Pediatric TB and HIV The Potential of New TB Vaccines Dr. Hoosen Coovadia Nelson Mandela School of Medicine, University of KwaZulu Natal Board of Directors, Aeras Global TB Vaccine Foundation Presentation to the CORE Group May 17, 2010 AERAS GLOBAL TB VACCINE FOUNDATION Estimated TB Incidence Rate, 2007 Estimated new TB cases (all forms) per 100 000 population No estimate 0-24 25-49 50-99 100-299 >= 300 The boundaries and names shown and the designations used on this map do not imply the expression of any opinion whatsoever on the part of the World Health Organization concerning the legal status of any country, territory, city or area or of its authorities, or concerning the delimitation of its frontiers or boundaries. Dotted lines on maps represent approximate border lines for which there may not yet be full agreement. WHO 2009. All rights reserved AERAS GLOBAL TB VACCINE FOUNDATION HIV Prevalence Among TB Cases, 2007 Global estimate: about 1.4 million TB/HIV cases and 450,000 TB/HIV deaths a year HIV prevalence in TB cases, (%) No estimate 0–4 5–19 20–49 >= 50 The boundaries and names shown and the designations used on this map do not imply the expression of any opinion whatsoever on the part of the World Health Organization concerning the legal status of any country, territory, city or area or of its authorities, or concerning the delimitation of its frontiers or boundaries. Dotted lines on maps represent approximate border lines for which there may not yet be full agreement. WHO 2009. All rights reserved AERAS GLOBAL TB VACCINE FOUNDATION HIV/AIDS and TB: A Deadly Combination + • • • • One in four HIV deaths is linked to TB HIV suppresses the human immune system TB suppresses the human immune system Each makes the other worse synergistically The number of new cases of TB has more than doubled in countries with high HIV prevalence in the past 15 years AERAS GLOBAL TB VACCINE FOUNDATION Drug Resistance • WHO estimates 490,000 MDR-TB cases emerge every year, with more than 110,000 deaths • Extensively drug-resistant (XDR) TB has been identified in 57 countries as of November 2009 • In 2008, WHO reported that the highest rates of MDR TB ever recorded, with peaks of up to 22% of new TB cases, were in some settings of the former Soviet Union. In the same region, 1 in 10 cases of MDR-TB is XDR-TB • Treatment for drug-resistant TB is much longer, more complex and more expensive - with much lower success rates AERAS GLOBAL TB VACCINE FOUNDATION Global Health issues for children WHO, “World Health Statistics, 2010” AERAS GLOBAL TB VACCINE FOUNDATION Human Rights Issue • No vaccine to provide long-term protection from pulmonary TB • No HIV vaccine • No benefit from biomedical advances for people and communities affected by TB • TB exposure due to inadequate health systems – poor delivery of INH prophylaxis • TB and HIV diagnostics inadequate for testing children • Poor pediatric tracking programs to measure incidence • Social circumstances lead to exposure – poverty, malnutrition AERAS GLOBAL TB VACCINE FOUNDATION Pediatric HIV • 2.1 million children were living with HIV/AIDS, vast majority in sub-Saharan Africa. • 1000 children get newly infected with HIV each day. • Children acquire HIV from their HIV-infected mothers during pregnancy, birth or breastfeeding. • PMTCT works, but needs broader rollout and accessibility to those who need it most. AERAS GLOBAL TB VACCINE FOUNDATION Maternal TB/HIV important risk factor for pediatric TB and mortality • Estimated TB rate: -10 times higher in HIV-exposed uninfected children <5 years than in non-HIV exposed -30 times higer in HIV-infected children<5 years than non-HIV exposed (Mukade 1997) -1596/100,000 pop. HIV+ infants ≤ 12 mo. vs 65.9/100,000 pop. In HIVinfants ≤ 12 mo. (Hesseling CID 2009) • Maternal TB/HIV important risk factor for pediatric TB and mortality (Pillay 2004; Khan 1999; Cotton 2008; Gupta 2007) Adapted from presentation by Amita Gupta, July 19, 209 AERAS GLOBAL TB VACCINE FOUNDATION WHO Estimated TB Cases by Age, 2006 Country Total Cases Cases in Children < 15 % in Children Myanmar Nigeria Pakistan The Phillipines 78,489 261,404 244,736 230,217 8,007 32,310 61,905 12,167 10.2 12.4 25.3 5.3 Russian Fed. South Africa Thailand Uganda Tanzania Viet Nam Zimbabwe Total 183,373 220,486 85,928 75,250 117,489 143,023 76,296 6,678,188 7,778 35,449 2,317 12,099 18,890 7,559 12,267 630,722 4.2 16.1 2.7 16.1 16.1 5.3 16.1 9.4 Adapted from “Childhood TB” by AHesseling, PMusoke, AGupta, JSadoff AERAS GLOBAL TB VACCINE FOUNDATION Existing TB Vaccine Ineffective • BCG provides unreliable protection against pulmonary TB, which accounts for most TB disease worldwide • BCG is not know to protect against latent TB • BCG is not recommended for use in infants infected with HIV due to increased risk for severe BCG-related complications • Despite wide use, particularly in high burden countries, BCG has had no apparent impact on the growing global TB epidemic • BCG does reduce risk of severe pediatric TB disease, so it should continue to be used until a better TB vaccine is available BCG introduced in 1921 AERAS GLOBAL TB VACCINE FOUNDATION Tuberculosis: TB Vaccine Too Dangerous for Babies With AIDS Virus, Study Says July 2, 2009 – The vaccine against tuberculosis that is routinely given to 75 percent of the world’s infants is too risky to give to those born infected with the AIDS virus, says a new study published by the World Health Organization. It recommended that vaccination be delayed until babies can be tested. AERAS GLOBAL TB VACCINE FOUNDATION Goals for Better TB Vaccines • Eliminate TB as a public health threat, in line with global targets (<1 case/million), in conjunction with new drugs and diagnostics • Safe and effective in preventing TB in children, adolescents and adults, including people with HIV (for whom BCG is unsafe) • Protect against all forms of TB – including MDR and XDR AERAS GLOBAL TB VACCINE FOUNDATION Global TB Vaccine Pipeline Vaccine Candidate Pre-Clinical Phase I Phase II Phase IIb Phase III AERAS402/Crucell Ad35 Crucell N.V./Aeras MVA85A/AERAS-485 OETC/Aeras GSK M72 GSK Biologicals/Aeras Hybrid 1 SSI IC-31 SSI, TBVI, Intercell HyVac4/AERAS-404 sanofi pasteur/SSI/Intercell/Aeras VPM 1002 Max Planck/Vakzine Projekt Management GmbH/TBVI AdAg85A McMaster University RUTI Archivel Farma, S.I. Hybrid 1 SSI CAF01 SSI AERAS-rBCG Aeras AERAS-Capsid Aeras Other rBCG rMtb Albert Einstein S. of Med., Institute Pasteur, Univ. of Zaragoza, TBVI AERAS-other virus Aeras Protein/Polysaccharides Inst. Pasteur de Lille/Inserm, Albert Einstein S. of Med., Aeras, Karolinska Instit. Additional research at the discovery/early pre-clinical level: Bhagawan Mahavir Medical Research Center; Cardiff University; EpiVax, Inc.; ImmunoBiology Ltd.; Infectious Disease Research Institute; Institute de Pharamacologie, Puso; Karolinska Institute; Malaysia-Finlay Institute, NIAID; NIH; Osaka University; Shanghai H&G Biotech; Sequella; UCLA; and, Vanderbilt University. As of November 2009 AERAS GLOBAL TB VACCINE FOUNDATION Aeras Global TB Vaccine Foundation Mission To develop new, more effective TB vaccines and ensure their availability to all who need them Goal • A more effective, safe and affordable TB vaccine by 2016 Method • Collaborate with academic, biotech, pharmaceutical and NGO partners to develop and test new TB vaccines • Pursing a Prime-Boost strategy by developing a modern replacement for BCG plus booster vaccines • Develops vaccines in its own lab and manufacturing plant AERAS GLOBAL TB VACCINE FOUNDATION Induction of Immunity: Prime –Boost Infants BCG or rBCG IM or as an aerosol Capsids in bacteria or as an aerosol 24 Weeks 14 Weeks AERAS GLOBAL TB VACCINE FOUNDATION Recombinant BCG (rBCG) - A Better BCG • Safer in HIV infected infants or others with immune-suppression • BCG or rBCG boosted with another TB vaccine is much better than either vaccine alone • Constructed to address each stage of the TB life cycle • Prevent infection and reactivation • A new vaccine candidate with all of these properties is expected to enter clinical trials in 2010 AERAS GLOBAL TB VACCINE FOUNDATION Summary of Aeras Candidates in Clinical Testing SSI HyVac4 / AERAS-404 Status: Phase I •Recombinant protein vaccine intended to be a booster vaccine •Phase I clinical trials •Current trials in Finland, Sweden, South Africa GSK M72 Status: Phase II •Recombinant protein vaccine intended to be a booster vaccine •Phase I and II trials conducted in Europe, Africa and Asia, including a Phase I trial in HIV+ in Europe •Current trials in South Africa, the Gambia AERAS-402 / Crucell Ad35 Status: Phase IIb •Viral vectored vaccine utilizing adenovirus 35; intended to be a booster vaccine •Phase I and II trials conducted in North America and Africa; Phase IIb recently initiated in HIV+ in South Africa •Current trials in South Africa MVA85A / AERAS-485 Status: Phase IIb •Viral vectored vaccine utilizing modified vaccinia Ankara; intended to be a booster vaccine •The most clinically-advanced booster vaccine for tuberculosis with an ongoing proof-of-concept Phase IIb trial in infants •Previous clinical trials in the UK and Africa, including in HIV+ •Awarded orphan drug status by EMEA •Current trial in South Africa AERAS GLOBAL TB VACCINE FOUNDATION Aeras Partnerships for Field Research St. John’s Research Institute Palamaner, India Makerere University Kampala, Uganda SATVI/U of Cape Town Worcester, South Africa KEMRI/CDC Kisumu, Kenya Cambodian Health Committee Svay Rieng, Cambodia Manhica Health Research Centre Manhica, Mozambique AERAS GLOBAL TB VACCINE FOUNDATION Example of Site Development South Africa • Partnership with South African Tuberculosis Vaccine Initiative (SATVI) • Field site developed in Worcester (~120 km from Cape Town) • Infrastructure developed: – State-of-the-art immunology laboratory – Highly skilled staff capable of performing the duties necessary to maintain the infrastructure and execute clinical research – Clinical and office facilities – Professional Development Program (Siyantinga- “Reach for the Stars”) – program initiated in 2001 – Resource Center established in 2005 AERAS GLOBAL TB VACCINE FOUNDATION Clinical Trials Field Site Development • Large-scale community-based clinical trials are conducted in high burden countries • Aeras partners with local research institutions to establish field sites and conduct clinical research • Build local infrastructure and health care/research capacity to perform future Good Clinical Practice (GCP) compliant Phase III clinical trials AERAS GLOBAL TB VACCINE FOUNDATION Activities in South Africa Research Partner - South African Tuberculosis Vaccine Initiative (SATVI) • Conducting Phase I, II and IIb studies of four vaccine candidates • Adult and infant enrollment • Over 230 staff trained since 2004 • Most advanced site for large-scale TB vaccine trials in the world • Future infant studies planned of AERAS402/Crucell Ad35 • Western Cape AERAS GLOBAL TB VACCINE FOUNDATION Activities in South Africa Research Partner – University of Cape Town Lung Institute • Phase II clinical trial in adults with active or previous TB (AERAS402/Crucell Ad35 ) • Cape Town • Future study of TB vaccine candidate in HIV infected adults planned (part of multi-center MVA85A/AERAS-485 study) AERAS GLOBAL TB VACCINE FOUNDATION Activities in South Africa Research Partner – Aurum Institute • Enrolling adults with HIV in Phase IIb trial • Safety and efficacy of TB vaccine (MVA85A/AERAS-485) • Klerksdorp, North West (mining area) AERAS GLOBAL TB VACCINE FOUNDATION Access and Availability • Future access considered at every stage of vaccine development • Manufacturing – Guarantee by partners for sufficient production and affordable prices, or technology transfer – Manufactured by Aeras with partners in developing world – Aeras will not consider vaccine candidates that will be costly to manufacture on a large scale • Pricing – Dual pricing for affordable distribution in resource-poor countries – Cost plus purchase from partner – Aeras provides at cost • Distribution – Developing world governments – International organizations (GAVI, UNICEF) – Developing world partners AERAS GLOBAL TB VACCINE FOUNDATION TB Vaccine Development Timeline Costs associated with the development of a portfolio of TB vaccine candidates Field Site Preparation ($2-4 million per yr, per site) Manufacturing ($310 million to build and upgrade facilities; $10 million per year to maintain) Phase IIb Vaccin e Disco very PreClinic al Testin 1 - 2 Years g $3.5 million Phase I Phase III Licensure Phase II 1 Year 2.5 Years 3 Years 4 Years $3 million $18 million $48 million up to $265 million Costs related to the development of one TB vaccine candidate •Direct costs to develop one TB vaccine candidate could be as much as $340 million •Phase III licensure trials are complex and the most costly component –Infant trial - between $70 and $140 million –Adolescent and adult trial - between $130 and $265 million •Aeras has a broad pipeline of vaccine candidates, 4 of which are currently in clinical trials •With sufficient resources, a new TB vaccine could be ready in 7 – 10 years. AERAS GLOBAL TB VACCINE FOUNDATION Aeras gratefully acknowledges the support of the following major donors THE MARY LYNN RICHARDSON FUND Netherlands Ministry of Foreign Affairs