Advances in Prenatal Diagnosis Dr Bryan Beattie Consultant in Fetal Medicine Cardiff and Vale UHB Advances in Prenatal Diagnosis • • • • NIPT CGH Genome Sequencing Congenital Heart Disease Smartphone Apps Brave New World Brave New World is a novel written in 1931 by Aldous Huxley and published in 1932. Set in London of AD 2540 (632 A.F. – "After Ford" – in the book), the novel anticipates developments in reproductive technology, sleep-learning, psychological manipulation, and classical conditioning that combine to profoundly change society. The title is from Miranda's speech in William Shakespeare's The Tempest O wonder! How many goodly creatures are there here! How beauteous mankind is! O brave new world, That has such people in't. — William Shakespeare, The Tempest, Act V, Scene I, ll. 203–206 Test Sensitivity 65% False Positive Gest. 1:20 15-18w 1:30 15-18w 1:40 11-14w TRIPLE 75% QUAD 85% Combined 1:1000 99% NIPT 10+w National Screening Programmes - UK TRIPLE TRIPLE TRIPLE QUAD Combined QUAD Combined Combined TRIPLE QUAD Combined Combined TRIPLE QUAD Combined Combined Brave New World YEAR NIPT 2009 2010 2011-13 2014 Maternal Blood Cell Free DNA Plasma Protein Cell Free RNA White Blood Cell Red Cell Syncytiotrophoblast Cells - Extraction and Separation Fetal Cell Syncytiotrophoblast Dennis Lo - 1997 Chemical Pathologist Dennis Lo, Chinese University of Hong Kong Discovered in 1997: • roughly 10% of the cell-free DNA floating in a pregnant woman's blood stream stems from her fetus. Published in 2010 “Science Translational Medicine” • enough fragments of fetal DNA to reconstruct the fetus's whole genome • should be possible to use this DNA to test the unborn child for genetic diseases without exposing it to the risk of an invasive procedure. • biggest advantage saving all those babies that would be lost Warned • Use it to target specific conditions • Not whole genome or late onset cardiovascular disease, Alzheimers etc Free Fetal DNA and RNA Cell Free DNA Cell Free RNA Fetal DNA in Maternal Blood How It Works • What: – Blood Sample 10+ weeks after counselling • Who: – Advanced maternal age – Positive screening test (Quad, NT) – Ultrasound abnormalities – Previous aneuploidy – ?ANY PREGNANT WOMAN • Accuracy over 99% False Positive 1:1000 • Trisomy 21,18,13,XO, Gender Anytime from 10 weeks Free Fetal DNA 10wks USA 2011 Redwood City San Jose San Diego Redwood City Big Business • Demand for prenatal testing is likely to increase • USA non-invasive market could exceed US$1 billion a year. • Sales volumes by Sequenom “substantially exceeded expectations” • Unaffordable for low-income or uninsured women (or the NHS?) • Costs ranged from £500 for Ariosa to £1700 for Sequenom (same test!) Legal Battles 14 Oct 2005 Sequenom licenses patent for non-invasive prenatal diagnosis 10 Aug 2010 Sequenom’s lawyers send Verinata warning that Verinata is developing tests that will infringe on Sequenom’s patent and patent application. 30 Aug 2011 Stephen Quake — founder of Verinata — and Hei-Mun Fan issued a patent for ‘Determination of fetal aneuploidies by massively parallel DNA sequencing’. 17 Oct 2011 Sequenom launches the MaterniT21 test. 6 Dec 2011 Sequenom sends Aria Diagnostics a letter warning about patent infringement. 19 Dec 2011 Aria files a complaint against Sequenom. 6 Jan 2012 Natera files a complaint against Sequenom. 24 Jan 2012 Sequenom sues Aria. 22 Feb 2012 Verinata and Stanford University sue Sequenom. 1 Mar 2012 Verinata launches the Verifi prenatal test. 7 May 2012 Ariosa (formerly Aria) launches the Harmony prenatal test. EUROPE 2012 Praena Germany Lichenstein Austria Switzerland UK 2012 December 2012 Harmony blood test and scan10 weeks £750 Cardiff Free CVS if Pos Results 12 weeks Option STOP Detection False Pos 99% 0.1% UK 2013 September 2103 Blood test and scan 10 weeks £320 Cardiff Results 14 working days Detection False Pos 99% 0.1% RCOG 2014 Non-invasive Prenatal Testing is likely to become a primary screening method in pregnancy Combined Screening £100 85% for 1:40 FP NIPT in NHS £100 99% for 1:1000 FP GP MAILSHOT 2014 – Time for Change? But How Long Will it Take!! Combined Test - Wales 2014 Welsh Executive National Standards Advisory Group Most Obstetricians RAPID Study Lynn Chitty UCLH Publish 2015 Test Detected 65 Amnios / Miscarriage 5000 TRIPLE Gest. 15-18w 55 75 3300 15-18w QUAD 33 2500 11-14w 85 Combined 25 100 10+w 99 NIPT 1 Wales - 3 years 100,000 births – 100 cases of Down Syndrome. (100% uptake) Case For Universal NIPT Proven screening test in low risk population S imple A ccurate F lexible E conomical R eliable simple blood test, Pos or Neg 99% detection , 1:1000 FP anytime from 10 weeks, twins £100 each test and very few amnios quality control is a laboratory issue Karyotyping G Banding Array CGH EACH STUDY Miscarriage Dev. Delay Abnormal Scan 10% Extra RESOLUTION Standard 5-10kbp High resolution 200 bp Congenital Heart Disease Commoner than Down Syndrome Detection rate at Anomaly Scan UK poor Detection rate at Anomaly Scan WALES better Detection at Fetal Echo Detection at Pulse Oximetry Cardiologist Dr Orhan Uzun and Llanelli sonographers 1:200 30% 50% 95% 90% Hand and Foot – 10 minutes Too Much Too Soon? Ethics / Counselling Eugenics and Sex Selection Brave New World? P.A.G.E. Whole genome sequencing Whats Next? Smartphone Doppler Unbornheart See, Hear, Record, Monitor, Share Smartphone Tracker Bellabeat Doppler, Kicks, Diary, weight, Mood Smartphone Custom Growth Charts Smartphone Vitals Pulse/BP Body Composition Analysis Glucose