Dr. Aby Abraham, MD, DM Assistant Professor Dr. Alok Srivastava, MD, FRACP, FRCPA, FRCP Professor of Medicine & Dr. Sukesh C. Nair, MD, FRCPA (Haematology), Professor, Department of Haematology and Department of Transfusion Medicine & Immuno Haematology, Christian Medical College, Vellore-632004. Why NICE Registry? Off label uses >> Evidence-based indications No consensus in dose and duration Practice-based collection of data NovoSeven® in Critical care Evaluation (NICE Registry) in April 2006 NovoSeven® Advisory Board – Dr. Alok Srivastava, MD, FRACP, FRCPA, FRCP Dr. M.B.Agarwal, MD, MNAMS, Dr. Palepu Gopal, MD, FRCA, CCST, Dr. Rajesh Pande, MD, PDCC. Aim: To see would it be possible to gather new information? 09/04/2011 NICE Registry 2011 2 Acknowledgements DR. A.C.SHUKLA DR. A.SATISH DR. AMITAVA SAHA DR. ANAND KATKAR DR. ARIJIT BOSE DR. C.K.AURANGABADKER DR. H. GADHIKAR DR. KAYANOOD KADAGNATT DR. KULDEEP A.DALAL DR. MITUL P. CHARDA DR. M.BHATTACHARYA DR. OMENDER SINGH DR. PRABHAKAR. S DR. PIYUSH RANJAN DR. RANJIT DESHMUKH DR. RAJESH PANDE DR. ROGESH BHURAT DR. ROHINI SRIDHAR DR. SAMEER PALTEWAR DR. SHASHIKANT J. APTE DR. SHAILESH R. SINGI DR. SHIVINDER SINGH DR. VILAS E. TAMBE DR. VIJAY RAMANAN DR. VINODAN DR. COL.SUDHIR MEHROTRA DR. A.R. BASU DR. A.N. JHA DR. ADARSH CHAUDHRY DR. MRINAL SIRCAR DR. P.AGARWAL DR. SAMUEL SYLVESTER 09/04/2011 MATA CHANAN DEVI HOSPITAL, DELHI. ABHAYA HOSPITAL, BANGALORE. B.P.PODDAR HOSPITAL, KOLKATA. BHARATI VIDHYAPEETH UNIVERSITY MEDICAL COLLEGE & HOSPITAL, PUNE. AMRI, KOLKATA. VIVEKANAND HOSPITAL, NAGPUR. DEENANATH MANGESHKAR HOSPITAL, PUNE. JEHANGIR HOSPITAL & MEDICAL CENTRE, PUNE. JASLOK HOSPITAL, MUMBAI. APOLLO HOSPITAL, CHENNAI. KOLKATA MEDICAL COLLEGE HOSPITAL, KOLKATA. MAX SUPER SPECIALITY HOSPITAL, SAKET. APOLLO HOSPITAL, HYDERABAD. SIR GANGA RAM HOSPITAL, DELHI. RUBY HALL CLINIC, PUNE. FORTIS HOSPITAL, NOIDA. LOKMANYA HOSPITAL, PUNE. APOLLO SPECIALITY HOSPITAL, MADURAI. SURETECH HOSPITAL & RESEARCH INSTITUTE, NAGPUR SAHYADRI SPECIALITY HOSPITAL, PUNE. FERNANDEZ HOSPITAL, HYDERABAD. BASE HOSPITAL, DELHI. CRITICAL CARE UNIT, NAGPUR. RUBY HALL CLINIC, PUNE. MEDICAL TRUST HOSPITAL, COCHIN. MH AMBALA MILITARY HOSPITAL COMMAND HOSPITAL, EASTERN COMMAND, KOLKATTA. MEDANTATHE MEDICITY HOSPITAL, GURGAON. MEDANTA THE MEDICITY HOSPITAL, GURGAON. FORTIS HOSPITAL, NOIDA. MAX SUPER SPECIALITY HOSPITAL, SAKET. FRONTIER LIFELINE HOSPITAL, CHENNAI. NICE Registry 2011 Contd… 3 Acknowledgements DR. BALACHANDRAN NAIR. P DR. NARENDRANATHAN. M DR. RAJALAKEHMI. A DR. SATISH. B DR. AJITH K. NAIR DR. VIJAYAN. K.N DR. MATHEW THOMAS DR. REVATHI RAJ DR. ZAHEER AHMED SAYEED DR. RAMNATH.S DR. VIJAYA SHANKAR DR. SOMNATH CHATERJEE DR. VIJAYA MANOHAR DR. KIRTHIVASAN DR. BHARESH DEDHIA DR. PRAVEEN MENON DR. MOHAN MATHEW DR. KHALEEL DR. MADANMOHAN RAO DR. HARISH DR. VASUDEV DR. ABHIJIT SARKAR DR. S.K.SINGH DR. MANASH GHOSH DR. NITIN.K / DR.ARUN AGARWAL DR. VISHAL SINGH DR. NIRMALA AGARWAL DR. CHIRAG SHAH DR. CHIRAG MATRAVADIA DR. SELVAKUMAR. 09/04/2011 KIMS, TRIVANDRUM. KIMS, TRIVANDRUM. KIMS, TRIVANDRUM. KIMS, TRIVANDRUM. KIMS, TRIVANDRUM. KIMS, TRIVANDRUM. KIMS, TRIVANDRUM. APOLLO HOSPITAL, CHENNAI. APOLLO HOSPITAL, CHENNAI. APOLLO HOSPITAL, CHENNAI. APOLLO HOSPITAL, CHENNAI. MANIPAL HOSPITAL, BANGALORE. AGADI HOSPITAL, BANGALORE. FRONTIER LIFELINE HOSPITAL, CHENNAI. WOCKHARDT HOSPITAL, MUMBAI. LOURDES HOSPITAL, ERNAKULAM. LAKESHORE HOSPITAL & RESEARCH CENTRE, COCHIN. MEDICAL TRUST HOSPITAL, COCHIN. HOPE HOSPITAL, HYDERABAD. KRISHNA CHILDREN’S HOSPITAL, HYDERABAD. MAX BALAJI HOSPITAL, DELHI. PEERLESS HOSPITAL, KOLKATA. AMRI HOSPITAL, KOLKATA. GNRC, GOUHATI. BMC HOSPITAL & RESEARCH CENTRE, JAIPUR. FORTIS ESCORTS HOSPITAL, OKHLA. SANT PARMANAND HOSPITAL, DELHI. APOLLO HOSPITAL, AHMEDABAD. STERLING HOSPITAL, RAJKOT. MADRAS MEDICAL MISSION HOSPITAL, CHENNAI. NICE Registry 2011 Contd… 4 Acknowledgements DR. SHABBAR H.K JOAD DR. A.K. MANDAL DR. BHARDWAJ / DR. BETTY ELIZABETH DR. SELVA KUMAR / DR. MANOHAR DR. VIMALA / DR. ROY/ DR. UDAY DR. NEVILLA AG SOLOMON DR. THANGARAJ / DR. PAUL JUDE DR. VIJAYSHANKAR DR. M. RAJA DR. JAYASHREE GAJRAJ DR. WAHIDA SURESH DR. SRINIVAS DR. LT. COL. P. MUKERJI DR. COL TVSP MURTHY DR. BRIG M LUTHRA DR. RAJESH PANDE DR. DEEPA DAS DR. VIVEK SINGH DR. YATIN METHA DR. RAJESH SHARMA DR. VINEET SANKHLA DR. SIBABRATA BANNERJEE DR. SHOBHA / DR.SATISH KRISHNA DR. MAMMEN CHANDY DR. ALOK SRIVASTAVA DR. AURO VISWABANDYA DR. VIKRAM MATHEWS DR. ARUNA KEKRE DR. NAGAMANI SEN DR. SUBRAMANIAN DR. BIJU GEORGE 09/04/2011 FORTIS ESCORTS HOSPITAL, JAIPUR. FORTIS HOSPITAL, MOHALI. MADRAS MEDICAL MISSION HOSPITAL, CHENNAI. MADRAS MEDICAL MISSION HOSPITAL, CHENNAI. MADRAS MEDICAL MISSION HOSPITAL, CHENNAI. APOLLO CHILDRENS HOSPITAL, CHENNAI. APOLLO SPECIALITY HOSPITAL, CHENNAI. APLLO SPECIALITY HOSPITAL, CHENNAI. APOLLO SPECIALITY HOSPITAL, CHENNAI. APOLLO SPECIALITY HOSPITAL, CHENNAI. APOLLO SPECIALITY HOSPITAL, CHENNAI. APOLLO CHILDRENS HOSPITAL, CHENNAI. ARMY HOSPITAL(R&R), DELHI. COMMAND HOSPITAL, LUCKNOW. ARMY HOSPITAL (R&R), DELHI. B.L KAPOOR MEMORIAL HOSPITAL, NEWDELHI. PARAS HOSPITAL, GURGOAN. COLUMBIA ASIA HOSPITAL, GURAGOAN. MEDANTA INSTITUTE OF NEUROSCIENCES, GURAGAON. ESCORTS HEART HOSPITAL, NEWDELHI. APOLLO HOSPITALS, AHMEDABAD. MISSION OF MERCY, KOLKATA. SREE UTHRADOM THIRUNAL HOSPITAL,TRIVANDRUM. CHRISTIAN MEDICAL COLLEGE, VELLORE. CHRISTIAN MEDICAL COLLEGE, VELLORE. CHRISTIAN MEDICAL COLLEGE, VELLORE. CHRISTIAN MEDICAL COLLEGE, VELLORE. CHRISTIAN MEDICAL COLLEGE, VELLORE. CHRISTIAN MEDICAL COLLEGE, VELLORE. CHRISTIAN MEDICAL COLLEGE, VELLORE. CHRISTIAN MEDICAL COLLEGE, VELLORE. NICE Registry 2011 5 Registry outline Both web-based (www.niceindia.net) and nonweb based Components of Registry Demographic data Clinical History and Indication of NovoSeven® Laboratory parameters Dose of NovoSeven® and Response to this complication Outcome 09/04/2011 NICE Registry 2011 6 19/04/2009 Christian Medical College, Vellore. NICE Registry 2011 7 7 19/04/2009 09/04/2011 Christian Medical College, Vellore. NICE Registry 2011 8 8 19/04/2009 09/04/2011 Christian Medical College, Vellore. NICE Registry 2011 9 9 Collection of data NICE Registry in April 2006 to Feb 2011 Distribution of demographic data (n=380) Age n Median Range (in years) Overall 380 40 1–91 Age ≤15 53 3 1–15 Age > 15 327 46 16–91 Sex n % Male Female 247 133 65 35 Indications (n=380) Milliliter Blood loss prior to the usage of NovoSeven® * Number of patients Haematological parameters Hb – Haemoglobin, PT – Prothrombin time, aPTT – activated partial thromboplastin time Other parameters P = 0.132 Mean Mean P=0.004 N 84 54 54 N 09/04/2011 38 p=0.212 Mean Mean p=0.054 37 10 38 p = 0.396 P = 0.373 N 69 17 8 17 N 8 NICE Registry 2011 42 17 23 8 23 8 15 Abnormal LFT (n=46) p=0.494 p=0.569 Median p=0.455 N 25 19 29 20 24 17 SGOT - Serum glutamic oxaloacetic transaminase; SGPT - Serum glutamic pyruvic transaminase Median Dosage of NovoSeven® used (µg/kg) (Based on body weight) N 380 98 23 14 9 Patients received 3 doses of NovoSeven® Median Range 2 42 24–60 Anticoagulant-associated bleed 1 90 90 UGI & LGI bleed 2 75 70–80 Cardiac 1 86.67 87 Thrombocytopenia/Coag/IC/Platelet 1 66 66 IC/Platelet 2 41 16–66 IC 3 30.76 16–66 Liver disease/UGI/Platelet 1 70 70 Indication (3 doses=9) Obstetric bleeding (µg/kg) (µg/kg) Patients received >3 doses of NovoSeven® Indication (>3 doses=14) Median Range (µg/kg) (µg/kg) Other surgery, Thrombocytopenia, Other Coagulopathies 1 40 40 Liver disease, UGI 1 90 90 Anticoagulate 1 90 90 Other coagulopathies 6 66.18 39–80 Thrombocytopenia, Dengue 1 67.5 68 IC 1 41.16 41 Obstetric bleeding 1 53 53 Platelet 1 150 150 Other Coagulopathies, Thrombocytopenia, Liver disease 1 80 80 Cardiac 1 26.6 27 Dengue 2 48.75 30–68 NovoSeven® – Indication and doses Medical causes of bleeding NovoSeven® – Indication and doses Median Dose (ug/kg) Surgical causes of bleeding and trauma Blood products usage in different medical/surgical condition before and after the usage of NovoSeven® Blood products usage in liver disease R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in UGI/LGI bleed R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in thrombocytopenia R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in dengue haemorrhagic fever R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in anti-coagulopathies R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in intracerebral haemorrhage R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in trauma R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in other coagulopathies R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in obstetric bleeding R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in cardiac surgery R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in other surgery R = RBCs, W = WBCs, P = Platelet, C = Cryoprecipitate, F = Fresh frozen plasma Blood products usage in different medical condition after the usage of rFVIIa After the administration of rFVIIa, most of the patients received ≤ 3 units of RBCs Transfusion of all blood products was substantially reduced Response 50 42.7 42.3 41.4 38.3 Percentage 40 28.3 30 20.3 20 0N 19.5 12 10.1 10 98 67 48 24 1 hr (237) Bleeding stopped 28 27.9 26 25.5 20.2 9.8 7.8 159 76 96 45 6 hrs (376) Minimal Bleeding 40 59 43 12 12 hrs (154) Bleeding reduced 35 23 16 Day 2 (82) Bleeding not reduced 8 Overall efficacy of NovoSeven® Overall survival rate with usage of NovoSeven® Usage of NovoSeven® in different medical and surgical bleeding Usage of NovoSeven® in anticoag-associated bleeding n= 11; Median dose – 60 µg/kg Efficacy Survival rate Usage of NovoSeven® in intra-cerebral haemorrhage n= 70; Median dose – 46.5 µg/kg Efficacy Survival rate Usage of NovoSeven® in cardiac surgery n= 66; Median dose – 40 µg/kg Efficacy Survival rate Usage of NovoSeven® in trauma n= 44; Median dose – 55 µg/kg Efficacy Survival rate Usage of NovoSeven® in obstetric bleeding n= 48; Median dose – 60 µg/kg Efficacy Survival rate Usage of NovoSeven® in other surgery n= 31; Median dose – 60 µg/kg Efficacy Survival rate Usage of NovoSeven® in UGI/LGI n= 40; Median dose – 60 µg/kg Efficacy Survival rate Usage of NovoSeven® in liver disease n= 46; Median dose – 60 µg/kg Efficacy Survival rate Usage of NovoSeven® in other coagulopathies n= 42; Median dose – 60 µg/kg Efficacy Survival rate Usage of NovoSeven® in thrombocytopenia n= 39; Median dose – 60 µg/kg Efficacy Survival rate Usage of NovoSeven® in dengue haemorrahagic fever n= 15; Median dose – 75 µg/kg Efficacy Survival rate Adverse events Adverse events Number of events CVA 1 DVT 2 Multi-organ failure 4 ARDS 7 Others 3 Causes of death [n=112] ACUTE FULMINANT HEPATIC FAILURE, SEPSIS, ARDS DHF/DIC/MODS. ACUTE RENAL FAILURE, METABOLIC ACIDOSIS, ANTRODUODENAL ULCER BLEED, CHRONIC LIVER DISEASE, CIRRHOSIS, PHT, DUODENAL VARICES DIC, MULTI ORGAN FAILURE - 2 ADVANCE METASTATIS CARCINOMA OF URETER WITH SEPSIS, MOF DIC, INTRACEREBRAL BLEEDING, ESRD, CHRONIC LIVER DISEASE APLASTIC ANAEMIA, DIFFUSE ALVEOLAR HAEMORRHAGE, GI BLEED, MODS, ARDS & ARF DISSEMINATED INTRAVASCULAR COAGULATION ARDS, CARDIORESPIRATORY ARREST END STAGE HF, ORTHOTOPIC HEART TRANSPLANTATION, SEPTICAEMIA, MODS ARDS, SHOCK, MULTI ORGAN FAILURE FEVER + DIC + DIFFUSE ALVEOLAR HAEMORRHAGE ASPIRATION FUNGAL PNEUMONIA & SEPTICEMIA BRADYCARDIA,HYPOTENSION, DILATED CARDIOMYOPATHY FUNGAL SEPSIS, SEPTIC SHOCK, SEVERE DIC BRAIN STEM DYSFUNCTION, EVANS SYNDROME, POST SPLENECTOMY - 2 HAEMORRAGIC SHOCK - 2 BLUNT TRAUMA ABDOMEN WITH MULTIPLE MESENTRIC TEARS, WITH SEPSIS WITH MOF. HEMORRHAGIC SHOCK / PPH CARDIAC ARREST, CARDIOGENIC SHOCK - 3 HYPOTENSIVE SHOCK CHRONIC LIVER DISEASE - 3 HYPOVOLEMIC SHOCK CMV PNEUMONIA WITH ARDS HYPOXIC ISCHAEMIC ENCEPHALOPATHY Causes of death [n=112] (Contd.) DECOMPENSATED LIVER DISEASE, MOF MODS DENGUE HAEMORRHAGIC SHOCK - 2 ICH DHF & CARDIAC ARREST HYPOVOLUEMIA SECONDARY TO SEVERE BLOOD LOSS WITH MULTIPLE LIVER LACERATIONS TO BLUNT TRAUMA ABDOMEN & CHEST ARDS & ARF INTRACEREBRAL HAEMORRHAGE INTRACRANIAL HAEMORRAGE MULTISYSTEM ORGAN FAILURE INTRACEREBRAL HAEMORRHAGE PATIENT DIED FROM OTHER COMPLICATIONS, BLEEDING WAS STOPPED AFTER rFVIIa INTRACTABLE VENTRICULAR ARRHYTHMIA WITH LOW CARDIO OUTPUT, POST CABG PERI AMPULLARY & PANCREATIC CARCINOMA PATIENT EXPIRED AFTER 8 DAYS BECAUSE OF ACUTE INTRACTABLE CARDIO RESPIRATORY FAILURE DUE TO FATTY LIVER OF PREGNANCY, THOUGH HER BLEEDING SEVERE PAH CRISIS, S/P TRUNCUS ARTERIOSUS REPAIR STOPPED AFTER rFVIIa (VSD CLOSURE, RV TO PA CONDUIT) INTRACTABLE RESPIRATORY FAILURE DUE TO RECURRENT PNEUMONIA WITH SEPSIS PULMONARY HAEMORRHAGE AND SEPSIS LIVER DAMAGED – 4 POLY TRAUMA, COLLAPSE OF RIGHT LUNG LOW CARDIAC OUTPUT,SEVERE PULMONARY ARTERIAL HYPERTENSION POLYTRAUMA LOW CARDIAC OUTPUT, MODS, AV CANAL DEFECT, VSD POST-OP SEPSIS LUNG BRONCHOPNEUMONIA, RENAL TRANSPLANT IMMUNOSUPPRESION, TYPE II DIABETES MELLITUS PPH WITH MULTIORGAN FAILURE MASSIVE BLEEDING/SEPSIS/ARDS MALIGNANT HYPERTHERMIA, RHABDOMYOLYSIS, ARF, SEPTICEAMIA, RESPIRATORY DISTRESS, DIC Causes of death [n=112] (Contd.) METABOLIC ACIDOSIS, SEVERE ANEMIA, SHOCK PULMONARY HAEMORRHAGE / ARDS MLC CARE REFRACTORY ACUTE CARDIAC ALLOGRAFT REJECTION MODS RTA, LIVER LACERATION, FULMINANT HEPATIC FAILURE, DIC MODS DUE TO DHF, IC BLEED MODS, ACS, REFRACTORY SHOCK MSOF, AML S/P ARTERIAL SWITCH OPERATION FOR D-TGA, ASD, PDA WITH HYPOXIC ENCEPHALOPATHY S/P ARTERIAL SWITCH OPERATION, VENTRICULAR TACHYCARDIA DEGENERATING TO CARDIAC ASYSTOLE SDH WITH MIDLINE SHIFT BRIANSTEM CONTUSION, RESPIRATORY ARREST MULTI-ORGAN FAILURE -3 SEPSIS DUE TO IMMUNOCOMPROMISED STATE MULTI-ORGAN FILURE WITH DIC SEPSIS WITH ARDS WITH ARF - 4 MULTI-ORGAN FAILURE WITH BLEEDING DIATHESIS SEPSIS, LIVER DAMAGED SEPSIS, MULTI-ORGAN FAILURE SEPTICAEMIA, LEFT LOWER LIMB, DIC, ARF SEPSIS, CHRONIC LIVER DISEASE, UPPER GI BLEED SEPTICEMIA,CARDIOGENIC SHOCK SEPSIS, MODS WITH UNCONTROLLED BLEEDING SEVERE CALCIFIC AORTIC STENOSIS SEPSIS/MODS/ARF/MOF - 3 SEVERE HYPOTENSION & EXCESS OF BLEEDING SDH, INTRACEREBRAL HAEMORRHAGE, DM, HTN, CRF SUB-ARACHNOID HAEMORRHAGE, BRAIN STEM DYSFUNCTION, CARDIO-RESPIRATORY ARREST SEPTIC SHOCK, MULTI-ORAGAN FAILURE, ACUTE RENAL FAILURE TERMINAL CARDIO-RESPIRATORY ARREST IN C/O HEPATO -RENAL SHUT DOWN, SEPTICEMIA, DIC, SHOCK, THROMBOCYTOPENIA IN K/C/O CIRRHOSIS OF LIVER SEPTIC SHOCK VENTRICULAR FIBRILLATION DEGENERATING TO ASYSTOLE SEPTICAEMIA WITH MOF WITH DIC - 3 UNKNOWN – 5 Limitations Not all cases reported Data incomplete No independent check of data No definite conclusions can be drawn Impact of NovoSeven® outcome Conclusion No significant variation in dose of rVIIa between those who responded vs. those who did not in medical causes of bleeding All patients with IC bleed who survived received a median dose of 48 µg/kg The median dose of rVIIa used was maximum in Dengue haemorrhagic fever though no difference in outcome Median dose correlated with outcome both in surgical and obstetric cases of bleeding was 60 µg/kg and 40 µg/kg, respectively There was no correlation with outcome and dose of rVIIa in trauma-related bleeding Conclusion (Contd.) 1st step towards collection of data in off-label use in India Wide variation in practice At present, a larger data is needed to substantiate any specific dose recommendation in off-label use