janssen, ViiV Travel/conference fees: AbbVie, BMS Holding stock and personal relationship: none PI of the ANRS Ipergay iPrEP trial Current Status of Intermittent PrEP Oral iPrEP is not approved and it use should be strongly discouraged until data are available iPrEP different from “periodic” PrEP which is the starting and stopping of daily PrEP Current Status of Daily Oral PrEP Randomized trials: proof of concept that daily PrEP can reduce HIV incidence in high risk individuals FDA approval of TDF/FTC for oral PrEP but current uptake is low, and no approval in other countries Other trials using the same daily regimen have shown no efficacy: PrEP effectiveness in real life settings ? The Challenge of Sustained Adherence to Daily PrEP Only very high adherence to daily PrEP (>80%) associated with significant reduction of HIV incidence Patients who have taken PrEP intermittently were not protected Unsustainable daily PrEP adherence in adolescents and young women Provide better support for adherence or assess more friendly regimens for long-term use Time-Driven iPrEP Friday Saturday Sunday Monday Tuesday Wednesday Thursday Friday Saturday Sunday Event-Driven iPrEP Friday Saturday Sunday Monday Tuesday Wednesday Thursday Friday Saturday Sunday Time and Event-Driven iPrEP Friday Saturday Sunday Monday Tuesday Wednesday Thursday Friday Saturday Sunday What Do We Need to Know to Design iPrEP Regimens Timing of HIV-infection following sexual exposure PK of drugs in blood and tissues to achieve right drug concentration at the right place and at the right time Assess people’s preference Potential Benefits of iPrEP Higher adherence to a more convenient dosing regimen Higher adherence to iPrEP could improve efficacy: Intermittent use of TDF gel effective in Caprisa 004 when daily TDF gel ineffective in VOICE Better safety due to lower drug exposure (kidneys, bones) Lower risk of selecting drug resistance in case of HIV-infection More cost-effective TDF PK in Blood and Mucosal Tissue Single Dose 300 mg TDF 6 healthy women, blood collected every 4 hours for the first 24h and up to 15 days Long half-lives : 69 h TDF, 48h TVF-DP TVF-DP peak 12h : 20 fmol/106 PBMC Cumulative exposure of rectal tissue to TDF and TFV-DP > 30 and 120-fold higher respectively vs. vaginal tissue Louissaint et al. AIDS Res Human Retrovirus 2013,29 What Do Gays Men Think about iPrEP? Online survey among 939 seronegative Gay men in France: 63% prefer « on demand » vs 25% daily PreP More interested by PrEP if unprotected anal sex (OR: 2.37, p<0.001) Online survey in > 1000 seronegative Gay men in the US. Those most suitable for event-based PrEP were: older more educated more frequently used sexual networking more often reported sex with a not committed partner Capote et Pilule study, Adam P, Alexandre A. et al - Volk JE et al. J AIDS 2012, 61: 112 Safety and Adherence to iPrEP in Kenya (IAVI E001) Adherence : MEMS Sexual activity: daily SMS and interviews 4-Month follow-up Daily oral TDF/FTC* (1 pill per day) (n =24) Daily oral Placebo* MSM (n=67) and FSW (n=5) Aged 18-49 yrs in Kenya Current or previous STI or Unprotected vaginal/anal sex or Transactional sex (1 pill per day) (n =12) Intermittent oral TDF/FTC* (1 pill Monday Friday and 2h after sex) (n =24) Intermittent oral Placebo* (1 pill Monday, Friday and 2h after sex) *Double blind vs. Placebo but Open-label daily vs. intermittent (n =12) Mutua et al. PLoS ONE 2012 e33103 PrEP Adherence Rates for Daily and Intermittent Regimens Dosing Schedule Active Placebo N=48 N=24 Overall N=72 Daily Adherence Rate (%) (median, IQR) Overall unadjsuted 82 84 83 (63-92) Adjusted* 92 92 92 (82-99) Overall unadjsuted** 72 68 68 (63-78) Fixed doses 56 34 55 (28-78) Post-coital doses (SMS + MEMS event) 32 19 26 (14-50) 100 100 100 Intermittent Adherence Rate (%) (median, IQR) Post-coital doses within 2h (self report) *Adjusted accounts for extra openings and extra pills taken out ** adherent to fixed dosing + post-coital dosing (SMS + MEMS) Mutua et al. PLoS ONE 2012 e33103 Summary of IAVI E001 Adherence to coitally-dependent dosing may be difficult SMS responses were low (23%) and may have impaired assessment of post-coital dosing adherence in IAVI E002 trial in serodiscordant couples in Uganda SMS responses (80%) and adherence to iPrEP higher (91% twiceweekly, 45% post-coital) Acceptability of PrEP was high and better with intermittent dosing (86%) despite challenges with the post-coital dosing Safety was similar among all groups Better methods to measure sexual activity and adherence to intermittent PrEP regimens What is the Evidence iPrEP Can Work ? Efficacy of iPrEP with TDF/FTC in the SHIV Macaque Model Garcia-Lerma , Science Trans Med 2010, 14,14ra4 TFV-DP Concentrations in IPrEx and STRAND Regression analysis in iPrEx: 90% reduction in HIV acquisition when TFV-DP>16 fmol/106 cells 16 Predicted risk reduction: 76% with 2 pills / week 96% with 4 pills / week 99% with 7 pills/ week * * Visit when HIV was first discovered Anderson et al, Science Translational Medicine 2012 4:151ra125 Ongoing Oral iPrEP Studies HPTN 067/ADAPT (Alternative dosing to augment PrEP pill taking) Phase II, Randomized, Open-Label, Pharmacokinetic and Behavioral Study of the Use of Intermittent Oral PrEP with TDF/FTC 6-week lead-in period 1 pill/week DOT before randomization High risk women and MSM (New York, Bangkok, Cape Town) Wk 24 primary endpoint Daily Truvada 1 tablet/d Regarless of sexual activity (n = 180) Time driven Truvada: 1 tablet 2 days/week + 1 post-exposure dose within 2 hours after sex (n = 180) Event driven Truvada: 1 tablet prior to sex + 1 post-exposure dose within 2 hours after sex (n = 180) Primary Objective: Is intermittent vs. daily dosing associated with equivalent coverage of sex events, lower number of pills used and decreased side effects R. Grant, F. Van Griensven, et al. IPERGAY Study Design Effectiveness of “on demand” PrEP Randomized placebo-controlled trial • High risk MSM • Condomless anal sex with > 2 partners Full prevention services* TDF/FTC before and after sex (n=950) Full prevention services* placebo before and after sex (n=950) Counseling, testing for STI, condoms, vaccination, PEP Primary endpoint : HIV infection, 64 events expected Incidence of HIV-infection: 3%PY, 50% efficacy, ~ 2000 pts www.ipergay.fr Conclusions Oral iPrEP is a potentially interesting and promising strategy Oral iPrEP should not be used outside research settings Individuals reluctant to use daily PrEP should consider other preventive tools More research is needed on iPrEP (PK and behavioral sciences)