SPPS-208 Syllabus Winter 2015 SPPS 208 Clinical Research Design and Applications Course Syllabus Winter 2015 Course Chair and Faculty: Grace M. Kuo, PharmD, MPH, PhD, FCCP Administrative Assistant: Victoria Banks SPPS-208 WINTER 2015 SYLLABUS COPYRIGHT ©2015 – UCSD SKAGGS SCHOOL OF PHARMACY AND PHARMACEUTICAL SCIENCES ALL RIGHTS RESERVED 1 SPPS-208 Syllabus Winter 2015 Goals: The Clinical Research Design and Applications course is intended to provide the pharmacy student with basic skills needed to 1. Formulate a research question and design a clinical pharmacy/medication study 2. Critically appraise studies presented in the medical, pharmacy and healthcare literature The focus will be on examining and designing different types of study that influence medication use and decision making in pharmacy practice settings. Types of study design range from randomized, controlled clinical trials to observational and evaluation studies. Not all possible study designs will be covered in class; however, highlights of common designs relevant to translational research in pharmacy practice will be reviewed in class. Objectives– At the end of the course students should be able to: 1. List the study design elements that provide evidence for therapeutic decision-making 2. Design a clinical study related to medication(s) or pharmacy practice, including study elements discussed in class 3. Compare and contrast major types of study designs used in clinical studies 4. Understand ethical issues associated with conducting clinical studies 5. Complete human subjects research training 6. Critically assess medical, pharmacy and healthcare literature to make clinical or practice decisions across clinical practice settings Contact Information: Course Chair: Grace M. Kuo, PharmD, MPH, PhD, FCCP Telephone: 858-822-7751; E-mail: gmkuo@ucsd.edu Administrative Assistant: Victoria Banks Telephone: 858-822-7807; E-mail: vbanks@ucsd.edu Office Hours and Location: Dr. Kuo’s office hours may be arranged by appointment. Please email Dr. Kuo to set up meeting times Office Location: Pharmaceutical Sciences Building Room 2272 Lecture Times and Location: Time: 1:00 PM – 2:50 PM on Tuesdays Location: Health Sciences Education Center Auditorium (basement level of the Pharmaceutical Sciences building at the Skaggs School of Pharmacy and Pharmaceutical Sciences) Course Format: The Clinical Research Design and Applications course consists of lecture/seminar sessions, reading assignments, human subjects research training, a mid-term exam, and a final exam. Reading Assignments (Materials Included in the Exam): You can check-out the course textbooks from the Biomedical Library Reservation desk. Journal articles are accessible via the Biomedical Library’s online Course Reserves. Required Text (2 Copies are on reserve at the Biomedical Library): • Designing Clinical Research. by Hulley SB, et al. Philadelphia, PA: Lippincott Williams & Wilkins, 2013. 4th edition. Optional Text (A copy is on reserve at the Biomedical Library: 2 SPPS-208 Syllabus • Winter 2015 Health Services research Methods by Leiyu Shi, DrPH, MBA, MPA. Clifton Park, NY: Delmar Learning, 2008. 2nd Edition. To Access Journal Articles via Biomedical Library Course Reserves: • Go to the Course Reserves section of the Biomedical Library. o http://libraries.ucsd.edu/resources/course-reserves/index.html • Click on STUDENTS • Select department: School of Pharmacy and Pharmaceutical Sciences • Select Course: SPPS208 • ‘Accept' terms and you should be able to view/print all the journal articles Course Website: The official web site for this course can be accessed at ted.ucsd.edu. You are strongly encouraged to visit this site to access handouts, exam score, and grades. Use of Audience Response Clickers: Students should bring your own TurningPoint clickers to class. Audience response participation may be used by lecturers in class. Performance Requirements/Evaluation Criteria: 1. Midterm Exam (40% of Course Grade) – includes Multiple choices, matching, or short answers. Exam questions cover materials discussed in class and included in reading assignments. 2. Human Subjects Research Training CITI Certificate (10% of Course Grade) a. Go to www.citiprogram.org and click on the "Register" button located in the blue log in box to the right of the homepage. b. Enter “University of California, San Diego” in the Organization Affiliation search. Select “Continue to Step 2”. c. Complete Steps 2-4 of the registration. d. At Step 5, select “No” when asked about CE credits. e. At Step 6, select “Basic Human Subjects – Biomedical”. f. At Step 7, Question 1, select “Biomedical Research Investigators”. Skip the other questions. g. Click “Finalize Registration”. h. You can now begin the course. The course does not have to be completed in one sitting. After you complete each module the date completed and score column will be filled in the Gradebook. i. Once you have completed the course, save the file name as CITI_LastName + initial of your first name (e.g., CITI_Kuog). j. Print a PDF copy (selecting File, Print, and print to PDF) of your Course Completion Report gradebook page (showing your scores for each module, with your name on top of page)) and upload to TED before the due date/time. Late submission will receive a 10 point deduction every day passed the due date/time. k. Your grade for the CITI certificate will be based on the average score you have received from all required modules. 3. Journal Article Reviews, Critiques, & Applications Write-Up (10% of Course Grade) – Turn in your write up at the beginning of class on February 17; your write-up should be 3 SPPS-208 Syllabus Winter 2015 based on the Journal Critique Questions provided in the syllabus. No points will be given to late submissions. 4. Final Exam (40% of Course Grade) – include Multiple choices, matching, short answers, and study-based designs and critiques. Exam questions cover cumulative materials discussed in class and included in reading materials. Grading: The final grade will be based on the percentage of points earned. Grade H P Y F Designation Honors Pass Provisionally unsatisfactory Fail % Range > 90 > 75 74 - 65 < 65 Policies: Examinations There will be two scheduled exams. Scantrons, calculators (when needed), and #2 pencils will be provided. Electronic devices (cell phones, ipads, etc.) are to be turned off and put away in backpacks or purses prior to the start of the exam. Backpacks and purses have to be put away before the exam is distributed. Food is not allowed during the exam. No bathroom breaks are allowed during the exams. Students may leave the exam at any time for any reason, but there will be no re-entry into the exam room. If you have a medical condition that requires you to leave and re-enter the room during the exam, please provide the course chair with the appropriate documentation, such as a letter from your doctor. Exam Review Students will be able to review their exams after the scores have been posted. Students who would like to review their exams can make an appointment with the administrative assistant and the course chair. Re-examination Policy According to SSPPS Policy, students will be allowed to reschedule exams only with the permission of the course chair and for the following reasons: • documented illness • approved personal or family emergency • approved professional commitment A score of 0 will be recorded for any examination that is missed due to an unexcused absence. If a student is unable to take an exam because of illness, s/he must notify the course chair, before the exam and receive permission to reschedule. If the illness is the result of a medical emergency, the student must notify the course chair as soon as medically possible. In each of these cases, the student is required to provide documentation of illness. If a student is unable to take an exam because of a personal or family emergency, s/he must notify the course chair before the exam and receive permission to reschedule the exam. 4 SPPS-208 Syllabus Winter 2015 If a student wishes to reschedule an exam in order to meet a professional commitment, s/he must contact the course chair at least three weeks in advance of the regularly scheduled exam and receive permission to reschedule. Documentation of attendance at the professional commitment may be requested by the course chair. In each of the above situations, in addition to notifying the course chair, the student must notify the Office of Student Affairs and inform the office of the arrangements that have been made with the course chair. The date and time of the rescheduled examination shall be at the discretion of the course chair after discussion with the student. Requests to reschedule exams in order to accommodate personal vacations or activities, or to allow a student to attend non-essential activities will not be approved. Posting of Grades Following the grading of each exam, grades will be posted on the course website. You will have access only to your grades and are asked to refer to the course website as grades will not be publically posted. Students who have earned a grade of Y this course will be offered the opportunity to take a repeat examination to demonstrate competency, prior to the start of the next academic year. The rectifying of the Y grade will occur during the summer, where at least 6 weeks will have passed between the end of Spring quarter courses and the rectifying of the Y grade. A student who has failed a course, or failed a repeat examination, and has been assigned a grade of F must repeat the course. Integrity of Scholarship Integrity of scholarship is essential for an academic community. The University expects both faculty and students to honor this principle and in so doing protect the validity of University intellectual work. For students, this means that all academic work will be done by the individual to whom it is assigned, without unauthorized aid of any kind. Instructors, for their part, will exercise care in planning and supervising academic work, so that honest effort will be upheld. Students with Disabilities Appropriate academic accommodations for qualified students with disabilities will be provided upon request. Please contact Kim Ciero, Director of Student Affairs (kciero@ucsd.edu) and Shelly Fromholtz, Curriculum Coordinator (sfromholtz@ucsd.edu) to arrange for special accommodations prior to each exam. Failure to prearrange accommodations will require that you take the exam with the rest of the class at the regularly scheduled time. Course and Faculty Evaluations: Course and faculty evaluations provide important feedback to instructors to improve course content and teaching methods. Completion of course and instructor evaluations is a requirement for successful completion of this course. Students who have academically passed this course but not completed evaluations will receive a grade of “I” (Incomplete) for the course. 5 SPPS-208 Syllabus Winter 2015 COURSE SCHEDULE Tuesdays 1:00 PM to 2:50 PM in the Health Sciences Education Center Auditorium EXCEPTION: Wednesday March 11, 2015; 1:00 PM to 3:00 PM (Final Exam) DATE Week 1 Jan. 6 LECTURE TOPIC LECTURER DUE Course introduction and Syllabus Review Dr. Grace Kuo Question, Hypothesis, Rationale, Specific Aim Week 2 Jan. 13 Randomized Controlled Study Dr. Grace Kuo Week 3 Jan. 20 Crossover Study Dr. William Norcross Cross-sectional Study Dr. Grace Kuo Cohort Study Dr. Tina Chambers Case Control Study Dr. Grace Kuo Survey Research & Practice-Based Research Dr. Grace Kuo Week 4 Jan. 27 Week 5 Feb. 3 CITI Certificate Due by 1 PM Program Evaluation Study Mid-Term Exam Dr. Grace Kuo & Proctor Quality Improvement – Lean Performance Study Mr. Anthony Biondo, MBA Week 7 Feb. 17 Journal Article Reviews, Critiques, & Applications UC San Diego pharmacy residents Week 8 Feb. 24 Interpretation of study findings from statistical tests Dr. Jonathan Watanabe Week 6 Feb. 10 Research Using Existing Data Week 9 March 3 Week 10 March 11 Drug Utilization Review & Medication Use Evaluation Dr. Katie Derry Designing Your Study; proposals; IRB reviews Dr. Grace Kuo Final Exam Dr. Grace Kuo & Proctor 6 Jounral Critique Write-Up Due by 1pm SPPS-208 Syllabus Winter 2015 Lecturers and Staff (in alphabetical order of last names): 1 Victoria Banks Administrative Assistant vbanks@ucsd.edu 2 Anthony Biondo, MBA Sr. Administrative Analyst Department of Pharmacy UC San Diego Health System abiondo@ucsd.edu 3 Christina Chambers, PhD, MPH Professor of Pediatrics Director, California Teratogen Information Service and Clinical Research Program chchambers@ucsd.edu 4 Katie Derry, Pharm.D., BCPS Pharmacoeconomic Specialist Department of Pharmacy UC San Diego Health System klderry@ucsd.edu 5 Grace M. Kuo, PharmD, MPH, PhD, FCCP Professor of Clinical Pharmacy Adjunct Professor of Family Medicine and Public Health Associate Dean for Academic Clinical Affairs, SSPPS gmkuo@ucsd.edu 6 William Norcross, MD Professor of Clinical Family Medicine Director, UCSD Physician Assessment and Clinical Education (PACE) Program wnorcross@ucsd.edu 7 Jonathan Watanabe, PharmD, PhD Assistant Professor of Clinical Pharmacy Skaggs School of Pharmacy & Pharmaceutical Sciences jhwatanabe@ucsd.edu UC San Diego Residents: UC San Diego Pharmacy Residents William Cang, PharmD Carissa Chan, PharmD Nina Haste, PharmD Jade Kozuch, PharmD Wan-Ting Huang, PharmD Trina Huynh, PharmD Kathryn Medders, PharmD Jeffrey Yin, PharmD wcang@ucsd.edu cac001@ucsd.edu nhaste@ucsd.edu jkozuch@ucsd.edu wah007@ucsd.edu trhuynh@ucsd.edu kmedders@ucsd.edu jfyin@ucsd.edu 8 7 SPPS-208 Syllabus DATE Week 1 Jan. 6 Week 2 Jan. 13 Winter 2015 LECTURE TOPIC READING ASSIGNMENTS Course introduction Syllabus; CITI online certificate reading Question, Hypothesis, Rationale, Aim Hulley (Chapters 1 & 2; 5; 19) Randomized Controlled Study Hulley (Chapter 10) Young JM, Solomon MJ. How to critically appraise an article. Nature Clinical Practice Gastroenterology & Hepatology 2009;6:82-91. Kendall JM. Designing a research project: randomized controlled trials and their principles. Emrg Med J 2003;20:164-8. Week 3 Jan. 20 Week 4 Jan. 27 Crossover Study Ganiats, et al. Does Beano prevent gas?: a double-blind crossover study of oral alpha-galactosidase to treat dietary oligosaccharide intolerance. J of Fam Practice 1994;39:5:1-4. Cross-sectional Study Hulley (Chapter 7) Cohort Study Hulley (Chapter 7) Chambers CD, Johnson KA, Dick LM, et al. Birth outcomes in pregnant women taking fluoxetine. N Engl J Med. 1996;335(14):1010-5. Week 5 Feb. 3 Week 6 Feb. 10 Case Control Study Hulley (Chapter 8) Survey Research Chambers CD, Hernandez-Diaz S, Van Marter LJ, et al. Selective serotonin-reuptake inhibitors and risk of persistent pulmonary hypertension of the newborn. N Engl J Med. 2006;354(6):579-87. Hulley (Chapter 15); Shi (Chapter 8) Practice-Based Research Carter BL, Clarke W, Ardery G, et al. A cluster-randomized effectiveness trial of a physician-pharmacist collaborative model to improve blood pressure control. Circ Cardiovasc Qual Outcomes 2010;3(4):418-23. Program Evaluation Shi (Chapter 9) Program evaluation in health care. Health Services Research Group. CMAJ 1992;146(8):1301-4. Quality Improvement IHI White Paper – Going Lean in Health Care 8 SPPS-208 Syllabus DATE Week 7 Feb. 17 Winter 2015 LECTURE TOPIC Journal Critiques READING ASSIGNMENTS Ridker PM, Cook NR, Lee IM, Gordon D, Gaziano JM, Manson JE, Hennekens CH, Buring JE. A randomized trial of low-dose aspirin in the primary prevention of cardiovascular disease in women. N Engl J Med 2005 Mar 31;352(13):1293-304. Greenhalgh T. How to Read a Paper: Assessing the methodological quality of published papers. BMJ 1997;315:305-8. Greenhalgh T. How to Read a Paper: Getting your bearings (deciding what the paper is about). BMJ 1997;315:243-6. Week 8 Feb. 24 Week 9 March 3 Interpretation of study findings Hulley (Chapter 13) Research Using Existing Data DUR/MUE TBD Designing Your Study Hulley (Chapter 19, 16, 14) 9 SPPS-208 Syllabus Winter 2015 Journal Critique Questions for Clinical Studies (20 points = 10% of total grade) Introduction (4 points): 1. Study question(s) and aim(s) of the Study: Was there a clear statement of question and aim? If yes, please state the specific aim(s). If no, how should the aim be stated? 2. What was the chosen study design? 3. Were the hypothesis clearly stated? Please state the hypothesis. 4. Did the authors provide sufficient background information to demonstrate that the study filled a knowledge gap? Methods (6 points): 1. Who was the study about? a. How were subjects recruited? b. Explain the inclusion and exclusion criteria. c. Was the sample size large enough to get a significant result? Explain. 2. What was the main exposure/intervention under investigation? How was it ascertained, defined, and measured in this study? 3. What outcome(s) were measured, and how? 4. What possible confounding factors or sources of bias might be present? 5. Was the study adequately controlled? a. Was the study randomized? b. Were demographics for the comparison groups similar post randomization? 6. Were data collected appropriately? Results/Statistical Aspects (5 points): 1. Had the authors determined whether their groups were comparable and, if necessary adjusted for baseline differences? 2. Did the authors use appropriate statistical tests? Explain. 3. Data presentation and analysis: a. How clear and complete? i. Descriptive Statistics ii. Complete presentation of numbers iii. Measures of association and risk 4. Statistical significance i. Were “p-values calculated and interpreted appropriately? ii. Had confidence intervals been calculated and did the authors’ conclusions reflect them? 5. Was study power calculated? Could a Type I or Type II error have occurred? Was there control for confounders and bias? Discussions/Conclusions (5 points): 1. Did the authors compare their study results to those of a systemic review of all previously published data? 2. Were the study conclusions consistent with the results? 3. Can you apply the findings to your patients? If so, how? Which patients or subset of patients would the study be applicable to? 4. Would you recommend this article to a colleague as one that provides quality evidence to seriously consider when making a therapy decision? Why or Why not? 5. How would you do the same study better? Look at all aspects of the study. 10 SPPS-208 Syllabus Winter 2015 Study Design Elements for Proposal Writing (Reference) 1. Study Question, Specific Aim, Hypothesis, & Rationale a. State the study question b. List primary specific aim (or objective) c. List hypothesis to the study objective d. Describe rationale for your study and knowledge gap identified 2. Research Design Selection & Methods a. Name your study design b. State the observation or intervention methods c. List comparison groups d. Name who subjects or participants are e. List inclusion and exclusion criteria f. Subject selection g. Recruitment strategy 3. Outcome, Sample Size, & Statistical methods a. Name the primary outcome endpoint and describe why this was chosen b. List and describe the data collection instrument (e.g., survey, BP device) to be used for the primary outcome endpoint c. State sample size number and describe how it’s derived d. Name the statistical method proposed for the primary outcome endpoint and explain the rationale for selection 4. Justification for the Selected Study Design a. Reasons (i.e., advantages and disadvantages) why the selected study design is the best b. Reasons (i.e., advantages and disadvantages) why the other study designs are not the best 11