The application of genome-wide association studies

advertisement

The application of genome-wide association studies of aging in a patient-driven clinical trial outline

Melanie Swan, Aaron Vollrath, Cindy Chen & Raymond McCauley, DIYgenomics, Palo Alto, CA USA melanie@DIYgenomics.org +1.415.505.4426 www.DIYgenomics.org/aging_poster.ppt

Background

The rapidly decreasing cost of whole genome sequencing could soon make the Personal Genome a reality for large numbers of individuals wanting access to and interpretation of their genomic information. Already the accessibility of this information is providing an impetus for patient-driven research. Though the advent of the truly personal genome, whereby everyone has access to their entire genomic data at an affordable price is not yet here, a number of options exist for individuals to obtain genotyping data from consumer genomic services. Costs range from $400-$2,000 for genotyping services to $20,000 for whole human genome sequencing for consumers. As proof of principle of a patient-driven clinical trial using personal genomic data in the form of identified variants, this study utilizes published data from genome-wide association studies (GWAS) to link genes and variants to a variety of biomarkers associated with human aging.

The study outline takes into consideration GWAS results for critical aspects of aging including the inability to adequately regulate glucose levels, the decline of the immune system, ineffective catabolism, shortening of telomeres, and defects in lipoprotein metabolism. Genotyping data for a group of twenty citizen scientists is reviewed and can be further integrated with phenotypic measures of aging (including blood pressure, cholesterol, BMI, VO2 max, erythrocyte glycosylation, LDL particle size, telomere length, and lymphocyte growth rate), and used as the basis for proposed personalized interventions. Citizen-science contributed biobanks and databases are examined as a resource for the immediate, costeffective, and large-scale application of research studies.

Methodology

The DIYgenomics study design methodology has three steps: identify strongly associated genomic variants for specific conditions, find corresponding phenotypic biomarkers, and establish corresponding interventions to the extent possible. Direct-toconsumer (DTC) genomic services cover some aging conditions.

These data were included and supplemented with a more recent and exhaustive self-curation of GWAS. Self-curated GWAS references are cited; DTC references are available at

DIYgenomics.org under ‘Health Risk.’ Approximately half of the

SNPs identified in DTC and DIYgenomics curation are available for analysis in 23andme genotyping files.

The five categories of aging-related GWAS are presented in

Figures 1-5

: aging-specific GWAS, diabetes, lipids, and metabolic disease, catabolism (waste break-down) and other, heart disease and blood operations, and cancer.

As illustrated in

Figure 1

, the best-known processes of aging are not yet extensively covered in human GWAS, for example insulin/IGF-1 signaling pathways, inflammation, mitochondrial dysfunction, reactive oxygen species generation, cell cycle, stem cell generation, and immune response. Other areas such as diabetes and adiposity (

Figure 2

) have broader coverage and continue to be the focus of recent significant findings of novel loci.

New cancer studies (

Figure 5

) have been more rare, and it is not necessary to supplement DTC curation.

1. Aging-specific GWAS

Figure 1

Genotype Phenotype

Condition

1.1

Aging GWAS

1.1.1 Aging GWAS - BU

Gene(s)

1.1.2 Aging GWAS - Meta

ANK2, APOE/TOMM40,

ARMC2, ATF6, ATP6V0E,

BACH2, BTNL2, C18orf1,

C19orf36, CDKN2B,

CEACAM16, CHAF1B, CHGA,

CLSTN2, CRTAC1, CTBP2,

CTNNA3, DBC1, DCPS,

DEFB1,

EIF4E3,

FDFT1,

DKFZp762E1312,

ELL2, FAM98B,

FGD5, FGFR1,

FLJ21103, FLJ46010, GIP,

GORASP2, GPC5, GPC6,

GPR27, GRM8, GUCA1A,

IGF2BP1, IL7, KSR2, LDHD,

LHFP,

LOC388882,

LOC202459,

LOC400499,

LOC441108, LUC7L, MATN2,

MGC35295, MORN1, MSI2,

NAV2, NTN1, PARP10,

PHYHIP, POU5F1, POU6F2,

RASGRF2, SH3BP4, SLC6A7,

SMYD3, SORCS1, SORCS2,

SPIRE1,

SULT1C3,

STK32A,

SUSD3,

STX8,

TEK,

TNFRSF11A, TPPP, TTC6,

TTC6, VISA, ZC3H3

FOXO1A, GAPDH, KL, LEPR,

PON1, PSEN1, SOD2, WRN

1.1.3 Aging GWAS - Meta ACCN1, ANKRD46, BMP4,

C3orf21, CASP7, CRISPLD1,

DIRAS2, GRIK2, IL20RB,

LASS3, LOC196913, MINPP1,

OR2W3, OTUD3, PAPPA2,

PIK3C3, REM2, RGS7,

SC4MOL, SCN7A, SPRY2,

TMPRSS5, ZNF19

1.2

Insulin/IGF-1

(IIS) pathway

1.3

RNA editing

1.6

Telomere length

1.7

Immune system signaling

1.4

DNA damage repair

1.5

Cell cycle, apoptosis, and transcription

ADIPOQ, FOXO1A, FOXO3A,

SIRT1, COQ7

ADARB1/2

CHK1/CHEK1

ATR

TERC, 9p21.1, 11q22.3, ISG15

ATG16L1, IRGM, PTPN2,

PTPN22

DTC

0

0

0

1

0

0

0

0

0

9

10

11

12

13

6

7

4

5

2

3

References

1 Aging GWAS - BU

Aging GWAS - Meta

Aging GWAS - Meta

Insulin/IGF-1 signaling

Insulin/IGF-1 signaling

RNA editing

8

DNA damage repair

Cell cycle

Telomere length

Telomere length

Telomere length

Immune system

Immune system

PMID

20595579

17903295

20304771

18765803

19901535

20011587

11691784

20351400

20139977

20157543

20016137

18852199

19038835

DIY

150

35

288

15

18

1

0

4

1

Total

150

35

288

16

18

1

0

4

1

23andMe

143-147

17

61

7

18

1

0

1

1

Ref

1

2

3

4,5

6

7

8

9-10

Multi-condition

Multi-condition

Multi-condition

Insulin signaling

Protein quality (custom assay)

Transcription & translation assay

Cell turnover (custom assay)

12 IgA, IgG, IgM (mg/dL); CD levels (CD4,

Citation

Sebastiani Science 2010

Lunetta BMC Med Genet 2007

Newman J Gerontol A Biol Sci Med Sci 2010

Willcox PNAS 2008

Narasimhan Cell Cycle 2009

Sebastiani PLoS One 2009

Menoyo Cancer Res 2001

Blagosklonny Aging 2010

Codd Nat Gen 2010

Lou Aging 2009

Andrews Gerontology 2010

Lettre Hum Mol Genet 2008

Willcox J Gerontol A Biol Sci Med Sci 2008

Telomere length

CD16, CD56); lymphocyte growth rate

Ref

11

13

2. Diabetes, lipids, and metabolic disease

Figure 2

2.1

Condition

Type 2 diabetes

2.2

Fasting glucose homeostasis ADCY5, ADRA2A, C2CD4B,

CRY2, DGKB-TMEM195,

FADS1, G6PC2, GCK, GCKR,

Glucose & metabolism

Obesity

GLIS3, IGF1, MADD, MTNR1B,

PROX1, SLC2A2, SLC30A8,

TCF7L2

G6PC2, SLC2A9

NEGR1, SEC16B, TMEM18,

2.3

2.4

2.5

BMI

Adiposity & fat distribution

Total Cholesterol

ETV5, PCSK1_2, AIF1/NCR3,

BDNF, FAIM2, SH2B1, FT0,

MC4R, KCTD15

FTO, MC4R

CTNNBL1, NOS1AP, TFAP2B,

MSRA, LYPLAL1

LDLRAP1, EVI5, MOSC1,

IRF2BP2, RAB3GAP1, RAF1,

HMGCR, TIMD4, HLA, FRK,

DNAH11, NPC1L1, CYP7A1,

GPAM, SPTY2D1, UBASH3B,

BRAP, HNF1A, HPR, CILP2,

FLJ36070, ERGIC3, MAFB

2.5.1 HDL CETP, LPL, LIPC, LIPG,

GALNT2, ABCA1, MMAB-MVK,

PABPC4, ZNF648, GALNT2,

IRS1, SLC39A8, ARL15,

C6orf106, CITED2, KLF14,

PPP1R3B, TRPS1, TTC39B,

ABCA1, AMPD3, LRP4,

PDE3A,

ZNF664,

MVK,

SCARB1,

SBNO1,

LIPC,

LACTB, LCAT, CMIP, STARD3,

ABCA8, PGS1, LIPG, MC4R,

ANGPTL4, LOC55908, LILRA3,

HNF4A, PLTP, UBE2L3

0

0

18

0

0

0

0

2.5.2 LDL

2.5.3 Triglycerides

Gene(s)

TCF7L2, CDKN2A-CDKN2B,

FTO, THADA, IGF2BP2,

KCNJ11, PPARG, CDKAL1,

HHEX-IDE, NOTCH2,

SLC30A8, CDC123-CAMK1D,

JAZF1, TSPAN8-LGR5,

ADAMTS9, ZFAND6, CHCHD9,

MTNR1B, HMGA2, CENTD2,

KCNQ1, BCL11A, ZBED3,

DUSP9, IRS1, HNF1A, PRC1,

TP53INP1, KLF14

DTC

59

LDLR, APOE-C1-C4, CELSR2-

PSRC1-SORT1, APOB, NCAN-

CILP2, PCSK9, HMGCR,

SORT1, APOB, ABCG5/8,

MYLIP, HFE, LPA, PLEC1,

ABO, ST3GAL4, NYNRIN,

OSBPL7, LDLR, APOE, TOP1

APOA5-A4-C3-A1, LPL, GCKR,

MLXIPL, ANGPTL3, TRIB1,

NCAN-CILP2, LIPC, GALNT2,

ANGPTL3, GCKR, COBLL1,

MSL2L1, KLHL8, MAP3K1,

TYW1B, MLXIPL, PINX1,

NAT2, LPL, TRIB1, JMJD1C,

CYP26A1, FADS1-2-3, APOA1,

LRP1, CAPN3, FRMD5, CTF1,

PLA2G6

0

0

5

6

3

4

7

References

1 Type 2 diabetes

2 Type 2 diabetes

Type 2 diabetes

Type 2 diabetes

Type 2 diabetes

Adiposity & fat distribution

Cholesterol

PMID

18852197

20581827

19038835

20200384

20081858

19557161

20686565

DIY Total 23andMe Ref

15

16

2

0

2

5

Genotype

25

44

20

32

74

16

2

18

2

5

25

44

20

32

45

5

2

12

1

4

10

18

13

13

Citation

Mohlke Hum Mol Genet 2008

Voight Nat Genet 2010

Willcox J Gerontol A Biol Sci Med Sci 2008

Selvin N Engl J Med 2010

Dupuis Nat Genet 2010

Lindgren PLoS Genet. 2009

Teslovich Nature 2010

1-2

5

1

1

1,6

7

1,7 HDL (mg/dL); TC/HDL (ratio)

1,7

1,7

Fasting glucose, nonfasting glucose, total protein, albumin, uric acid (mg/dl); glycosylated hemoglobin (HbA1c)

Fasting & nonfasting glucose (mg/dl)

Fasting & nonfasting glucose (mg/dl)

BMI

BMI, BMI/waist circumference

BMI, caliper

Cholesterol (mg/dL)

Phenotype

LDL (mg/dL); LDL particle size

Triglycerides (mg/dL)

Ref

3,4

3

3

3

3

3

3

3

3

3. Catabolism (waste break-down) and other

Figure 3

3.1

3.2

Macular degeneration

3.3

3.4

3.5

3.6

3.7

3.8

3.9

Condition

Alzheimer's disease

Rheumatoid arthritis

Osteoarthritis

Osteoporosis

Sarcopenia

Liver function

Kidney function

Lung capacity

28

29

30

31

32

33

34

24

25

26

27

20

21

22

23

15

16

17

18

19

11

12

13

14

7

8

9

10

5

6

3

4

References

1

2

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Alzheimer's disease

Macular degeneration

Macular degeneration

Rheumatoid arthritis

Osteoarthritis

Osteoporosis

Osteoporosis

Sarcopenia

Sarcopenia

Sarcopenia

Sarcopenia

Sarcopenia

Sarcopenia

Sarcopenia

Sarcopenia

Sarcopenia

Liver function

Liver function

Kidney function

Kidney function

Lung capacity

Lung capacity

Lung capacity

Lung capacity

Lung capacity

Genotype Phenotype

Gene(s)

APOE, TOMM40, CLU,

ADAM10, CTNNA3, GALP,

APOC1, GAB2, GOLPH2,

LRAT, LMNA, TRPC4AP,

PCDH11X, PICALM, CR1

ARMS2/HTRA1, CFH, C2/CFB,

C3-R80G

DTC

3

9

PTPN22, PADI4, MMEL1,

STAT4, IL2/IL21, MHC, HLA-

DRB1, TNFAIP3/OLIG3,

TRAF1/C5

EDG2, PTGS2, PLA2G4A,

DVWA

PPAP2B, GPR177, HECW2,

CASR, MMRN1, IRX2, PDZD2,

TGFBI, CACNB2, DOCK1,

SOX6, PDGFD, PDGFD,

RAD51L1, SALL1, FBXO31,

CDH2, RANKL, RANK, OPG

IGF-1, ACE, ACTN3, IL-1B, IL-

1RN, IL6, CKMM/CKM,

MSTN/GDF8, PEPCK-C/PCK1,

VDR

33

2

0

0

DIY Total 23andMe Ref

28 31 17 1-8 Spinal fluid protein signature of three proteins (CSF beta-amyloid protein 1-42

1 10 7

(CSF Aß1-42), total CSF tau protein, and

CSF phosphorylated tau181P (P-

Tau181P)); mid-life cholesterol levels

11 Vision impairment (blurry or white-spot

0 33 12 area in center of vision), early detection of choroidal neovascularization

Blood assay to determine pre-clinical autoantibody and cytokine profiles

Ref

9,10

12

13

3

17

5

17

2

7

14

15, 16

Joint function

Bone mineral density

ABCG8, HLA-DPA/B, CPN1-

ERLIN1-CHUK, PNPLA3-

SAMM50, ALPL, GPLD, ABO,

JMJD1C, REEP3, HNF1A,

IL12A, IL12RB2, HLA-B*5701,

IL28B

UMOD, APOE, ABCA1, PTGS1,

TNF, CPB2, AGTR1, OR13G1,

GNB3

NRF1,

PPARGC1A

ADRB1, APOE,

20548944

20205168

20175886

20459474

19237423

19630564

20490824

19724965

20005538

20148371

20157530

19916168

19038835

20686651

19056482

16421173

19666693

20044476

20459474

19713012

PMID

20029386

20457951

20298972

20236449

20460622

19608551

20595579

17761686

20697045

19648749

17884985

18724980

19460157

18325907

0

0

0

17

22

2

6

17

22

2

6

10

5

1

4

17-24 Muscle mass baseline, degeneration & replacement; quality of proteolytic systems activation (calpain, ubiquitin-proteasome, and caspases), and alteration in muscle growth factors

26 Gallstones, fatty liver, primary cholestatic

28-29

19,20,

31-33

Citation

Roses Pharmacogenomics 2009

Roses Arch Neurol 2010

Lutz Alz Dement 2010

Erekin-Taner Alz Res & Therapy 2010

Seshadri JAMA 2010

Kim Hum Mol Genet 2009

Sebastiani Science 2010

Miyashita Hum Mol Genet 2007

De Meyer Arch Neurol 2010

Solomon Dement Geriatr Cogn Disord 2009

Kanda PNAS 2007

Friedman Am J Ophthalmol 2008

Hueber Arthritis Res & Therapy 2009

Mototani Hum Mol Gen 2008

Hsu PLoS Genet 2010

Roshandel J Bone Miner Res 2010

Cauci BMC Med Genet 2010

Buxens Scand J Med Sci Sports 2010

Ruiz J Physiol 2009

Ostrander Annu Rev Genomics Hum Genet 2009

Kostek Eur J Appl Physiol 2010

Wackerhage J Sports Sci 2009

Eynon Metabolism 2010

Bustamante-Ara Int J Sports Med 2010

Scicchitan Aging 2009

Melum World J Gastroenterol 2009

Willcox J Gerontol A Biol Sci Med Sci 2008

Gudbjartsson PLoS Genetics 2010

Yoshida Genomics 2009

Defoor Eur Heart J 2006

Enyon Exp Physiol 2009

Tsianos J Appl Physiol 2010

Scand J Med Sci Sports 2010 Buxens

Sergi Clin Nutr 2010 liver diseases, chronic hepatitis C virus

(HCV) infection, and progressive liver fibrosis. Serum levels of hepatic enzymes:

GOT (AST), GPT (ALT), ALP, GGT (IU/L)

Measure: creatinine (mg/dL); eGFR (mL)

VO2 max

25

27

30

34

4. Heart disease and blood operations

Figure 4

Condition Gene(s) DTC

Genotype

DIY Total 23andMe Ref

Phenotype

5

6

3

4

7

8

1

2

4.1

Cardiovascular disease

Plasma lipid transfer CETP protein

Serum lipoprotein levels and particle size

APOA4, APOC3

Hemostatic factors

(Fibrinogen, FVII, PAI1, tPA, vWF)

AB002360,

AK092739,

AB116074,

AK123267,

AK127723, APG4C, ATP2B1,

BC036771, CR603372, CSK,

CYP17A1, F7, F10, HSPC159,

LRRC7, MCF2L, NEGR1,

PLEKHA7, PROZ, SLC9A10,

SMYD3, VAV3, ZNF165

Blood pressure essential hypertension

& ATP2B1, CACNB2, CSK,

CYP17A1, ITGA9, MTHFR,

PLEKHA7, PMS1, TBX3-TBX5,

4.2

Coronary artery disease & atherosclerosis

ULK4, ZNF652

CDKN2A-CDKN2B, CELSR2-

PSRC1-SORT1,

NPY

MTHFD1L,

4.3

4.4

Myocardial infarction

Atrial fibrillation

CDKN2A/CDKN2B,

CELSR2/PSRC1,

MIA3, MRAS,

PHACTR1,

CXCL12,

MTHFD1L,

SH2B3,

SLC5A3/MRPS6/KCNE2,

WDR12

CAV1, PITX2/ENPEP, TBX5,

ZFHX3

4.5

C-reactive protein (CRP) APOE, CRP, LEPR, HNF1A,

GCKR, IL6R, 12q23

0

0

0

0

12

18

5

1

References

Cardiovascular disease

Cardiovascular disease

Cardiovascular disease

Cardiovascular disease

Cardiovascular disease

Cardiovascular disease

Coronary artery disease

Atherosclerosis

PMID

20068209

17190939

16602826

17903294

20414254

19038835

18852197

19119412

1

1

25

27

25

0

0

7

1

1

25

27

37

18

5

8

1

1

11

13

4

8

5

6

Citation

Sanders JAMA 2010

Barzilai Neurology 2006

Atzmon PLoS 2006

Yang BMC Med Gen 2007

Hong J Hum Genet 2010

Willcox J Gerontol A Biol Sci Med Sci 2008

Mohlke Hum Mol Genet 2008

Shah PLoS Genetics 2009

1-2

3

Systolic & diastolic Blood Pressure (mm

Hg); Hematocrit (%); Hemoglobin (g/dL);

RBC, WBC, platelets (x 10

4

/uL)

4

5

7-8

7 C-reactive protein (CRP) (mg/L)

Ref

6

5. Cancer

Figure 5

5.01

5.02

5.03

5.04

Condition

Basal Cell Carcinoma

Bladder

Brain (Glioma)

Breast

Gene(s)

CDKN2A/B, KRT5, PADI6,

TERT

MYC, PSCA, TERT, TP63

CCDC26, CDKN2A/B, RTEL1,

TERT

CASP8, COX11, FGFR2, LSP1,

MAP3K1, MRPS30, NEK10,

RAD51L1, TNRC9/TOX3

DTC

6

4

4

17

5.05

Breast BRCA mutations CHEK2, FGFR2, 16q12 region

5.06

Colorectal

5.07

5.08

5.09

5.1

5.11

Esophageal

Larynx

Leukemia

Lung

Melanoma

5.12

Neuroblastoma

5.13

Oral and Throat

5.14

Ovarian

5.15

Pancreatic

5.16

5.17

5.18

5.19

Prostate

Stomach

Testicular

Thyroid

BMP4, C11orf92, CRAC1,

EIF3H, POU5F1P1, SMAD7

PSCA

ADH7

ACOXL, IRF4, PKRD2, SP140

CHRNA3/A5/B4,

CHRNA3/LOC123688, TERT

ASIP, MC1R, PIGU , SLC45A2,

TYR , TYRP1

6p22

ADH7

BNC2, LOC648570, CNTLN

ABO, CLPTM1L/TERT, NR5A2

CTBP2, EHBP1,

IGF2/IGF2AS/INS/TH, JAZF1,

KLK2/KLK3, LMTK2, MSMB,

NKX3.1, NUDT11, POU5F1P1,

SLC22A3, TCF2, TERT, TET2

PSCA

BAK1, KITLG, SPRY4

FOXE1, NKX2-1

2

1

1

1

4

43

6

9

1

1

1

3

3

3

9

0

0

0

Genotype

DIY Total 23andMe

0 6 6

4

4

17

4

4

16

0

0

0

0

0

0

0

0

0

0

0

0

0

0

0

3

9

1

1

6

9

2

1

1

1

4

43

1

3

3

1

3

3

6

3

1

1

2

3

8

1

1

1

4

27

Discussion

These ~thousand variants associated with aging and their corresponding phenotypic measures provide the start of a comprehensive program for personal aging measurement and intervention. There are two kinds of intervention, traditional solutions and novel solutions. Traditional solutions consist of the usual condition management through diet, exercise, vitamins, and pharmaceuticals. Novel interventions consist of a variety of emerging solutions, many of which are speculative. Some of these include a crosslink breakers supplement to improve systolic hypertension (Zieman Journal of Hypertension 2007), brain fitness programs and mid-life cholesterol management for Alzheimer’s disease, TA-65 telomerase activation (TA Sciences) for telomere length management, resistance weight lifting for sarcopenia, interval training and aerobic exercise for VO2 max improvement, and blood-based assays for early detection and response to rheumatoid arthritis (Swanson Nat Rev Rheumatol 2009), macular degeneration (MacuCLEAR), and kidney and liver disease.

Conclusion

An urgent contemporary objective in public health is to implement preventive medicine. Tools are needed for personalized genome interpretation, and the meaningful integration of multiple health data streams: various levels of genomic and phenotypic data, and as they become available, environmental, microbiome, and other data.

The large-scale open platforms of citizen science biobanks could be ideal for crowdsourced longitudinal data collection, targeted patient recruitment, and the conduct of a new generation of health research studies.

Acknowledgements

We would like to acknowledge review feedback from Lorenzo

Albanello, Mark Hamalainen, and Anne and Gary Hudson.

DIYgenomics is a non-profit research organization coordinating patient-driven clinical trials and providing personal genome data applications for 20 health conditions and 250 pharmaceutical drugs at

http://www.DIYgenomics.org

.

Download